JPWO2022018518A5 - - Google Patents

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Publication number
JPWO2022018518A5
JPWO2022018518A5 JP2023512665A JP2023512665A JPWO2022018518A5 JP WO2022018518 A5 JPWO2022018518 A5 JP WO2022018518A5 JP 2023512665 A JP2023512665 A JP 2023512665A JP 2023512665 A JP2023512665 A JP 2023512665A JP WO2022018518 A5 JPWO2022018518 A5 JP WO2022018518A5
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Japan
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sequence
promoter
seq
aav
identity
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Pending
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JP2023512665A
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English (en)
Japanese (ja)
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JP2023542279A (ja
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Priority claimed from CN202010705069.XA external-priority patent/CN113952472A/zh
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Publication of JP2023542279A publication Critical patent/JP2023542279A/ja
Publication of JPWO2022018518A5 publication Critical patent/JPWO2022018518A5/ja
Pending legal-status Critical Current

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JP2023512665A 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法 Pending JP2023542279A (ja)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
CN202010705069.XA CN113952472A (zh) 2020-07-21 2020-07-21 用于治疗眼部疾病的组合物和方法
PCT/IB2021/000509 WO2022018518A1 (en) 2020-07-21 2021-07-20 Compositions and methods for the treatment of eye diseases

Publications (2)

Publication Number Publication Date
JP2023542279A JP2023542279A (ja) 2023-10-06
JPWO2022018518A5 true JPWO2022018518A5 (cg-RX-API-DMAC7.html) 2024-07-26

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ID=79459955

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Application Number Title Priority Date Filing Date
JP2023512665A Pending JP2023542279A (ja) 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法

Country Status (7)

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US (1) US20230321281A1 (cg-RX-API-DMAC7.html)
EP (1) EP4185319A4 (cg-RX-API-DMAC7.html)
JP (1) JP2023542279A (cg-RX-API-DMAC7.html)
CN (2) CN113952472A (cg-RX-API-DMAC7.html)
AU (1) AU2021312379A1 (cg-RX-API-DMAC7.html)
CA (1) CA3186826A1 (cg-RX-API-DMAC7.html)
WO (1) WO2022018518A1 (cg-RX-API-DMAC7.html)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
BR112023003834A2 (pt) * 2020-09-02 2023-03-28 4D Molecular Therapeutics Inc Genes rpgrorf15 otimizados por códon e usos dos mesmos

Family Cites Families (13)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP1567198A4 (en) * 2002-12-02 2006-05-31 Genvec Inc MATERIALS AND METHOD FOR THE TREATMENT OF EYE DISEASES
CN105120901A (zh) * 2012-07-11 2015-12-02 宾夕法尼亚大学托管会 Rpgr x染色体连锁视网膜退化的aav介导的基因治疗
WO2014045674A1 (ja) * 2012-09-19 2014-03-27 国立大学法人東京大学 神経活動依存的プロモータ活性を有するdna、及びこれを含むベクター
CA2919995A1 (en) * 2013-08-05 2015-02-12 Academisch Ziekenhuis Leiden H.O.D.N. Leids Universitair Medisch Centrum Recombinant aav-crumbs homologue composition and methods for treating lca-8 and progressive rp
WO2015082690A1 (en) * 2013-12-06 2015-06-11 INSERM (Institut National de la Santé et de la Recherche Médicale) Methods and pharmaceutical compositions for expressing a polynucleotide of interest in the retinal pigment epithelium of a subject
EP3132051B1 (en) * 2014-04-15 2019-03-20 Applied Genetic Technologies Corporation Codon optimized nucleic acid encoding a retinitis pigmentosa gtpase regulator (rpgr)
PE20170260A1 (es) * 2014-05-02 2017-04-12 Genzyme Corp Vectores de aav para la terapia genica de la retina y el snc
GB201516066D0 (en) * 2015-09-10 2015-10-28 Young & Co Llp D Treatment of retinitis pigmentosa
MX2019001276A (es) * 2016-07-29 2019-06-13 Univ California Viriones de virus adenoasociados con cápside variante y métodos para su uso.
AU2018290954B2 (en) * 2017-06-30 2023-07-13 The Regents Of The University Of California Adeno-associated virus virions with variant capsids and methods of use thereof
TWI815856B (zh) * 2018-01-31 2023-09-21 美國全美兒童醫院之研究學會 用於肢帶型肌肉失養症2c型之基因療法
JOP20210054A1 (ar) * 2018-09-21 2020-03-21 Nightstarx Ltd تركيبات وطرق لعلاج التهاب الشبكية الصباغي
WO2021142447A1 (en) * 2020-01-10 2021-07-15 Solid Biosciences Inc. Viral vector for combination therapy

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