JPWO2022266045A5 - - Google Patents

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Publication number
JPWO2022266045A5
JPWO2022266045A5 JP2023576324A JP2023576324A JPWO2022266045A5 JP WO2022266045 A5 JPWO2022266045 A5 JP WO2022266045A5 JP 2023576324 A JP2023576324 A JP 2023576324A JP 2023576324 A JP2023576324 A JP 2023576324A JP WO2022266045 A5 JPWO2022266045 A5 JP WO2022266045A5
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JP
Japan
Prior art keywords
purines
pyrimidines
fluoro
modified
methyl modified
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023576324A
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English (en)
Japanese (ja)
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JP2024523265A5 (https=
JP2024523265A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/033356 external-priority patent/WO2022266045A1/en
Publication of JP2024523265A publication Critical patent/JP2024523265A/ja
Publication of JP2024523265A5 publication Critical patent/JP2024523265A5/ja
Publication of JPWO2022266045A5 publication Critical patent/JPWO2022266045A5/ja
Pending legal-status Critical Current

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JP2023576324A 2021-06-16 2022-06-14 Mtres1関連の疾患および障害の処置 Pending JP2024523265A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163211379P 2021-06-16 2021-06-16
US63/211,379 2021-06-16
PCT/US2022/033356 WO2022266045A1 (en) 2021-06-16 2022-06-14 Treatment of mtres1 related diseases and disorders

Publications (3)

Publication Number Publication Date
JP2024523265A JP2024523265A (ja) 2024-06-28
JP2024523265A5 JP2024523265A5 (https=) 2025-06-20
JPWO2022266045A5 true JPWO2022266045A5 (https=) 2025-06-20

Family

ID=84527350

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023576324A Pending JP2024523265A (ja) 2021-06-16 2022-06-14 Mtres1関連の疾患および障害の処置

Country Status (10)

Country Link
US (1) US20240287518A1 (https=)
EP (1) EP4355878A4 (https=)
JP (1) JP2024523265A (https=)
KR (1) KR20240034185A (https=)
CN (1) CN117980478A (https=)
AU (1) AU2022293669A1 (https=)
CA (1) CA3221625A1 (https=)
IL (1) IL309317A (https=)
MX (1) MX2023015242A (https=)
WO (1) WO2022266045A1 (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2024091874A1 (en) * 2022-10-25 2024-05-02 Empirico Inc. Gene therapy treatment of mtres1 related diseases and disorders
WO2024091873A2 (en) * 2022-10-25 2024-05-02 Empirico Inc. Small molecule treatment of mtres1 related diseases and disorders
WO2025158407A2 (en) * 2024-01-26 2025-07-31 Empirico Inc. Treatment of mtres1 related diseases and disorders
WO2025226835A1 (en) * 2024-04-24 2025-10-30 Empirico Inc. Gene therapy treatment of mtres1 related diseases and disorders
WO2025255269A1 (en) * 2024-06-05 2025-12-11 Empirico Inc. Treatment of mtres1 related diseases and disorders

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20080279846A1 (en) * 2007-05-11 2008-11-13 Thomas Jefferson University Methods of treatment and prevention of neurodegenerative diseases and disorders
US10004814B2 (en) * 2013-11-11 2018-06-26 Sirna Therapeutics, Inc. Systemic delivery of myostatin short interfering nucleic acids (siNA) conjugated to a lipophilic moiety
US10287580B2 (en) * 2014-03-14 2019-05-14 The General Hospital Corporation Molecular re-engineering of excitation-inhibition balance in memory circuits
PH12018501207B1 (en) * 2015-12-21 2024-02-23 Novartis Ag Compositions and methods for decreasing tau expression
EP4004206A1 (en) * 2019-07-23 2022-06-01 University of Rochester Targeted rna cleavage with crispr-cas

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