JPWO2020160458A5 - - Google Patents
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- JPWO2020160458A5 JPWO2020160458A5 JP2021544547A JP2021544547A JPWO2020160458A5 JP WO2020160458 A5 JPWO2020160458 A5 JP WO2020160458A5 JP 2021544547 A JP2021544547 A JP 2021544547A JP 2021544547 A JP2021544547 A JP 2021544547A JP WO2020160458 A5 JPWO2020160458 A5 JP WO2020160458A5
- Authority
- JP
- Japan
- Prior art keywords
- acid sequence
- amino acid
- grn
- optionally
- seq
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962800096P | 2019-02-01 | 2019-02-01 | |
| US62/800,096 | 2019-02-01 | ||
| PCT/US2020/016192 WO2020160458A1 (en) | 2019-02-01 | 2020-01-31 | Compositions and methods for treating neurocognitive disorders |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022523913A JP2022523913A (ja) | 2022-04-27 |
| JPWO2020160458A5 true JPWO2020160458A5 (de) | 2023-04-25 |
Family
ID=71841663
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021544547A Pending JP2022523913A (ja) | 2019-02-01 | 2020-01-31 | 神経認知障害を処置するための組成物及び方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20220111005A1 (de) |
| EP (1) | EP3917539A4 (de) |
| JP (1) | JP2022523913A (de) |
| CA (1) | CA3128003A1 (de) |
| IL (1) | IL285269A (de) |
| MA (1) | MA54874A (de) |
| WO (1) | WO2020160458A1 (de) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20210147872A1 (en) * | 2019-10-22 | 2021-05-20 | Applied Genetic Technologies Corporation | Adeno-associated virus (aav) systems for treatment of progranulin associated neurodegenerative diseases or disorders |
| EP4146797A1 (de) * | 2020-05-06 | 2023-03-15 | Orchard Therapeutics (Europe) Limited | Behandlung von neurodegenerativen erkrankungen |
| WO2023015175A1 (en) * | 2021-08-02 | 2023-02-09 | Board Of Regents, The University Of Texas System | Modified nucleic acid compositions and associated methods for treatment of phenylketonuria |
| WO2023196619A1 (en) * | 2022-04-08 | 2023-10-12 | Shape Therapeutics Inc. | Promoter switches for tissue-specific expression |
Family Cites Families (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU647754B2 (en) * | 1989-10-16 | 1994-03-31 | Hem Research, Inc. | Diagnosis and treatment of neuro-cognitive disorders associated with systemic immunological malfunction |
| US8486635B2 (en) * | 2006-05-30 | 2013-07-16 | Mayo Foundation For Medical Education And Research | Detecting and treating dementia |
| ES2596885T3 (es) * | 2006-06-07 | 2017-01-12 | Genzyme Corporation | Terapia génica para esclerosis lateral amiotrófica y otros trastornos de la medula espinal |
| US20100324127A1 (en) * | 2008-01-16 | 2010-12-23 | Kay Denis G | Treating neurodegenerative diseases with progranulin |
| WO2010022175A1 (en) * | 2008-08-19 | 2010-02-25 | Yale University | Identification of sortilin as a neuronal receptor for the frontotemporal dementia protein, progranulin |
| SG10202109219SA (en) * | 2009-05-02 | 2021-10-28 | Genzyme Corp | Gene therapy for neurodegenerative disorders |
| US20110203007A1 (en) * | 2010-02-16 | 2011-08-18 | Board Of Supervisors Of Louisiana State University And Agricultural And Mechanical College | Assays of neurodegenerative disorders, including frontotemporal dementia and amyotrophic lateral sclerosis |
| CN103491974A (zh) * | 2010-11-16 | 2014-01-01 | 神经机能生命科学公司 | 用于提高中性溶酶的表达与活性的方法 |
| AU2017227803B2 (en) * | 2016-03-02 | 2024-05-02 | Defne AMADO | Therapy for frontotemporal dementia |
| WO2018013775A2 (en) * | 2016-07-14 | 2018-01-18 | Emory University | Granulin compositions and uses related thereto |
| AU2018236353B2 (en) * | 2017-03-15 | 2023-12-21 | The Regents Of The University Of California | Methods of treating lysosomal disorders |
| WO2020172490A1 (en) * | 2019-02-22 | 2020-08-27 | The Trustees Of The University Of Pennsylvania | Recombinant adeno-associated virus for treatment of grn-associated adult-onset neurodegeneration |
-
2020
- 2020-01-31 MA MA054874A patent/MA54874A/fr unknown
- 2020-01-31 EP EP20748326.4A patent/EP3917539A4/de active Pending
- 2020-01-31 WO PCT/US2020/016192 patent/WO2020160458A1/en unknown
- 2020-01-31 US US17/427,298 patent/US20220111005A1/en active Pending
- 2020-01-31 JP JP2021544547A patent/JP2022523913A/ja active Pending
- 2020-01-31 CA CA3128003A patent/CA3128003A1/en active Pending
-
2021
- 2021-08-01 IL IL285269A patent/IL285269A/en unknown
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