JP6924487B2 - 非組み込みウイルス送達システムおよびその使用の方法 - Google Patents

非組み込みウイルス送達システムおよびその使用の方法 Download PDF

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JP6924487B2
JP6924487B2 JP2017564550A JP2017564550A JP6924487B2 JP 6924487 B2 JP6924487 B2 JP 6924487B2 JP 2017564550 A JP2017564550 A JP 2017564550A JP 2017564550 A JP2017564550 A JP 2017564550A JP 6924487 B2 JP6924487 B2 JP 6924487B2
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JP2018521643A5 (enExample
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チャールズ デイビッド パウザ，
チャールズ デイビッド パウザ，
テイラー ローゼン，
テイラー ローゼン，
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アメリカン ジーン テクノロジーズ インターナショナル インコーポレイテッド
アメリカン ジーン テクノロジーズ インターナショナル インコーポレイテッド
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    • C12N15/63—Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
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    • A61K48/0008—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition
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    • C12N15/1131—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing against viruses
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JP2017564550A 2015-06-10 2016-06-08 非組み込みウイルス送達システムおよびその使用の方法 Active JP6924487B2 (ja)

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US201562173784P 2015-06-10 2015-06-10
US62/173,784 2015-06-10
PCT/US2016/036519 WO2016200997A1 (en) 2015-06-10 2016-06-08 Non-integrating viral delivery system and methods of use thereof

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JP2018521643A JP2018521643A (ja) 2018-08-09
JP2018521643A5 JP2018521643A5 (enExample) 2019-07-11
JP6924487B2 true JP6924487B2 (ja) 2021-08-25

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JP2021021627A Pending JP2021072865A (ja) 2015-06-10 2021-02-15 非組み込みウイルス送達システムおよびその使用の方法
JP2023099918A Withdrawn JP2023113963A (ja) 2015-06-10 2023-06-19 非組み込みウイルス送達システムおよびその使用の方法
JP2025063242A Pending JP2025114562A (ja) 2015-06-10 2025-04-07 非組み込みウイルス送達システムおよびその使用の方法

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JP2023099918A Withdrawn JP2023113963A (ja) 2015-06-10 2023-06-19 非組み込みウイルス送達システムおよびその使用の方法
JP2025063242A Pending JP2025114562A (ja) 2015-06-10 2025-04-07 非組み込みウイルス送達システムおよびその使用の方法

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US20100183558A1 (en) 2008-10-17 2010-07-22 Zhennan Lai Safe lentiviral vectors for targeted delivery of multiple therapeutic molecules
JP6890831B2 (ja) 2015-07-08 2021-06-18 アメリカン ジーン テクノロジーズ インターナショナル インコーポレイテッド Ｈｉｖ予備免疫化および免疫療法
AU2017207906B2 (en) 2016-01-15 2021-03-11 American Gene Technologies International Inc. Methods and compositions for the activation of gamma-delta T-cells
US10137144B2 (en) 2016-01-15 2018-11-27 American Gene Technologies International Inc. Methods and compositions for the activation of gamma-delta T-cells
WO2017139065A1 (en) 2016-02-08 2017-08-17 American Gene Technologies International Inc. Hiv vaccination and immunotherapy
WO2017156311A2 (en) 2016-03-09 2017-09-14 American Gene Technologies International Inc. Combination vectors and methods for treating cancer
WO2017213697A1 (en) * 2016-06-08 2017-12-14 American Gene Technologies International Inc. Non-integrating viral delivery system and methods related thereto
WO2018009246A1 (en) 2016-07-08 2018-01-11 American Gene Technologies International Inc. Hiv pre-immunization and immunotherapy
EP3487507A4 (en) 2016-07-21 2020-04-08 American Gene Technologies International, Inc. VIRAL VECTORS FOR THE TREATMENT OF PARKINSON'S DISEASE
US11820999B2 (en) 2017-04-03 2023-11-21 American Gene Technologies International Inc. Compositions and methods for treating phenylketonuria
US12480129B1 (en) * 2024-09-17 2025-11-25 Wyvern Pharmaceuticals Inc. Composition for regulating production of interfering ribonucleic acid

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WO1994012629A1 (en) * 1992-12-02 1994-06-09 Baylor College Of Medicine Episomal vectors for gene therapy
BR9405507A (pt) * 1993-07-13 1999-05-25 Rhone Poulenc Rorer Sa Adenovirus recombinante defeituoso linhagem celular e composição farmaceutica
EP1012236A1 (en) * 1997-08-15 2000-06-28 Rubicon Laboratory Inc. Retrovirus and viral vectors
US6399383B1 (en) * 1997-10-28 2002-06-04 Maxygen, Inc. Human papilloma virus vectors
ATE286138T1 (de) * 1998-03-20 2005-01-15 Univ Pennsylvania Zusammensetzungen und verfahren zur helfer-freien herstellung von rekombinante adeno-assoziierten viren
WO2004053137A2 (en) 2002-12-11 2004-06-24 Cytos Biotechnology Ag Method for protein production
WO2005005644A1 (en) * 2003-07-11 2005-01-20 Cytos Biotechnology Ag Gene expression system
WO2006048215A1 (en) 2004-11-02 2006-05-11 Istituto Di Ricerche Di Biologia Molecolare P Angeletti Spa Adenoviral amplicon and producer cells for the production of replication-defective adenoviral vectors, methods of preparation and use thereof
WO2007133674A2 (en) * 2006-05-12 2007-11-22 Lentigen Corporation Lentiviral vector compositions, methods and applications
WO2010033722A2 (en) * 2008-09-17 2010-03-25 Isogenis, Inc. Construction of fully-deleted adenovirus-based gene delivery vectors and uses thereof
WO2011071476A2 (en) 2008-11-14 2011-06-16 Life Technologies Corporation Compositions and methods for engineering cells
WO2011119942A1 (en) * 2010-03-25 2011-09-29 Vistagen Therapeutics, Inc. Induction of ips cells using transient episomal vectors
EP2878674A1 (en) * 2013-11-28 2015-06-03 Fundación Centro Nacional de Investigaciones Cardiovasculares Carlos III (CNIC) Stable episomes based on non-integrative lentiviral vectors

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EP3307894A1 (en) 2018-04-18
JP2018521643A (ja) 2018-08-09
JP2025114562A (ja) 2025-08-05
US20180161455A1 (en) 2018-06-14
JP2023113963A (ja) 2023-08-16
JP2021072865A (ja) 2021-05-13
WO2016200997A1 (en) 2016-12-15
EP3307894A4 (en) 2019-01-16

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