JPWO2023150688A5 - - Google Patents
Info
- Publication number
- JPWO2023150688A5 JPWO2023150688A5 JP2024545922A JP2024545922A JPWO2023150688A5 JP WO2023150688 A5 JPWO2023150688 A5 JP WO2023150688A5 JP 2024545922 A JP2024545922 A JP 2024545922A JP 2024545922 A JP2024545922 A JP 2024545922A JP WO2023150688 A5 JPWO2023150688 A5 JP WO2023150688A5
- Authority
- JP
- Japan
- Prior art keywords
- patient
- corticosteroid
- viral vector
- administration
- optionally
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202263306361P | 2022-02-03 | 2022-02-03 | |
| US63/306,361 | 2022-02-03 | ||
| US202263402850P | 2022-08-31 | 2022-08-31 | |
| US63/402,850 | 2022-08-31 | ||
| PCT/US2023/061951 WO2023150688A2 (en) | 2022-02-03 | 2023-02-03 | Compositions and methods for improved treatment of pompe disease |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2025505575A JP2025505575A (ja) | 2025-02-28 |
| JP2025505575A5 JP2025505575A5 (https=) | 2026-02-12 |
| JPWO2023150688A5 true JPWO2023150688A5 (https=) | 2026-02-12 |
Family
ID=87552969
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024545922A Pending JP2025505575A (ja) | 2022-02-03 | 2023-02-03 | ポンペ病の改善された治療のための組成物及び方法 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20250135038A1 (https=) |
| EP (1) | EP4472658A4 (https=) |
| JP (1) | JP2025505575A (https=) |
| KR (1) | KR20240145491A (https=) |
| AU (1) | AU2023216268A1 (https=) |
| CA (1) | CA3250992A1 (https=) |
| CL (1) | CL2024002307A1 (https=) |
| IL (1) | IL314586A (https=) |
| MX (1) | MX2024009519A (https=) |
| TW (1) | TW202342092A (https=) |
| WO (1) | WO2023150688A2 (https=) |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2003224880A1 (en) * | 2002-04-05 | 2003-10-27 | Genzyme Corporation | Methods of enhancing lysosomal storage disease therapy |
| WO2021081338A1 (en) * | 2019-10-25 | 2021-04-29 | Audentes Therapeutics, Inc. | Compositions and methods for treating glycogen storage disorders |
| CA3159018A1 (en) * | 2019-11-19 | 2021-05-27 | Michael W. O'CALLAGHAN | Therapeutic adeno-associated virus comprising liver-specific promoters for treating pompe disease and lysosomal disorders |
| EP4103725A4 (en) * | 2020-02-14 | 2024-03-27 | Asklepios Biopharmaceutical, Inc. | Method of treating gene therapy associated toxicity with antibiotics |
| WO2021202599A2 (en) * | 2020-04-01 | 2021-10-07 | Valiant Biosciences, Llc | Adeno-associated virus based compositions and related methods for inducing humoral immunity |
-
2023
- 2023-02-03 KR KR1020247029043A patent/KR20240145491A/ko active Pending
- 2023-02-03 IL IL314586A patent/IL314586A/en unknown
- 2023-02-03 US US18/835,480 patent/US20250135038A1/en active Pending
- 2023-02-03 WO PCT/US2023/061951 patent/WO2023150688A2/en not_active Ceased
- 2023-02-03 CA CA3250992A patent/CA3250992A1/en active Pending
- 2023-02-03 JP JP2024545922A patent/JP2025505575A/ja active Pending
- 2023-02-03 EP EP23750442.8A patent/EP4472658A4/en active Pending
- 2023-02-03 TW TW112103875A patent/TW202342092A/zh unknown
- 2023-02-03 MX MX2024009519A patent/MX2024009519A/es unknown
- 2023-02-03 AU AU2023216268A patent/AU2023216268A1/en active Pending
-
2024
- 2024-07-31 CL CL2024002307A patent/CL2024002307A1/es unknown
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