JP2021514956A5 - - Google Patents
Info
- Publication number
- JP2021514956A5 JP2021514956A5 JP2020544456A JP2020544456A JP2021514956A5 JP 2021514956 A5 JP2021514956 A5 JP 2021514956A5 JP 2020544456 A JP2020544456 A JP 2020544456A JP 2020544456 A JP2020544456 A JP 2020544456A JP 2021514956 A5 JP2021514956 A5 JP 2021514956A5
- Authority
- JP
- Japan
- Prior art keywords
- composition according
- enzyme
- administered
- composition
- trin
- Prior art date
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2023139463A JP2023162344A (ja) | 2018-02-22 | 2023-08-30 | コハク酸セミアルデヒドデヒドロゲナーゼ欠損症（ｓｓａｄｈｄ）を処置するための組成物および方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862634092P | 2018-02-22 | 2018-02-22 | |
| US62/634,092 | 2018-02-22 | ||
| PCT/US2019/017623 WO2019164703A1 (en) | 2018-02-22 | 2019-02-12 | Compositions and methods for treating succinic semialdehyde dehydrogenase deficiency (ssadhd) |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023139463A Division JP2023162344A (ja) | 2018-02-22 | 2023-08-30 | コハク酸セミアルデヒドデヒドロゲナーゼ欠損症（ｓｓａｄｈｄ）を処置するための組成物および方法 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2021514956A JP2021514956A (ja) | 2021-06-17 |
| JP2021514956A5 true JP2021514956A5 (https=) | 2022-03-31 |
| JPWO2019164703A5 JPWO2019164703A5 (https=) | 2022-03-31 |
Family
ID=67688295
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020544456A Pending JP2021514956A (ja) | 2018-02-22 | 2019-02-12 | コハク酸セミアルデヒドデヒドロゲナーゼ欠損症（ｓｓａｄｈｄ）を処置するための組成物および方法 |
| JP2023139463A Pending JP2023162344A (ja) | 2018-02-22 | 2023-08-30 | コハク酸セミアルデヒドデヒドロゲナーゼ欠損症（ｓｓａｄｈｄ）を処置するための組成物および方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023139463A Pending JP2023162344A (ja) | 2018-02-22 | 2023-08-30 | コハク酸セミアルデヒドデヒドロゲナーゼ欠損症（ｓｓａｄｈｄ）を処置するための組成物および方法 |
Country Status (6)
| Country | Link |
|---|---|
| US (2) | US20210008225A1 (https=) |
| JP (2) | JP2021514956A (https=) |
| KR (1) | KR20200140255A (https=) |
| AU (1) | AU2019225729A1 (https=) |
| CA (1) | CA3092035A1 (https=) |
| WO (1) | WO2019164703A1 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20250018061A1 (en) * | 2021-12-02 | 2025-01-16 | The Children`S Medical Center Corporation | Gene therapy in succinic semialdehyde dehydrogenase deficiency (ssadhd) |
| CN116478961B (zh) * | 2023-04-27 | 2023-09-15 | 北京因诺惟康医药科技有限公司 | CRISPR/SprCas9基因编辑系统的开发及应用 |
| WO2025042900A1 (en) * | 2023-08-21 | 2025-02-27 | Washington State University | Messenger rna treatment for succinic semialdehyde dehydrogenase deficiency |
-
2019
- 2019-02-12 JP JP2020544456A patent/JP2021514956A/ja active Pending
- 2019-02-12 KR KR1020207026886A patent/KR20200140255A/ko not_active Ceased
- 2019-02-12 CA CA3092035A patent/CA3092035A1/en active Pending
- 2019-02-12 WO PCT/US2019/017623 patent/WO2019164703A1/en not_active Ceased
- 2019-02-12 AU AU2019225729A patent/AU2019225729A1/en not_active Abandoned
- 2019-02-12 US US16/969,927 patent/US20210008225A1/en not_active Abandoned
-
2022
- 2022-03-30 US US17/708,799 patent/US20220331448A1/en not_active Abandoned
-
2023
- 2023-08-30 JP JP2023139463A patent/JP2023162344A/ja active Pending
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