JP2025518052A5 - - Google Patents
Info
- Publication number
- JP2025518052A5 JP2025518052A5 JP2024569534A JP2024569534A JP2025518052A5 JP 2025518052 A5 JP2025518052 A5 JP 2025518052A5 JP 2024569534 A JP2024569534 A JP 2024569534A JP 2024569534 A JP2024569534 A JP 2024569534A JP 2025518052 A5 JP2025518052 A5 JP 2025518052A5
- Authority
- JP
- Japan
- Prior art keywords
- aav vector
- vector according
- seq
- amino acid
- aav
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202263345144P | 2022-05-24 | 2022-05-24 | |
| US63/345,144 | 2022-05-24 | ||
| PCT/US2023/066865 WO2023230409A1 (en) | 2022-05-24 | 2023-05-11 | Compositions for treating xlmtm |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025518052A JP2025518052A (ja) | 2025-06-12 |
| JP2025518052A5 true JP2025518052A5 (enExample) | 2026-05-07 |
Family
ID=88920170
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024569534A Pending JP2025518052A (ja) | 2022-05-24 | 2023-05-11 | Ｘｌｍｔｍを処置するための組成物 |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20260009049A1 (enExample) |
| EP (1) | EP4532516A4 (enExample) |
| JP (1) | JP2025518052A (enExample) |
| KR (1) | KR20250039324A (enExample) |
| CN (1) | CN119630687A (enExample) |
| AU (1) | AU2023276729A1 (enExample) |
| CA (1) | CA3256727A1 (enExample) |
| CL (1) | CL2024003578A1 (enExample) |
| CO (1) | CO2024016313A2 (enExample) |
| IL (1) | IL317433A (enExample) |
| MX (1) | MX2024014499A (enExample) |
| WO (1) | WO2023230409A1 (enExample) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR20260114566A (ko) * | 2023-11-14 | 2026-07-22 | 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 | 심근 및 골격근-특이적 표적화 모티프를 갖는 조성물 및 이의 용도 |
| WO2026030244A1 (en) * | 2024-07-30 | 2026-02-05 | Kate Therapeutics, Inc. | Adeno-associated virus compositions for the treatment of limb girdle muscular dystrophy 2a |
| WO2026122921A1 (en) | 2024-12-05 | 2026-06-11 | The Trustees Of The University Of Pennsylvania | Gene therapy for barth syndrome |
Family Cites Families (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP1668143B1 (en) * | 2003-09-30 | 2013-03-20 | The Trustees of The University of Pennsylvania | Adeno-associated virus (aav) clades, sequences, vectors containing same, and uses therefor |
| US20210355509A1 (en) * | 2018-08-07 | 2021-11-18 | The Children's Hospital Of Philadelphia | Alternative splicing regulation of gene expression and therapeutic methods |
| WO2022020616A1 (en) * | 2020-07-22 | 2022-01-27 | The Broad Institute, Inc. | Engineered muscle targeting compositions |
-
2023
- 2023-05-11 KR KR1020247042275A patent/KR20250039324A/ko active Pending
- 2023-05-11 CN CN202380053671.1A patent/CN119630687A/zh active Pending
- 2023-05-11 EP EP23812681.7A patent/EP4532516A4/en active Pending
- 2023-05-11 AU AU2023276729A patent/AU2023276729A1/en active Pending
- 2023-05-11 US US18/868,544 patent/US20260009049A1/en active Pending
- 2023-05-11 CA CA3256727A patent/CA3256727A1/en active Pending
- 2023-05-11 JP JP2024569534A patent/JP2025518052A/ja active Pending
- 2023-05-11 WO PCT/US2023/066865 patent/WO2023230409A1/en not_active Ceased
- 2023-05-11 IL IL317433A patent/IL317433A/en unknown
-
2024
- 2024-11-22 MX MX2024014499A patent/MX2024014499A/es unknown
- 2024-11-22 CL CL2024003578A patent/CL2024003578A1/es unknown
- 2024-11-29 CO CONC2024/0016313A patent/CO2024016313A2/es unknown