JP6866385B2 - 造血幹細胞における遺伝子編集のための方法および組成物 - Google Patents

造血幹細胞における遺伝子編集のための方法および組成物 Download PDF

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JP6866385B2
JP6866385B2 JP2018543036A JP2018543036A JP6866385B2 JP 6866385 B2 JP6866385 B2 JP 6866385B2 JP 2018543036 A JP2018543036 A JP 2018543036A JP 2018543036 A JP2018543036 A JP 2018543036A JP 6866385 B2 JP6866385 B2 JP 6866385B2
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cells
hspc
cell
cancer
nucleic acid
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JP2018533625A (ja
JP2018533625A5 (OSRAM
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ザール ジル
ザール ジル
ミリアム キム
ミリアム キム
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ザ トラスティーズ オブ ザ ユニバーシティ オブ ペンシルバニア
ザ トラスティーズ オブ ザ ユニバーシティ オブ ペンシルバニア
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JP2018543036A 2015-11-04 2016-11-03 造血幹細胞における遺伝子編集のための方法および組成物 Expired - Fee Related JP6866385B2 (ja)

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JP2021065361A JP7378439B2 (ja) 2015-11-04 2021-04-07 造血幹細胞における遺伝子編集のための方法および組成物
JP2023097365A JP2023115069A (ja) 2015-11-04 2023-06-14 造血幹細胞における遺伝子編集のための方法および組成物

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PCT/US2016/060273 WO2017079400A1 (en) 2015-11-04 2016-11-03 Methods and compositions for gene editing in hematopoietic stem cells

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US (3) US10548922B2 (OSRAM)
EP (1) EP3370741B1 (OSRAM)
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KR (1) KR20180073679A (OSRAM)
CN (1) CN108463227A (OSRAM)
AU (2) AU2016349280B2 (OSRAM)
BR (1) BR112018009098A8 (OSRAM)
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