RS64301B1 - Rekombinantna humana kisela alfa-glukozidaza - Google Patents

Rekombinantna humana kisela alfa-glukozidaza

Info

Publication number
RS64301B1
RS64301B1 RS20230478A RSP20230478A RS64301B1 RS 64301 B1 RS64301 B1 RS 64301B1 RS 20230478 A RS20230478 A RS 20230478A RS P20230478 A RSP20230478 A RS P20230478A RS 64301 B1 RS64301 B1 RS 64301B1
Authority
RS
Serbia
Prior art keywords
glucosidase
recombinant human
acid alpha
human acid
alpha
Prior art date
Application number
RS20230478A
Other languages
English (en)
Inventor
Hung Do
Russell Gotschall
Richie Khanna
Yi Lun
Hing Char
Sergey Tesler
Wendy Sunderland
Enrique Diloné
Original Assignee
Amicus Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Amicus Therapeutics Inc filed Critical Amicus Therapeutics Inc
Publication of RS64301B1 publication Critical patent/RS64301B1/sr

Links

Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K38/00Medicinal preparations containing peptides
    • A61K38/16Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • A61K38/43Enzymes; Proenzymes; Derivatives thereof
    • A61K38/46Hydrolases (3)
    • A61K38/47Hydrolases (3) acting on glycosyl compounds (3.2), e.g. cellulases, lactases
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00Drugs for disorders of the muscular or neuromuscular system
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P25/00Drugs for disorders of the nervous system
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12YENZYMES
    • C12Y302/00Hydrolases acting on glycosyl compounds, i.e. glycosylases (3.2)
    • C12Y302/01Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
    • C12Y302/0102Alpha-glucosidase (3.2.1.20)

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Engineering & Computer Science (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • General Health & Medical Sciences (AREA)
  • Organic Chemistry (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • Animal Behavior & Ethology (AREA)
  • Medicinal Chemistry (AREA)
  • General Chemical & Material Sciences (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Neurology (AREA)
  • Epidemiology (AREA)
  • Orthopedic Medicine & Surgery (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Immunology (AREA)
  • Proteomics, Peptides & Aminoacids (AREA)
  • Physical Education & Sports Medicine (AREA)
  • Neurosurgery (AREA)
  • Biomedical Technology (AREA)
  • Biochemistry (AREA)
  • General Engineering & Computer Science (AREA)
  • Genetics & Genomics (AREA)
  • Wood Science & Technology (AREA)
  • Zoology (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Enzymes And Modification Thereof (AREA)
RS20230478A 2017-05-15 2018-05-15 Rekombinantna humana kisela alfa-glukozidaza RS64301B1 (sr)

Applications Claiming Priority (11)

Application Number Priority Date Filing Date Title
US201762506569P 2017-05-15 2017-05-15
US201762506574P 2017-05-15 2017-05-15
US201762506561P 2017-05-15 2017-05-15
US201762529300P 2017-07-06 2017-07-06
US201762564083P 2017-09-27 2017-09-27
US201762567334P 2017-10-03 2017-10-03
US201862618021P 2018-01-16 2018-01-16
US201862624638P 2018-01-31 2018-01-31
US201862660758P 2018-04-20 2018-04-20
PCT/US2018/032815 WO2018213340A1 (en) 2017-05-15 2018-05-15 Recombinant human acid alpha-glucosidase
EP18802722.1A EP3624831B1 (en) 2017-05-15 2018-05-15 Recombinant human acid alpha-glucosidase

Publications (1)

Publication Number Publication Date
RS64301B1 true RS64301B1 (sr) 2023-07-31

Family

ID=64274660

Family Applications (1)

Application Number Title Priority Date Filing Date
RS20230478A RS64301B1 (sr) 2017-05-15 2018-05-15 Rekombinantna humana kisela alfa-glukozidaza

Country Status (23)

