KR20190106990A - 제대혈 이식(ucbt) 및 증가된 갈락토세레브로시다아제(galc) 발현을 이용한 크라베병의 치료 - Google Patents

제대혈 이식(ucbt) 및 증가된 갈락토세레브로시다아제(galc) 발현을 이용한 크라베병의 치료 Download PDF

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KR20190106990A
KR20190106990A KR1020197012608A KR20197012608A KR20190106990A KR 20190106990 A KR20190106990 A KR 20190106990A KR 1020197012608 A KR1020197012608 A KR 1020197012608A KR 20197012608 A KR20197012608 A KR 20197012608A KR 20190106990 A KR20190106990 A KR 20190106990A
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galc
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nucleic acid
gly
leu
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마리아 루이사 에스콜라
폴 사볼치
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유니버시티 오브 피츠버그-오브 더 커먼웰쓰 시스템 오브 하이어 에듀케이션
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    • A—HUMAN NECESSITIES
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KR1020197012608A 2017-01-20 2018-01-19 제대혈 이식(ucbt) 및 증가된 갈락토세레브로시다아제(galc) 발현을 이용한 크라베병의 치료 Ceased KR20190106990A (ko)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201762448433P 2017-01-20 2017-01-20
US62/448,433 2017-01-20
PCT/US2018/014370 WO2018136710A1 (en) 2017-01-20 2018-01-19 Treatment of krabbe disease with umbilical cord blood transplantion (ucbt) and increased galactocerebrosidase (galc) expression

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KR20190106990A true KR20190106990A (ko) 2019-09-18

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KR1020197012608A Ceased KR20190106990A (ko) 2017-01-20 2018-01-19 제대혈 이식(ucbt) 및 증가된 갈락토세레브로시다아제(galc) 발현을 이용한 크라베병의 치료

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US (2) US12599636B2 (enExample)
EP (1) EP3571298B1 (enExample)
JP (2) JP2020505317A (enExample)
KR (1) KR20190106990A (enExample)
CN (2) CN118078860A (enExample)
AU (1) AU2018210326B9 (enExample)
CA (1) CA3042467A1 (enExample)
IL (1) IL266287A (enExample)
WO (1) WO2018136710A1 (enExample)

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EP3884057A4 (en) 2018-12-21 2022-09-07 The University of North Carolina at Chapel Hill OPTIMIZED GALC GENES AND EXPRESSION CASSETTE AND THEIR USE
EP3931337A1 (en) * 2019-02-26 2022-01-05 The Trustees of The University of Pennsylvania Compositions useful in treatment of krabbe disease
EA202192328A1 (ru) * 2019-03-22 2022-02-21 Раш Юниверсити Медикал Сентер Комбинация назальной доставки генов и пероральной доставки коричной кислоты, олеамида или гемфиброзила для лечения лизосомных болезней накопления
AU2021271635A1 (en) * 2020-05-12 2023-01-05 The Trustees Of The University Of Pennsylvania Compositions useful in treatment of krabbe disease
WO2021262498A1 (en) * 2020-06-26 2021-12-30 University Of Pittsburgh - Of The Commonwealth System Of Higher Education Methods and materials for treating non-malignant disorders or diseases with cord blood
WO2022170098A2 (en) * 2021-02-05 2022-08-11 Sigilon Therapeutics, Inc. Compositions, devices and methods for treating mps vi disease

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Publication number Priority date Publication date Assignee Title
US4458066A (en) 1980-02-29 1984-07-03 University Patents, Inc. Process for preparing polynucleotides
US6730297B1 (en) 1999-05-28 2004-05-04 Chiron Corporation Use of recombinant gene delivery vectors for treating or preventing lysosomal storage disorders
CN103589692B (zh) 2001-11-13 2018-07-24 宾夕法尼亚大学托管会 检测和/或鉴定腺伴随病毒(aav)序列以及分离所鉴定的新型序列的方法
WO2004042033A2 (en) 2002-11-01 2004-05-21 The Board Of Trustees Of The Leland Stanford Junior University Circulating stem cells and uses related thereto
US9986722B2 (en) * 2012-08-07 2018-06-05 Chiesi Farmaceutici S.P.A. Animal model of Krabbe's disease

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CA3042467A1 (en) 2018-07-26
CN118078860A (zh) 2024-05-28
EP3571298A1 (en) 2019-11-27
JP2023041950A (ja) 2023-03-24
AU2018210326B2 (en) 2024-03-07
WO2018136710A1 (en) 2018-07-26
IL266287A (en) 2019-06-30
US12599636B2 (en) 2026-04-14
AU2018210326B9 (en) 2024-04-04
EP3571298A4 (en) 2020-10-21
US20190336540A1 (en) 2019-11-07
JP2020505317A (ja) 2020-02-20
CN110168085A (zh) 2019-08-23
EP3571298C0 (en) 2026-03-04
US20260224639A1 (en) 2026-08-06
EP3571298B1 (en) 2026-03-04
AU2018210326A1 (en) 2019-05-23

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