JPWO2022192622A5 - - Google Patents

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Publication number
JPWO2022192622A5
JPWO2022192622A5 JP2023555441A JP2023555441A JPWO2022192622A5 JP WO2022192622 A5 JPWO2022192622 A5 JP WO2022192622A5 JP 2023555441 A JP2023555441 A JP 2023555441A JP 2023555441 A JP2023555441 A JP 2023555441A JP WO2022192622 A5 JPWO2022192622 A5 JP WO2022192622A5
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JP
Japan
Prior art keywords
patient
mmhg
respiratory
assessed
trial
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023555441A
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English (en)
Japanese (ja)
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JP2024510972A (ja
JP2024510972A5 (https=
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/019876 external-priority patent/WO2022192622A1/en
Publication of JP2024510972A publication Critical patent/JP2024510972A/ja
Publication of JP2024510972A5 publication Critical patent/JP2024510972A5/ja
Publication of JPWO2022192622A5 publication Critical patent/JPWO2022192622A5/ja
Pending legal-status Critical Current

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JP2023555441A 2021-03-11 2022-03-11 X連鎖性ミオチュブラーミオパチーを処置するための組成物及び方法 Pending JP2024510972A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163159898P 2021-03-11 2021-03-11
US63/159,898 2021-03-11
PCT/US2022/019876 WO2022192622A1 (en) 2021-03-11 2022-03-11 Compositions and methods for treating x-linked myotubular myopathy

Publications (3)

Publication Number Publication Date
JP2024510972A JP2024510972A (ja) 2024-03-12
JP2024510972A5 JP2024510972A5 (https=) 2025-03-19
JPWO2022192622A5 true JPWO2022192622A5 (https=) 2025-03-19

Family

ID=83227148

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023555441A Pending JP2024510972A (ja) 2021-03-11 2022-03-11 X連鎖性ミオチュブラーミオパチーを処置するための組成物及び方法

Country Status (7)

Country Link
US (1) US20240148906A1 (https=)
EP (1) EP4304664A4 (https=)
JP (1) JP2024510972A (https=)
CN (1) CN117255698A (https=)
AR (1) AR125077A1 (https=)
TW (1) TW202302156A (https=)
WO (1) WO2022192622A1 (https=)

Family Cites Families (23)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
SE9502543D0 (sv) * 1995-07-10 1995-07-10 Lachmann Burkhardt Artificial ventilation system
US6148814A (en) * 1996-02-08 2000-11-21 Ihc Health Services, Inc Method and system for patient monitoring and respiratory assistance control through mechanical ventilation by the use of deterministic protocols
US6804656B1 (en) * 1999-06-23 2004-10-12 Visicu, Inc. System and method for providing continuous, expert network critical care services from a remote location(s)
US7246618B2 (en) * 2001-06-21 2007-07-24 Nader Maher Habashi Ventilation method and control of a ventilator based on same
US8695593B2 (en) * 2007-03-31 2014-04-15 Fleur T. Tehrani Weaning and decision support system for mechanical ventilation
US20080295839A1 (en) * 2007-06-01 2008-12-04 Habashi Nader M Ventilator Apparatus and System of Ventilation
JP2012531246A (ja) * 2009-06-24 2012-12-10 オリディオン メディカル 1987 リミテッド 人工呼吸から離脱させる統合肺指標
US8789529B2 (en) * 2009-08-20 2014-07-29 Covidien Lp Method for ventilation
US20160199608A1 (en) * 2010-02-18 2016-07-14 Orlando Morejon System and method of expediting weaning from ventilator support including an artificial airway cleaning apparatus
US20110213215A1 (en) * 2010-02-26 2011-09-01 Nellcor Puritan Bennett Llc Spontaneous Breathing Trial Manager
US20180280646A1 (en) * 2010-08-13 2018-10-04 Respiratory Motion, Inc. Respiratory volume monitor and ventilator
US9327090B2 (en) * 2012-06-29 2016-05-03 Carefusion 303, Inc. Respiratory knowledge portal
US20140060540A1 (en) * 2012-09-06 2014-03-06 Nellcor Puritan Bennett Llc Method and system for automated spontaneous breathing trial
US20140150796A1 (en) * 2012-11-30 2014-06-05 Covidien Lp System and method for detecting minimal ventilation support with proportional assist ventilation plus software and remote monitoring
US20140235959A1 (en) * 2013-02-15 2014-08-21 Covidien Lp Methods and algorithms for supervisory closed-loop determination of optimized scheduling of ventilator weaning trials
US8957044B2 (en) * 2013-03-01 2015-02-17 Wake Forest University Health Sciences Systemic gene replacement therapy for treatment of X-linked myotubular myopathy (XLMTM)
WO2018035311A1 (en) * 2016-08-19 2018-02-22 Gray John T Compositions and methods for modulating gene expression using reading frame surveillance
FI128346B (en) * 2018-11-19 2020-03-31 Hapella Oy A device for taking care of respiratory well-being and for practicing and improving respiratory function
US11166862B2 (en) * 2018-12-06 2021-11-09 General Electric Company System and method for a thermoregulated environment
WO2021110576A1 (en) * 2019-12-02 2021-06-10 Koninklijke Philips N.V. Providing information for assisting in the treatment of a ventilated and sedated patient
CN115052515B (zh) * 2019-12-05 2026-01-30 迪萨蒂医疗公司 用于确定患者呼吸时所付出的呼吸努力程度的系统和方法
WO2021142336A1 (en) * 2020-01-08 2021-07-15 Puretech Lyt, Inc. Vesicle compositions for oral delivery
EP4351725A4 (en) * 2021-05-24 2025-04-23 Astellas Gene Therapies, Inc. Compositions and methods for improved treatment of cross-linked myotube myopathy

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