JP7057281B2 - 眼疾患のための遺伝子療法 - Google Patents

眼疾患のための遺伝子療法 Download PDF

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JP7057281B2
JP7057281B2 JP2018531202A JP2018531202A JP7057281B2 JP 7057281 B2 JP7057281 B2 JP 7057281B2 JP 2018531202 A JP2018531202 A JP 2018531202A JP 2018531202 A JP2018531202 A JP 2018531202A JP 7057281 B2 JP7057281 B2 JP 7057281B2
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aav
promoter
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sequence
expression
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JP2019502378A5 (enExample
JP2019502378A (ja
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ベネット，ジーン
ベニセリ，ジャネット
サン，ジャンウェイ
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ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア
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    • A61K48/00—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
    • A61K48/005—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'active' part of the composition delivered, i.e. the nucleic acid delivered
    • A61K48/0058—Nucleic acids adapted for tissue specific expression, e.g. having tissue specific promoters as part of a contruct
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    • C12N2840/00—Vectors comprising a special translation-regulating system
    • C12N2840/007—Vectors comprising a special translation-regulating system cell or tissue specific

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JP2018531202A 2015-12-14 2016-12-13 眼疾患のための遺伝子療法 Active JP7057281B2 (ja)

Priority Applications (1)

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JP2022063749A JP2022088656A (ja) 2015-12-14 2022-04-07 眼疾患のための遺伝子療法

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US201562266789P 2015-12-14 2015-12-14
US62/266,789 2015-12-14
PCT/US2016/066402 WO2017106202A2 (en) 2015-12-14 2016-12-13 Gene therapy for ocular disorders

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JP2019502378A5 JP2019502378A5 (enExample) 2020-01-30
JP7057281B2 true JP7057281B2 (ja) 2022-04-19

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EP (2) EP3795180B1 (enExample)
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KR (1) KR20180099719A (enExample)
CN (1) CN109069668B (enExample)
AU (1) AU2016370487C1 (enExample)
BR (1) BR112018011838A2 (enExample)
CA (1) CA3008264A1 (enExample)
ES (1) ES2826384T3 (enExample)
MX (2) MX2018007230A (enExample)
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JP7766393B2 (ja) 2017-06-14 2025-11-10 ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア 眼疾患のための遺伝子療法
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