KR20200140255A - 숙시닉 세미알데하이드 데하이드로게나제 결핍(ssadhd)을 치료하기 위한 조성물 및 방법 - Google Patents

숙시닉 세미알데하이드 데하이드로게나제 결핍(ssadhd)을 치료하기 위한 조성물 및 방법 Download PDF

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KR20200140255A
KR20200140255A KR1020207026886A KR20207026886A KR20200140255A KR 20200140255 A KR20200140255 A KR 20200140255A KR 1020207026886 A KR1020207026886 A KR 1020207026886A KR 20207026886 A KR20207026886 A KR 20207026886A KR 20200140255 A KR20200140255 A KR 20200140255A
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gaba
ssadhd
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카라 레인 보겔
케네스 마이클 깁슨
개럿 로버트 에인슬리
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워싱턴 스테이트 유니버시티
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    • C12Y102/01024—Succinate-semialdehyde dehydrogenase (NAD+) (1.2.1.24)

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  • Nitrogen And Oxygen Or Sulfur-Condensed Heterocyclic Ring Systems (AREA)
  • Steroid Compounds (AREA)
KR1020207026886A 2018-02-22 2019-02-12 숙시닉 세미알데하이드 데하이드로게나제 결핍(ssadhd)을 치료하기 위한 조성물 및 방법 Ceased KR20200140255A (ko)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862634092P 2018-02-22 2018-02-22
US62/634,092 2018-02-22
PCT/US2019/017623 WO2019164703A1 (en) 2018-02-22 2019-02-12 Compositions and methods for treating succinic semialdehyde dehydrogenase deficiency (ssadhd)

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KR20200140255A true KR20200140255A (ko) 2020-12-15

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KR1020207026886A Ceased KR20200140255A (ko) 2018-02-22 2019-02-12 숙시닉 세미알데하이드 데하이드로게나제 결핍(ssadhd)을 치료하기 위한 조성물 및 방법

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US (2) US20210008225A1 (https=)
JP (2) JP2021514956A (https=)
KR (1) KR20200140255A (https=)
AU (1) AU2019225729A1 (https=)
CA (1) CA3092035A1 (https=)
WO (1) WO2019164703A1 (https=)

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* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20250018061A1 (en) * 2021-12-02 2025-01-16 The Children`S Medical Center Corporation Gene therapy in succinic semialdehyde dehydrogenase deficiency (ssadhd)
CN116478961B (zh) * 2023-04-27 2023-09-15 北京因诺惟康医药科技有限公司 CRISPR/SprCas9基因编辑系统的开发及应用
WO2025042900A1 (en) * 2023-08-21 2025-02-27 Washington State University Messenger rna treatment for succinic semialdehyde dehydrogenase deficiency

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AU2019225729A1 (en) 2020-09-03
US20220331448A1 (en) 2022-10-20
CA3092035A1 (en) 2019-08-29
US20210008225A1 (en) 2021-01-14
JP2021514956A (ja) 2021-06-17
WO2019164703A1 (en) 2019-08-29
JP2023162344A (ja) 2023-11-08

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