JPWO2019164703A5 - - Google Patents

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Publication number
JPWO2019164703A5
JPWO2019164703A5 JP2020544456A JP2020544456A JPWO2019164703A5 JP WO2019164703 A5 JPWO2019164703 A5 JP WO2019164703A5 JP 2020544456 A JP2020544456 A JP 2020544456A JP 2020544456 A JP2020544456 A JP 2020544456A JP WO2019164703 A5 JPWO2019164703 A5 JP WO2019164703A5
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JP
Japan
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composition
enzyme
administered
composition according
trin
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Pending
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JP2020544456A
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English (en)
Japanese (ja)
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JP2021514956A (ja
JP2021514956A5 (https=
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Priority claimed from PCT/US2019/017623 external-priority patent/WO2019164703A1/en
Publication of JP2021514956A publication Critical patent/JP2021514956A/ja
Publication of JP2021514956A5 publication Critical patent/JP2021514956A5/ja
Publication of JPWO2019164703A5 publication Critical patent/JPWO2019164703A5/ja
Priority to JP2023139463A priority Critical patent/JP2023162344A/ja
Pending legal-status Critical Current

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JP2020544456A 2018-02-22 2019-02-12 コハク酸セミアルデヒドデヒドロゲナーゼ欠損症(ssadhd)を処置するための組成物および方法 Pending JP2021514956A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023139463A JP2023162344A (ja) 2018-02-22 2023-08-30 コハク酸セミアルデヒドデヒドロゲナーゼ欠損症(ssadhd)を処置するための組成物および方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862634092P 2018-02-22 2018-02-22
US62/634,092 2018-02-22
PCT/US2019/017623 WO2019164703A1 (en) 2018-02-22 2019-02-12 Compositions and methods for treating succinic semialdehyde dehydrogenase deficiency (ssadhd)

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2023139463A Division JP2023162344A (ja) 2018-02-22 2023-08-30 コハク酸セミアルデヒドデヒドロゲナーゼ欠損症(ssadhd)を処置するための組成物および方法

Publications (3)

Publication Number Publication Date
JP2021514956A JP2021514956A (ja) 2021-06-17
JP2021514956A5 JP2021514956A5 (https=) 2022-03-31
JPWO2019164703A5 true JPWO2019164703A5 (https=) 2022-03-31

Family

ID=67688295

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2020544456A Pending JP2021514956A (ja) 2018-02-22 2019-02-12 コハク酸セミアルデヒドデヒドロゲナーゼ欠損症(ssadhd)を処置するための組成物および方法
JP2023139463A Pending JP2023162344A (ja) 2018-02-22 2023-08-30 コハク酸セミアルデヒドデヒドロゲナーゼ欠損症(ssadhd)を処置するための組成物および方法

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2023139463A Pending JP2023162344A (ja) 2018-02-22 2023-08-30 コハク酸セミアルデヒドデヒドロゲナーゼ欠損症(ssadhd)を処置するための組成物および方法

Country Status (6)

Country Link
US (2) US20210008225A1 (https=)
JP (2) JP2021514956A (https=)
KR (1) KR20200140255A (https=)
AU (1) AU2019225729A1 (https=)
CA (1) CA3092035A1 (https=)
WO (1) WO2019164703A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20250018061A1 (en) * 2021-12-02 2025-01-16 The Children`S Medical Center Corporation Gene therapy in succinic semialdehyde dehydrogenase deficiency (ssadhd)
CN116478961B (zh) * 2023-04-27 2023-09-15 北京因诺惟康医药科技有限公司 CRISPR/SprCas9基因编辑系统的开发及应用
WO2025042900A1 (en) * 2023-08-21 2025-02-27 Washington State University Messenger rna treatment for succinic semialdehyde dehydrogenase deficiency

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