JPWO2023039435A5 - - Google Patents

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Publication number
JPWO2023039435A5
JPWO2023039435A5 JP2024515071A JP2024515071A JPWO2023039435A5 JP WO2023039435 A5 JPWO2023039435 A5 JP WO2023039435A5 JP 2024515071 A JP2024515071 A JP 2024515071A JP 2024515071 A JP2024515071 A JP 2024515071A JP WO2023039435 A5 JPWO2023039435 A5 JP WO2023039435A5
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JP
Japan
Prior art keywords
sequence
mutation
grna
domain
optionally
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024515071A
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English (en)
Japanese (ja)
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JP2024533315A (ja
JP2024533315A5 (https=
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/076058 external-priority patent/WO2023039435A2/en
Publication of JP2024533315A publication Critical patent/JP2024533315A/ja
Publication of JP2024533315A5 publication Critical patent/JP2024533315A5/ja
Publication of JPWO2023039435A5 publication Critical patent/JPWO2023039435A5/ja
Pending legal-status Critical Current

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JP2024515071A 2021-09-08 2022-09-07 Pah調節性組成物及び方法 Pending JP2024533315A (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US202163241897P 2021-09-08 2021-09-08
US63/241,897 2021-09-08
US202263303927P 2022-01-27 2022-01-27
US63/303,927 2022-01-27
US202263367025P 2022-06-24 2022-06-24
US63/367,025 2022-06-24
PCT/US2022/076058 WO2023039435A2 (en) 2021-09-08 2022-09-07 Pah-modulating compositions and methods

Publications (3)

Publication Number Publication Date
JP2024533315A JP2024533315A (ja) 2024-09-12
JP2024533315A5 JP2024533315A5 (https=) 2025-09-17
JPWO2023039435A5 true JPWO2023039435A5 (https=) 2025-09-17

Family

ID=85506900

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024515071A Pending JP2024533315A (ja) 2021-09-08 2022-09-07 Pah調節性組成物及び方法

Country Status (9)

Country Link
US (1) US12544458B2 (https=)
EP (1) EP4399306A4 (https=)
JP (1) JP2024533315A (https=)
KR (1) KR20240099164A (https=)
AU (1) AU2022342168A1 (https=)
CA (1) CA3231712A1 (https=)
IL (1) IL311218A (https=)
TW (1) TW202320810A (https=)
WO (1) WO2023039435A2 (https=)

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CA3174483A1 (en) 2020-03-04 2021-09-10 Flagship Pioneering Innovations Vi, Llc Improved methods and compositions for modulating a genome
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KR20240099164A (ko) 2021-09-08 2024-06-28 플래그쉽 파이어니어링 이노베이션스 브이아이, 엘엘씨 Pah-조절 조성물 및 방법
JP2024533311A (ja) 2021-09-08 2024-09-12 フラッグシップ パイオニアリング イノベーションズ シックス,エルエルシー ゲノムを調節するための方法及び組成物
EP4444362A4 (en) 2021-12-10 2026-04-01 Flagship Pioneering Innovations Vi Llc CFTR COMPOSITIONS AND MODULATION METHODS
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US20250059567A1 (en) * 2023-08-17 2025-02-20 The Trustees Of The University Of Pennsylvania Compositions and methods for the management and treatment of phenylketonuria

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EP3875603A1 (en) * 2016-07-12 2021-09-08 Life Technologies Corporation Compositions and methods for detecting nucleic acid regions
CN118530967A (zh) 2017-08-23 2024-08-23 通用医疗公司 具有改变的PAM特异性的工程化的CRISPR-Cas9核酸酶
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EP4504921A4 (en) 2022-04-01 2026-04-15 Prime Medicine Inc METHODS AND COMPOSITIONS FOR EDITING NUCLEOTID SEQUENCES

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