JPWO2021247924A5 - - Google Patents
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- JPWO2021247924A5 JPWO2021247924A5 JP2022574652A JP2022574652A JPWO2021247924A5 JP WO2021247924 A5 JPWO2021247924 A5 JP WO2021247924A5 JP 2022574652 A JP2022574652 A JP 2022574652A JP 2022574652 A JP2022574652 A JP 2022574652A JP WO2021247924 A5 JPWO2021247924 A5 JP WO2021247924A5
- Authority
- JP
- Japan
- Prior art keywords
- nucleic acid
- nuclease
- programmable
- casφ
- sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
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Applications Claiming Priority (17)
Application Number | Priority Date | Filing Date | Title |
---|---|---|---|
US202063034346P | 2020-06-03 | 2020-06-03 | |
US63/034,346 | 2020-06-03 | ||
US202063037535P | 2020-06-10 | 2020-06-10 | |
US63/037,535 | 2020-06-10 | ||
US202063040998P | 2020-06-18 | 2020-06-18 | |
US63/040,998 | 2020-06-18 | ||
US202063092481P | 2020-10-15 | 2020-10-15 | |
US63/092,481 | 2020-10-15 | ||
US202063116083P | 2020-11-19 | 2020-11-19 | |
US63/116,083 | 2020-11-19 | ||
US202063124676P | 2020-12-11 | 2020-12-11 | |
US63/124,676 | 2020-12-11 | ||
US202163156883P | 2021-03-04 | 2021-03-04 | |
US63/156,883 | 2021-03-04 | ||
US202163178472P | 2021-04-22 | 2021-04-22 | |
US63/178,472 | 2021-04-22 | ||
PCT/US2021/035781 WO2021247924A1 (fr) | 2020-06-03 | 2021-06-03 | Nucléases programmables et méthodes d'utilisation |
Publications (2)
Publication Number | Publication Date |
---|---|
JP2023529151A JP2023529151A (ja) | 2023-07-07 |
JPWO2021247924A5 true JPWO2021247924A5 (fr) | 2024-06-11 |
Family
ID=78829953
Family Applications (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
JP2022574652A Withdrawn JP2023529151A (ja) | 2020-06-03 | 2021-06-03 | プログラム可能なヌクレアーゼ及び使用方法 |
Country Status (7)
Country | Link |
---|---|
US (2) | US20230357735A1 (fr) |
EP (1) | EP4162052A4 (fr) |
JP (1) | JP2023529151A (fr) |
CN (1) | CN116209755A (fr) |
AU (1) | AU2021282578A1 (fr) |
CA (1) | CA3178670A1 (fr) |
WO (1) | WO2021247924A1 (fr) |
Families Citing this family (11)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
WO2020028729A1 (fr) | 2018-08-01 | 2020-02-06 | Mammoth Biosciences, Inc. | Compositions de nucléase programmable et leurs méthodes d'utilisation |
AU2021368740A1 (en) * | 2020-10-30 | 2023-06-01 | Arbor Biotechnologies, Inc. | Compositions comprising an rna guide targeting trac and uses thereof |
WO2023173110A1 (fr) * | 2022-03-11 | 2023-09-14 | Epicrispr Biotechnologies, Inc. | Compositions, systèmes et méthodes de traitement de l'hypercholestérolémie familiale par ciblage de pcsk9 |
WO2023220654A2 (fr) * | 2022-05-10 | 2023-11-16 | Mammoth Biosciences, Inc. | Compositions de protéines effectrices et procédés d'utilisation associés |
WO2023220649A2 (fr) * | 2022-05-10 | 2023-11-16 | Mammoth Biosciences, Inc. | Compositions protéiques effectrices et leurs méthodes d'utilisation |
WO2024047587A1 (fr) * | 2022-08-31 | 2024-03-07 | Regel Therapeutics, Inc. | Compositions cas-phi et méthodes d'utilisation |
WO2024073114A1 (fr) * | 2022-09-30 | 2024-04-04 | Vedabio, Inc. | Administration d'agents thérapeutiques in vivo par l'intermédiaire d'un système en cascade basé sur crispr |
WO2024091958A1 (fr) * | 2022-10-25 | 2024-05-02 | Mammoth Biosciences, Inc. | Protéines effectrices, compositions, systèmes et procédés de modification de serpina1 |
WO2024107665A1 (fr) * | 2022-11-14 | 2024-05-23 | Mammoth Biosciences, Inc. | Protéines effectrices, compositions, systèmes et procédés d'utilisation associés |
WO2024127370A1 (fr) * | 2022-12-16 | 2024-06-20 | LifeEDIT Therapeutics, Inc. | Arn guides ciblant le gène trac et procédés d'utilisation |
WO2024137767A1 (fr) * | 2022-12-22 | 2024-06-27 | Mammoth Biosciences, Inc. | Compositions et procédés de modification de dux4 |
Family Cites Families (7)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
US20050108791A1 (en) * | 2001-12-04 | 2005-05-19 | Edgerton Michael D. | Transgenic plants with improved phenotypes |
US20110275135A1 (en) * | 2010-05-05 | 2011-11-10 | Battelle Energy Alliance, Llc | Genetic elements, proteins, and associated methods including application of additional genetic information to gram (+) thermoacidophiles |
US20140113376A1 (en) * | 2011-06-01 | 2014-04-24 | Rotem Sorek | Compositions and methods for downregulating prokaryotic genes |
EP3800248A3 (fr) * | 2014-04-18 | 2021-08-04 | Editas Medicine, Inc. | Méthodes, compositions et constituants associés à crispr/cas pour l'immunothérapie du cancer |
US9790490B2 (en) * | 2015-06-18 | 2017-10-17 | The Broad Institute Inc. | CRISPR enzymes and systems |
EP3445853A1 (fr) * | 2016-04-19 | 2019-02-27 | The Broad Institute, Inc. | Complexes cpf1 à activité d'indel réduite |
WO2020181101A1 (fr) * | 2019-03-07 | 2020-09-10 | The Regents Of The University Of California | Polypeptides effecteurs crispr-cas et procédés d'utilisation associés |
-
2021
- 2021-06-03 JP JP2022574652A patent/JP2023529151A/ja not_active Withdrawn
- 2021-06-03 CA CA3178670A patent/CA3178670A1/fr active Pending
- 2021-06-03 WO PCT/US2021/035781 patent/WO2021247924A1/fr unknown
- 2021-06-03 CN CN202180056722.7A patent/CN116209755A/zh active Pending
- 2021-06-03 EP EP21819013.0A patent/EP4162052A4/fr active Pending
- 2021-06-03 AU AU2021282578A patent/AU2021282578A1/en active Pending
- 2021-06-03 US US18/000,640 patent/US20230357735A1/en active Pending
-
2022
- 2022-08-11 US US17/819,137 patent/US20230167454A1/en not_active Abandoned
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