JPWO2019153009A5 - - Google Patents
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- Publication number
- JPWO2019153009A5 JPWO2019153009A5 JP2020564045A JP2020564045A JPWO2019153009A5 JP WO2019153009 A5 JPWO2019153009 A5 JP WO2019153009A5 JP 2020564045 A JP2020564045 A JP 2020564045A JP 2020564045 A JP2020564045 A JP 2020564045A JP WO2019153009 A5 JPWO2019153009 A5 JP WO2019153009A5
- Authority
- JP
- Japan
- Prior art keywords
- nucleic acid
- acid sequence
- regulatory element
- segment
- seq
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
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Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2023188066A JP2024012479A (ja) | 2018-02-05 | 2023-11-02 | 転写調節要素及びその使用 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862626561P | 2018-02-05 | 2018-02-05 | |
| US62/626,561 | 2018-02-05 | ||
| PCT/US2019/016692 WO2019153009A1 (en) | 2018-02-05 | 2019-02-05 | Transcription regulatory elements and uses thereof |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023188066A Division JP2024012479A (ja) | 2018-02-05 | 2023-11-02 | 転写調節要素及びその使用 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2021512649A JP2021512649A (ja) | 2021-05-20 |
| JPWO2019153009A5 true JPWO2019153009A5 (enrdf_load_stackoverflow) | 2022-02-09 |
| JP7381494B2 JP7381494B2 (ja) | 2023-11-15 |
Family
ID=67478520
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020564045A Active JP7381494B2 (ja) | 2018-02-05 | 2019-02-05 | 転写調節要素及びその使用 |
| JP2023188066A Pending JP2024012479A (ja) | 2018-02-05 | 2023-11-02 | 転写調節要素及びその使用 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023188066A Pending JP2024012479A (ja) | 2018-02-05 | 2023-11-02 | 転写調節要素及びその使用 |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US12296026B2 (enrdf_load_stackoverflow) |
| EP (1) | EP3749756A4 (enrdf_load_stackoverflow) |
| JP (2) | JP7381494B2 (enrdf_load_stackoverflow) |
| CN (1) | CN111936621B (enrdf_load_stackoverflow) |
| MA (1) | MA51753A (enrdf_load_stackoverflow) |
| WO (1) | WO2019153009A1 (enrdf_load_stackoverflow) |
Families Citing this family (16)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3066569A1 (en) | 2017-06-07 | 2018-12-13 | Regeneron Pharmaceuticals, Inc. | Compositions and methods for internalizing enzymes |
| KR20200118151A (ko) | 2018-02-07 | 2020-10-14 | 리제너론 파마슈티칼스 인코포레이티드 | 치료 단백질 전달을 위한 방법 및 조성물 |
| JP7467356B2 (ja) * | 2018-02-07 | 2024-04-15 | ジェネトン | ハイブリッド調節要素 |
| CN112135624B (zh) | 2018-05-17 | 2024-07-19 | 瑞泽恩制药公司 | 抗cd63抗体、缀合物和其用途 |
| GB201813528D0 (en) | 2018-08-20 | 2018-10-03 | Ucl Business Plc | Factor IX encoding nucleotides |
| US10842885B2 (en) | 2018-08-20 | 2020-11-24 | Ucl Business Ltd | Factor IX encoding nucleotides |
| EP4048286A4 (en) * | 2019-10-25 | 2023-12-06 | Audentes Therapeutics, Inc. | Compositions and methods for treating glycogen storage disorders |
| CA3159018A1 (en) * | 2019-11-19 | 2021-05-27 | Michael W. O'CALLAGHAN | Therapeutic adeno-associated virus comprising liver-specific promoters for treating pompe disease and lysosomal disorders |
| EP4107259A1 (en) * | 2020-02-18 | 2022-12-28 | Vrije Universiteit Brussel | Novel combination of nucleic acid regulatory elements and methods and uses thereof |
| GB202013194D0 (en) * | 2020-08-24 | 2020-10-07 | Combigene Ab | Gene therapy for lipodystrophy |
| AR126660A1 (es) * | 2021-07-28 | 2023-11-01 | Univ Brussel Vrije | Mejorando la eficacia de la terapia génica dirigida a músculos |
| WO2023173078A2 (en) * | 2022-03-11 | 2023-09-14 | Homology Medicines, Inc. | Bidirectional dual promoter expression vectors and uses thereof |
| TW202409290A (zh) * | 2022-06-27 | 2024-03-01 | 美商安斯泰來基因治療股份有限公司 | 用於治療肌強直性營養不良之組合物及方法 |
| WO2024074143A1 (en) * | 2022-10-08 | 2024-04-11 | Lingyi Biotech Co., Ltd. | Construct for enhancing gene expression |
| WO2025004002A2 (en) | 2023-06-30 | 2025-01-02 | Takeda Pharmaceutical Company Limited | Treatment of pompe disease |
| CN118064436B (zh) * | 2024-04-18 | 2024-07-26 | 上海凌医生物科技有限公司 | 一种增强基因表达的嵌合启动子 |
Family Cites Families (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2004535801A (ja) * | 2001-05-24 | 2004-12-02 | ジェンザイム コーポレイション | 筋特異的発現ベクター |
| US8021875B2 (en) | 2001-08-27 | 2011-09-20 | Roche Madison Inc. | Methods for expression of transgenes |
| ES2381796T3 (es) | 2004-09-22 | 2012-05-31 | St. Jude Children's Research Hospital | Expresión mejorada de Factor IX en vectores de terapia génica |
| US20070161031A1 (en) | 2005-12-16 | 2007-07-12 | The Board Of Trustees Of The Leland Stanford Junior University | Functional arrays for high throughput characterization of gene expression regulatory elements |
| RU2015101276A (ru) | 2012-06-19 | 2016-08-10 | Юниверсити Оф Флорида Рисерч Фаундейшн, Инк. | Способы лечения болезней и композиции для их осуществления |
| US20140242595A1 (en) * | 2013-02-22 | 2014-08-28 | Cellular Dynamics International, Inc. | Hepatocyte production via forward programming by combined genetic and chemical engineering |
| EP3097197B1 (en) | 2014-01-21 | 2020-12-16 | Vrije Universiteit Brussel | Muscle-specific nucleic acid regulatory elements and methods and use thereof |
| WO2015196179A1 (en) | 2014-06-20 | 2015-12-23 | University Of Florida Research Foundation, Inc. | Methods of packaging multiple adeno-associated virus vectors |
| EP4491733A3 (en) | 2015-04-23 | 2025-03-26 | University of Massachusetts | Modulation of aav vector transgene expression |
| WO2017053677A1 (en) * | 2015-09-24 | 2017-03-30 | Biomarin Pharmaceutical Inc. | Adeno-associated virus factor viii vectors, associated viral particles and therapeutic formulations comprising the same |
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2019
- 2019-02-05 US US16/966,521 patent/US12296026B2/en active Active
- 2019-02-05 EP EP19748361.3A patent/EP3749756A4/en active Pending
- 2019-02-05 JP JP2020564045A patent/JP7381494B2/ja active Active
- 2019-02-05 WO PCT/US2019/016692 patent/WO2019153009A1/en active IP Right Grant
- 2019-02-05 CN CN201980015960.6A patent/CN111936621B/zh active Active
- 2019-02-05 MA MA051753A patent/MA51753A/fr unknown
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2023
- 2023-11-02 JP JP2023188066A patent/JP2024012479A/ja active Pending