Country Link
US (1) US20210393747A1 (sr)
EP (2) EP3624831B1 (sr)
JP (2) JP7193476B2 (sr)
KR (1) KR20200004414A (sr)
CN (1) CN111356474A (sr)
AU (1) AU2018270925A1 (sr)
BR (1) BR112019024125A2 (sr)
CA (1) CA3063615A1 (sr)
CL (1) CL2019003251A1 (sr)
DK (1) DK3624831T3 (sr)
ES (1) ES2950808T3 (sr)
FI (1) FI3624831T3 (sr)
HR (1) HRP20230576T1 (sr)
HU (1) HUE062504T2 (sr)
IL (2) IL310719A (sr)
LT (1) LT3624831T (sr)
MX (1) MX2019013624A (sr)
PL (1) PL3624831T3 (sr)
PT (1) PT3624831T (sr)
RS (1) RS64301B1 (sr)
SI (1) SI3624831T1 (sr)
TW (1) TW201900208A (sr)
WO (1) WO2018213340A1 (sr)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
BR112019025888A2 (pt) 2017-06-07 2020-06-30 Regeneron Pharmaceuticals, Inc. polinucleotídeo que codifica uma proteína terapêutica multidomínio, vetor de terapia gênica, proteína terapêutica multidomínio recombinante, método de expressão, métodos para reduzir o acúmulo de glicogênio em um tecido em um paciente em necessidade, para reduzir o acúmulo de glicogênio em um tecido em um paciente em necessidade epara tratar a deficiência enzimática em um paciente em necessidade e/ou tolerar o paciente à enzima para a qual é deficiente, anticorpo anti-cd63 ou fragmento de ligação a antígeno, e, composição farmacêutica
EP3871687A1 (en) * 2020-02-27 2021-09-01 eleva GmbH Enzyme replacement therapy for treating pompe disease
KR20230155622A (ko) * 2021-02-11 2023-11-10 아미쿠스 세라퓨틱스, 인코포레이티드 재조합 인간 산성 알파-글루코시다제 및 이의 용도
CN114280182A (zh) * 2021-12-23 2022-04-05 福建省中医药科学院 一种太子参均一多糖的hplc-fld检测方法
WO2023150387A1 (en) * 2022-02-07 2023-08-10 M6P Therapeutics, Inc. Compositions comprising acid alpha glucosidase and methods of use thereof
TW202400212A (zh) * 2022-05-05 2024-01-01 美商阿米庫斯醫療股份有限公司 用於治療龐貝氏病之方法

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6534300B1 (en) 1999-09-14 2003-03-18 Genzyme Glycobiology Research Institute, Inc. Methods for producing highly phosphorylated lysosomal hydrolases
EP2946785B1 (en) 2008-02-12 2018-10-24 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
JP5990102B2 (ja) * 2009-09-29 2016-09-07 ユニフェルシテイト ヘント ホスホ−6−マンノースへのマンノース−1−ホスホ−6−マンノース結合の加水分解
US9512463B2 (en) * 2011-11-08 2016-12-06 University Of Washington Methods and compositions for assaying the activity of one or more lysosomal enzymes
JP6236406B2 (ja) * 2012-03-07 2017-11-22 アミカス セラピューティックス インコーポレイテッド ポンペ病の処置のための高濃度α−グルコシダーゼ組成物
AU2014205378B2 (en) 2013-01-09 2018-08-30 Amicus Therapeutics, Inc. Stable parenteral DNJ compositions
RS65066B1 (sr) * 2014-09-30 2024-02-29 Amicus Therapeutics Inc Visoko potentna kisela alfa-glukozidaza sa pojačanim ugljenim hidratima
WO2017049161A1 (en) * 2015-09-18 2017-03-23 Duke University ACID ALPHA-GLUCOSIDASE AND A β-2 AGONIST FOR THE TREATMENT OF LYSOSOMAL STORAGE DISORDER
IL299470A (en) * 2015-12-30 2023-02-01 Amicus Therapeutics Inc Improved acid alpha-glucosidase for the treatment of Pompe disease
SG11201808592PA (en) * 2016-03-30 2018-10-30 Amicus Therapeutics Inc Method for selection of high m6p recombinant proteins

Also Published As

Publication number Publication date
DK3624831T3 (da) 2023-06-26
IL270530A (en) 2020-01-30
TW201900208A (zh) 2019-01-01
IL310719A (en) 2024-04-01
JP7193476B2 (ja) 2022-12-20
EP3624831A1 (en) 2020-03-25
FI3624831T3 (fi) 2023-06-12
EP4223310A3 (en) 2023-10-11
WO2018213340A1 (en) 2018-11-22
HUE062504T2 (hu) 2023-11-28
US20210393747A1 (en) 2021-12-23
EP4223310A2 (en) 2023-08-09
PL3624831T3 (pl) 2023-08-14
MX2019013624A (es) 2020-01-13
LT3624831T (lt) 2023-07-10
JP2023051927A (ja) 2023-04-11
HRP20230576T1 (hr) 2023-09-01
SI3624831T1 (sl) 2023-08-31
ES2950808T3 (es) 2023-10-13
JP2020519638A (ja) 2020-07-02
EP3624831B1 (en) 2023-03-29
BR112019024125A2 (pt) 2020-06-02
CN111356474A (zh) 2020-06-30
AU2018270925A1 (en) 2019-11-28
IL270530B1 (en) 2024-03-01
CA3063615A1 (en) 2018-11-22
CL2019003251A1 (es) 2020-05-22
KR20200004414A (ko) 2020-01-13
PT3624831T (pt) 2023-07-04
EP3624831A4 (en) 2021-02-17

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