JPWO2023141247A5 - - Google Patents

Info

Publication number
JPWO2023141247A5
JPWO2023141247A5 JP2024543083A JP2024543083A JPWO2023141247A5 JP WO2023141247 A5 JPWO2023141247 A5 JP WO2023141247A5 JP 2024543083 A JP2024543083 A JP 2024543083A JP 2024543083 A JP2024543083 A JP 2024543083A JP WO2023141247 A5 JPWO2023141247 A5 JP WO2023141247A5
Authority
JP
Japan
Prior art keywords
pharmaceutically acceptable
acceptable salt
nucleotides
rnai oligonucleotide
oligonucleotide
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024543083A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025503034A (ja
JP2025503034A5 (https=
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/011200 external-priority patent/WO2023141247A2/en
Publication of JP2025503034A publication Critical patent/JP2025503034A/ja
Publication of JPWO2023141247A5 publication Critical patent/JPWO2023141247A5/ja
Publication of JP2025503034A5 publication Critical patent/JP2025503034A5/ja
Pending legal-status Critical Current

Links

JP2024543083A 2022-01-20 2023-01-20 補体因子bを阻害するための組成物及び方法 Pending JP2025503034A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202263301454P 2022-01-20 2022-01-20
US63/301,454 2022-01-20
US202263328629P 2022-04-07 2022-04-07
US63/328,629 2022-04-07
PCT/US2023/011200 WO2023141247A2 (en) 2022-01-20 2023-01-20 Compositions and methods for inhibiting complement factor b

Publications (3)

Publication Number Publication Date
JP2025503034A JP2025503034A (ja) 2025-01-30
JPWO2023141247A5 true JPWO2023141247A5 (https=) 2026-01-27
JP2025503034A5 JP2025503034A5 (https=) 2026-01-27

Family

ID=87349101

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024543083A Pending JP2025503034A (ja) 2022-01-20 2023-01-20 補体因子bを阻害するための組成物及び方法

Country Status (16)

Country Link
US (1) US20250327070A1 (https=)
EP (1) EP4465996A2 (https=)
JP (1) JP2025503034A (https=)
KR (1) KR20240135650A (https=)
AU (1) AU2023208539A1 (https=)
CA (1) CA3247136A1 (https=)
CL (1) CL2024002156A1 (https=)
CO (1) CO2024011199A2 (https=)
CR (1) CR20240346A (https=)
DO (1) DOP2024000140A (https=)
IL (1) IL314240A (https=)
MX (1) MX2024009019A (https=)
PE (1) PE20250156A1 (https=)
TW (1) TW202345866A (https=)
UY (1) UY40118A (https=)
WO (1) WO2023141247A2 (https=)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025026228A1 (zh) * 2023-07-28 2025-02-06 苏州炫景生物科技有限公司 Cfb抑制剂组合物及其应用
WO2025113592A1 (zh) * 2023-12-01 2025-06-05 厦门甘宝利生物医药有限公司 一种抑制补体系统基因表达的rna抑制剂及其应用
WO2025140402A1 (zh) * 2023-12-28 2025-07-03 苏州瑞博生物技术股份有限公司 一种核酸、含有该核酸的组合物与缀合物及制备方法和用途
WO2025151250A2 (en) * 2024-01-09 2025-07-17 Adarx Pharmaceuticals, Inc. Complement factor b-modulating compositions and methods of use thereof
US20250382616A1 (en) * 2024-06-18 2025-12-18 Sanegene Bio Usa Inc. Small interfering rna targeting cfb and uses thereof
WO2026046277A1 (zh) * 2024-08-28 2026-03-05 倍臻生物技术(苏州)有限公司 用于抑制补体因子b(cfb)基因表达的双链核糖核酸及其缀合体

Family Cites Families (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
SG10201804960RA (en) * 2013-12-12 2018-07-30 Alnylam Pharmaceuticals Inc Complement component irna compositions and methods of use thereof
MX2022013606A (es) * 2020-04-30 2023-01-16 Alnylam Pharmaceuticals Inc Composiciones de ácido ribonucleico interferente (arni) del factor b de complemento (cfb) y métodos de uso de las mismas.

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