JPWO2022192622A5 - - Google Patents
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- Publication number
- JPWO2022192622A5 JPWO2022192622A5 JP2023555441A JP2023555441A JPWO2022192622A5 JP WO2022192622 A5 JPWO2022192622 A5 JP WO2022192622A5 JP 2023555441 A JP2023555441 A JP 2023555441A JP 2023555441 A JP2023555441 A JP 2023555441A JP WO2022192622 A5 JPWO2022192622 A5 JP WO2022192622A5
- Authority
- JP
- Japan
- Prior art keywords
- patient
- mmhg
- respiratory
- assessed
- trial
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163159898P | 2021-03-11 | 2021-03-11 | |
| US63/159,898 | 2021-03-11 | ||
| PCT/US2022/019876 WO2022192622A1 (en) | 2021-03-11 | 2022-03-11 | Compositions and methods for treating x-linked myotubular myopathy |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2024510972A JP2024510972A (ja) | 2024-03-12 |
| JP2024510972A5 JP2024510972A5 (https=) | 2025-03-19 |
| JPWO2022192622A5 true JPWO2022192622A5 (https=) | 2025-03-19 |
Family
ID=83227148
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023555441A Pending JP2024510972A (ja) | 2021-03-11 | 2022-03-11 | X連鎖性ミオチュブラーミオパチーを処置するための組成物及び方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20240148906A1 (https=) |
| EP (1) | EP4304664A4 (https=) |
| JP (1) | JP2024510972A (https=) |
| CN (1) | CN117255698A (https=) |
| AR (1) | AR125077A1 (https=) |
| TW (1) | TW202302156A (https=) |
| WO (1) | WO2022192622A1 (https=) |
Family Cites Families (23)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| SE9502543D0 (sv) * | 1995-07-10 | 1995-07-10 | Lachmann Burkhardt | Artificial ventilation system |
| US6148814A (en) * | 1996-02-08 | 2000-11-21 | Ihc Health Services, Inc | Method and system for patient monitoring and respiratory assistance control through mechanical ventilation by the use of deterministic protocols |
| US6804656B1 (en) * | 1999-06-23 | 2004-10-12 | Visicu, Inc. | System and method for providing continuous, expert network critical care services from a remote location(s) |
| US7246618B2 (en) * | 2001-06-21 | 2007-07-24 | Nader Maher Habashi | Ventilation method and control of a ventilator based on same |
| US8695593B2 (en) * | 2007-03-31 | 2014-04-15 | Fleur T. Tehrani | Weaning and decision support system for mechanical ventilation |
| US20080295839A1 (en) * | 2007-06-01 | 2008-12-04 | Habashi Nader M | Ventilator Apparatus and System of Ventilation |
| JP2012531246A (ja) * | 2009-06-24 | 2012-12-10 | オリディオン メディカル 1987 リミテッド | 人工呼吸から離脱させる統合肺指標 |
| US8789529B2 (en) * | 2009-08-20 | 2014-07-29 | Covidien Lp | Method for ventilation |
| US20160199608A1 (en) * | 2010-02-18 | 2016-07-14 | Orlando Morejon | System and method of expediting weaning from ventilator support including an artificial airway cleaning apparatus |
| US20110213215A1 (en) * | 2010-02-26 | 2011-09-01 | Nellcor Puritan Bennett Llc | Spontaneous Breathing Trial Manager |
| US20180280646A1 (en) * | 2010-08-13 | 2018-10-04 | Respiratory Motion, Inc. | Respiratory volume monitor and ventilator |
| US9327090B2 (en) * | 2012-06-29 | 2016-05-03 | Carefusion 303, Inc. | Respiratory knowledge portal |
| US20140060540A1 (en) * | 2012-09-06 | 2014-03-06 | Nellcor Puritan Bennett Llc | Method and system for automated spontaneous breathing trial |
| US20140150796A1 (en) * | 2012-11-30 | 2014-06-05 | Covidien Lp | System and method for detecting minimal ventilation support with proportional assist ventilation plus software and remote monitoring |
| US20140235959A1 (en) * | 2013-02-15 | 2014-08-21 | Covidien Lp | Methods and algorithms for supervisory closed-loop determination of optimized scheduling of ventilator weaning trials |
| US8957044B2 (en) * | 2013-03-01 | 2015-02-17 | Wake Forest University Health Sciences | Systemic gene replacement therapy for treatment of X-linked myotubular myopathy (XLMTM) |
| WO2018035311A1 (en) * | 2016-08-19 | 2018-02-22 | Gray John T | Compositions and methods for modulating gene expression using reading frame surveillance |
| FI128346B (en) * | 2018-11-19 | 2020-03-31 | Hapella Oy | A device for taking care of respiratory well-being and for practicing and improving respiratory function |
| US11166862B2 (en) * | 2018-12-06 | 2021-11-09 | General Electric Company | System and method for a thermoregulated environment |
| WO2021110576A1 (en) * | 2019-12-02 | 2021-06-10 | Koninklijke Philips N.V. | Providing information for assisting in the treatment of a ventilated and sedated patient |
| CN115052515B (zh) * | 2019-12-05 | 2026-01-30 | 迪萨蒂医疗公司 | 用于确定患者呼吸时所付出的呼吸努力程度的系统和方法 |
| WO2021142336A1 (en) * | 2020-01-08 | 2021-07-15 | Puretech Lyt, Inc. | Vesicle compositions for oral delivery |
| EP4351725A4 (en) * | 2021-05-24 | 2025-04-23 | Astellas Gene Therapies, Inc. | Compositions and methods for improved treatment of cross-linked myotube myopathy |
-
2022
- 2022-03-11 AR ARP220100570A patent/AR125077A1/es unknown
- 2022-03-11 US US18/281,346 patent/US20240148906A1/en active Pending
- 2022-03-11 EP EP22768049.3A patent/EP4304664A4/en active Pending
- 2022-03-11 TW TW111109009A patent/TW202302156A/zh unknown
- 2022-03-11 JP JP2023555441A patent/JP2024510972A/ja active Pending
- 2022-03-11 WO PCT/US2022/019876 patent/WO2022192622A1/en not_active Ceased
- 2022-03-11 CN CN202280029197.4A patent/CN117255698A/zh active Pending
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