JP7406253B2 - 免疫回避性ベクターおよび遺伝子療法のための使用 - Google Patents

免疫回避性ベクターおよび遺伝子療法のための使用 Download PDF

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JP7406253B2
JP7406253B2 JP2020538958A JP2020538958A JP7406253B2 JP 7406253 B2 JP7406253 B2 JP 7406253B2 JP 2020538958 A JP2020538958 A JP 2020538958A JP 2020538958 A JP2020538958 A JP 2020538958A JP 7406253 B2 JP7406253 B2 JP 7406253B2
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ジェニン ウィンズロウ,
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カメレオン バイオサイエンシーズ, インコーポレイテッド
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    • C12N15/63Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
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    • C07K14/745Blood coagulation or fibrinolysis factors
    • C07K14/755Factors VIII, e.g. factor VIII C (AHF), factor VIII Ag (VWF)
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    • C12N2750/14011Parvoviridae
    • C12N2750/14111Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141Use of virus, viral particle or viral elements as a vector
    • C12N2750/14143Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector

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  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
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JP2020538958A 2018-01-11 2019-01-11 免疫回避性ベクターおよび遺伝子療法のための使用 Active JP7406253B2 (ja)

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JP2023146391A JP2023160938A (ja) 2018-01-11 2023-09-08 免疫回避性ベクターおよび遺伝子療法のための使用

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US201862616167P 2018-01-11 2018-01-11
US62/616,167 2018-01-11
US201862768779P 2018-11-16 2018-11-16
US62/768,779 2018-11-16
PCT/US2019/013361 WO2019140311A1 (en) 2018-01-11 2019-01-11 Immuno-evasive vectors and use for gene therapy

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JP2021510522A JP2021510522A (ja) 2021-04-30
JP2021510522A5 JP2021510522A5 (https=) 2022-02-07
JP7406253B2 true JP7406253B2 (ja) 2023-12-27

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US (1) US20200338216A1 (https=)
EP (1) EP3737768A1 (https=)
JP (2) JP7406253B2 (https=)
KR (1) KR20200128519A (https=)
CN (1) CN111836896A (https=)
AU (1) AU2019206639A1 (https=)
BR (1) BR112020014093A2 (https=)
CA (1) CA3088897A1 (https=)
CL (1) CL2020001850A1 (https=)
IL (1) IL275951A (https=)
MX (1) MX2020007390A (https=)
RU (1) RU2020126574A (https=)
SG (1) SG11202006298XA (https=)
WO (1) WO2019140311A1 (https=)

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EP4118219A4 (en) * 2020-03-11 2024-04-17 Shanghai Belief-Delivery Biomed Co., Ltd. Novel use of aspirin compound in increasing nucleic acid expression
US20230355803A1 (en) * 2020-06-24 2023-11-09 Chameleon Biosciences, Inc. Extracellular vesicles with immune modulators
CN112410304A (zh) * 2020-11-12 2021-02-26 天津大学 一种基因修饰的外泌体及其制备方法和应用
WO2023028035A1 (en) * 2021-08-23 2023-03-02 University Of Florida Research Foundation, Incorporated Lipid enveloped recombinant aav particles for gene therapy use
EP4660308A1 (en) * 2023-01-31 2025-12-10 Synplogen Co., Ltd. Helper gene

Citations (6)

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JP2001512142A (ja) 1997-07-31 2001-08-21 カイロン コーポレイション 宿主の免疫抑制を介するaavベクターの再投与を可能にする方法
JP2002514388A (ja) 1998-04-29 2002-05-21 ユニバーシティー・オブ・サウザーン・カリフォルニア 修飾エンベロープエスコート蛋白質を含むレトロウイルスベクター
JP2002518050A (ja) 1998-06-19 2002-06-25 メディジーン・アクチェンゲゼルシャフト Aavの構造タンパク質、その製造及び用途
WO2006138670A2 (en) 2005-06-16 2006-12-28 Virxsys Corporation Antibody complexes
JP2008504821A (ja) 2004-07-01 2008-02-21 バイレクシス コーポレイション ベクター・パッケージング細胞系列
US20160067228A1 (en) 2014-09-07 2016-03-10 Selecta Biosciences, Inc. Methods and compositions for attenuating anti-viral transfer vector immune responses

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JP4691611B1 (ja) 2010-01-15 2011-06-01 富士フイルム株式会社 有機電界発光素子
WO2011106376A2 (en) * 2010-02-23 2011-09-01 The General Hospital Corporation Use of microvesicles in the treatment of medical conditions
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WO2017136764A1 (en) * 2016-02-05 2017-08-10 The General Hospital Corporation Hybrid system for efficient gene delivery to cells of the inner ear

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JP2001512142A (ja) 1997-07-31 2001-08-21 カイロン コーポレイション 宿主の免疫抑制を介するaavベクターの再投与を可能にする方法
JP2002514388A (ja) 1998-04-29 2002-05-21 ユニバーシティー・オブ・サウザーン・カリフォルニア 修飾エンベロープエスコート蛋白質を含むレトロウイルスベクター
JP2002518050A (ja) 1998-06-19 2002-06-25 メディジーン・アクチェンゲゼルシャフト Aavの構造タンパク質、その製造及び用途
JP2008504821A (ja) 2004-07-01 2008-02-21 バイレクシス コーポレイション ベクター・パッケージング細胞系列
WO2006138670A2 (en) 2005-06-16 2006-12-28 Virxsys Corporation Antibody complexes
US20160067228A1 (en) 2014-09-07 2016-03-10 Selecta Biosciences, Inc. Methods and compositions for attenuating anti-viral transfer vector immune responses

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Title
www.moleculartherapy.org, 2012年,vol.20 no.5,p.960-971,doi:10.1038/mt.2011.303

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KR20200128519A (ko) 2020-11-13
US20200338216A1 (en) 2020-10-29
JP2021510522A (ja) 2021-04-30
WO2019140311A1 (en) 2019-07-18
BR112020014093A2 (pt) 2020-12-01
EP3737768A1 (en) 2020-11-18
MX2020007390A (es) 2020-10-14
AU2019206639A1 (en) 2020-08-20
CA3088897A1 (en) 2019-07-18
IL275951A (en) 2020-08-31
JP2023160938A (ja) 2023-11-02
CL2020001850A1 (es) 2020-12-04
SG11202006298XA (en) 2020-07-29
RU2020126574A (ru) 2022-02-11
CN111836896A (zh) 2020-10-27

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