JP7413256B2 - 神経変性疾患の遺伝子治療 - Google Patents

神経変性疾患の遺伝子治療 Download PDF

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JP7413256B2
JP7413256B2 JP2020523011A JP2020523011A JP7413256B2 JP 7413256 B2 JP7413256 B2 JP 7413256B2 JP 2020523011 A JP2020523011 A JP 2020523011A JP 2020523011 A JP2020523011 A JP 2020523011A JP 7413256 B2 JP7413256 B2 JP 7413256B2
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nucleic acid
vector
raav
c9orf72
protein
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JP2021500049A (ja
JP2021500049A5 (enExample
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アベリオビッチ，アサ
ヘックマン，ラウラ
リーン，エルベ
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Prevail Therapeutics Inc
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Prevail Therapeutics Inc
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    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
    • C12N15/1138—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing against receptors or cell surface proteins
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JP2020523011A 2017-10-23 2018-10-23 神経変性疾患の遺伝子治療 Active JP7413256B2 (ja)

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JP2023220260A JP2024045131A (ja) 2017-10-23 2023-12-27 神経変性疾患の遺伝子治療

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US201762575795P 2017-10-23 2017-10-23
US62/575,795 2017-10-23
US201862742723P 2018-10-08 2018-10-08
US62/742,723 2018-10-08
PCT/US2018/057187 WO2019084068A1 (en) 2017-10-23 2018-10-23 GENE THERAPIES FOR NEURODEGENERATIVE DISEASE

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JP2021500049A JP2021500049A (ja) 2021-01-07
JP2021500049A5 JP2021500049A5 (enExample) 2021-11-25
JP7413256B2 true JP7413256B2 (ja) 2024-01-15

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JP2023220260A Pending JP2024045131A (ja) 2017-10-23 2023-12-27 神経変性疾患の遺伝子治療

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US (1) US20210261981A1 (enExample)
EP (1) EP3701030A4 (enExample)
JP (2) JP7413256B2 (enExample)
KR (1) KR20200075865A (enExample)
CN (2) CN111819281B (enExample)
AU (1) AU2018354195A1 (enExample)
BR (1) BR112020008033A2 (enExample)
CA (2) CA3083582A1 (enExample)
IL (2) IL274129A (enExample)
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JPWO2022097727A1 (enExample) 2020-11-06 2022-05-12
KR20220109347A (ko) 2021-01-28 2022-08-04 주식회사 에이브레인 신경 퇴행성 질환의 치료를 위한 유전자 요법
KR102711715B1 (ko) 2021-01-28 2024-09-30 주식회사 에이브레인 신경 퇴행성 질환의 치료를 위한 유전자 요법
KR102707250B1 (ko) 2021-10-28 2024-09-13 한국해양과학기술원 신규 화합물 및 이를 유효성분으로 포함하는 신경염증성 뇌질환 예방 또는 치료용 조성물
WO2023133574A1 (en) * 2022-01-10 2023-07-13 The Trustees Of The University Of Pennsylvania Compositions and methods useful for treatment of c9orf72-mediated disorders
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