JPWO2021247924A5 - - Google Patents

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Publication number
JPWO2021247924A5
JPWO2021247924A5 JP2022574652A JP2022574652A JPWO2021247924A5 JP WO2021247924 A5 JPWO2021247924 A5 JP WO2021247924A5 JP 2022574652 A JP2022574652 A JP 2022574652A JP 2022574652 A JP2022574652 A JP 2022574652A JP WO2021247924 A5 JPWO2021247924 A5 JP WO2021247924A5
Authority
JP
Japan
Prior art keywords
nucleic acid
nuclease
programmable
casφ
sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022574652A
Other languages
English (en)
Japanese (ja)
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JP2023529151A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/035781 external-priority patent/WO2021247924A1/fr
Publication of JP2023529151A publication Critical patent/JP2023529151A/ja
Publication of JPWO2021247924A5 publication Critical patent/JPWO2021247924A5/ja
Withdrawn legal-status Critical Current

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JP2022574652A 2020-06-03 2021-06-03 プログラム可能なヌクレアーゼ及び使用方法 Withdrawn JP2023529151A (ja)

Applications Claiming Priority (17)

Application Number Priority Date Filing Date Title
US202063034346P 2020-06-03 2020-06-03
US63/034,346 2020-06-03
US202063037535P 2020-06-10 2020-06-10
US63/037,535 2020-06-10
US202063040998P 2020-06-18 2020-06-18
US63/040,998 2020-06-18
US202063092481P 2020-10-15 2020-10-15
US63/092,481 2020-10-15
US202063116083P 2020-11-19 2020-11-19
US63/116,083 2020-11-19
US202063124676P 2020-12-11 2020-12-11
US63/124,676 2020-12-11
US202163156883P 2021-03-04 2021-03-04
US63/156,883 2021-03-04
US202163178472P 2021-04-22 2021-04-22
US63/178,472 2021-04-22
PCT/US2021/035781 WO2021247924A1 (fr) 2020-06-03 2021-06-03 Nucléases programmables et méthodes d'utilisation

Publications (2)

Publication Number Publication Date
JP2023529151A JP2023529151A (ja) 2023-07-07
JPWO2021247924A5 true JPWO2021247924A5 (fr) 2024-06-11

Family

ID=78829953

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022574652A Withdrawn JP2023529151A (ja) 2020-06-03 2021-06-03 プログラム可能なヌクレアーゼ及び使用方法

Country Status (7)

Country Link
US (2) US20230357735A1 (fr)
EP (1) EP4162052A4 (fr)
JP (1) JP2023529151A (fr)
CN (1) CN116209755A (fr)
AU (1) AU2021282578A1 (fr)
CA (1) CA3178670A1 (fr)
WO (1) WO2021247924A1 (fr)

Families Citing this family (11)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2020028729A1 (fr) 2018-08-01 2020-02-06 Mammoth Biosciences, Inc. Compositions de nucléase programmable et leurs méthodes d'utilisation
AU2021368740A1 (en) * 2020-10-30 2023-06-01 Arbor Biotechnologies, Inc. Compositions comprising an rna guide targeting trac and uses thereof
WO2023173110A1 (fr) * 2022-03-11 2023-09-14 Epicrispr Biotechnologies, Inc. Compositions, systèmes et méthodes de traitement de l'hypercholestérolémie familiale par ciblage de pcsk9
WO2023220654A2 (fr) * 2022-05-10 2023-11-16 Mammoth Biosciences, Inc. Compositions de protéines effectrices et procédés d'utilisation associés
WO2023220649A2 (fr) * 2022-05-10 2023-11-16 Mammoth Biosciences, Inc. Compositions protéiques effectrices et leurs méthodes d'utilisation
WO2024047587A1 (fr) * 2022-08-31 2024-03-07 Regel Therapeutics, Inc. Compositions cas-phi et méthodes d'utilisation
WO2024073114A1 (fr) * 2022-09-30 2024-04-04 Vedabio, Inc. Administration d'agents thérapeutiques in vivo par l'intermédiaire d'un système en cascade basé sur crispr
WO2024091958A1 (fr) * 2022-10-25 2024-05-02 Mammoth Biosciences, Inc. Protéines effectrices, compositions, systèmes et procédés de modification de serpina1
WO2024107665A1 (fr) * 2022-11-14 2024-05-23 Mammoth Biosciences, Inc. Protéines effectrices, compositions, systèmes et procédés d'utilisation associés
WO2024127370A1 (fr) * 2022-12-16 2024-06-20 LifeEDIT Therapeutics, Inc. Arn guides ciblant le gène trac et procédés d'utilisation
WO2024137767A1 (fr) * 2022-12-22 2024-06-27 Mammoth Biosciences, Inc. Compositions et procédés de modification de dux4

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20050108791A1 (en) * 2001-12-04 2005-05-19 Edgerton Michael D. Transgenic plants with improved phenotypes
US20110275135A1 (en) * 2010-05-05 2011-11-10 Battelle Energy Alliance, Llc Genetic elements, proteins, and associated methods including application of additional genetic information to gram (+) thermoacidophiles
US20140113376A1 (en) * 2011-06-01 2014-04-24 Rotem Sorek Compositions and methods for downregulating prokaryotic genes
EP3800248A3 (fr) * 2014-04-18 2021-08-04 Editas Medicine, Inc. Méthodes, compositions et constituants associés à crispr/cas pour l'immunothérapie du cancer
US9790490B2 (en) * 2015-06-18 2017-10-17 The Broad Institute Inc. CRISPR enzymes and systems
EP3445853A1 (fr) * 2016-04-19 2019-02-27 The Broad Institute, Inc. Complexes cpf1 à activité d'indel réduite
WO2020181101A1 (fr) * 2019-03-07 2020-09-10 The Regents Of The University Of California Polypeptides effecteurs crispr-cas et procédés d'utilisation associés

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