KR20220107222A - 마이크로디스트로핀 유전자 치료 작제물 및 이의 용도 - Google Patents

마이크로디스트로핀 유전자 치료 작제물 및 이의 용도 Download PDF

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KR20220107222A
KR20220107222A KR1020227021099A KR20227021099A KR20220107222A KR 20220107222 A KR20220107222 A KR 20220107222A KR 1020227021099 A KR1020227021099 A KR 1020227021099A KR 20227021099 A KR20227021099 A KR 20227021099A KR 20220107222 A KR20220107222 A KR 20220107222A
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nucleic acid
seq
acid sequence
dystrophin
aav
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Korean (ko)
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춘핑 치아오
데빈 맥두걸드
예 리우
올리비에 다노스
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리젠엑스바이오 인크.
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KR1020227021099A 2019-11-28 2020-11-27 마이크로디스트로핀 유전자 치료 작제물 및 이의 용도 Pending KR20220107222A (ko)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201962941719P 2019-11-28 2019-11-28
US62/941,719 2019-11-28
US202063024933P 2020-05-14 2020-05-14
US63/024,933 2020-05-14
PCT/US2020/062484 WO2021108755A2 (en) 2019-11-28 2020-11-27 Microdystrophin gene therapy constructs and uses thereof

Publications (1)

Publication Number Publication Date
KR20220107222A true KR20220107222A (ko) 2022-08-02

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KR1020227021099A Pending KR20220107222A (ko) 2019-11-28 2020-11-27 마이크로디스트로핀 유전자 치료 작제물 및 이의 용도

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US (4) US20230270886A1 (https=)
EP (1) EP4065596A2 (https=)
JP (2) JP7822933B2 (https=)
KR (1) KR20220107222A (https=)
AU (1) AU2020392243A1 (https=)
BR (1) BR112022009895A2 (https=)
CA (1) CA3159516A1 (https=)
CL (1) CL2022001372A1 (https=)
MX (1) MX2022006427A (https=)
TW (1) TWI908746B (https=)
WO (1) WO2021108755A2 (https=)

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CN115838725B (zh) * 2022-12-30 2023-09-08 广州派真生物技术有限公司 在哺乳动物心脏中特异性启动基因的启动子序列及其应用
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