JP2025513740A5 - - Google Patents

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Publication number
JP2025513740A5
JP2025513740A5 JP2024557542A JP2024557542A JP2025513740A5 JP 2025513740 A5 JP2025513740 A5 JP 2025513740A5 JP 2024557542 A JP2024557542 A JP 2024557542A JP 2024557542 A JP2024557542 A JP 2024557542A JP 2025513740 A5 JP2025513740 A5 JP 2025513740A5
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JP
Japan
Prior art keywords
aon
nucleotides
lna
modified
bases
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024557542A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025513740A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/065098 external-priority patent/WO2023192904A1/en
Publication of JP2025513740A publication Critical patent/JP2025513740A/ja
Publication of JP2025513740A5 publication Critical patent/JP2025513740A5/ja
Pending legal-status Critical Current

Links

JP2024557542A 2022-03-30 2023-03-29 ジストロフィンエクソンスキッピングオリゴヌクレオチド Pending JP2025513740A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263362189P 2022-03-30 2022-03-30
US63/362,189 2022-03-30
PCT/US2023/065098 WO2023192904A1 (en) 2022-03-30 2023-03-29 Dystrophin exon skipping oligonucleotides

Publications (2)

Publication Number Publication Date
JP2025513740A JP2025513740A (ja) 2025-04-30
JP2025513740A5 true JP2025513740A5 (https=) 2026-03-26

Family

ID=86054214

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024557542A Pending JP2025513740A (ja) 2022-03-30 2023-03-29 ジストロフィンエクソンスキッピングオリゴヌクレオチド

Country Status (8)

Country Link
US (1) US20230348909A1 (https=)
EP (1) EP4499828A1 (https=)
JP (1) JP2025513740A (https=)
AR (1) AR128918A1 (https=)
AU (1) AU2023245901A1 (https=)
CA (1) CA3254863A1 (https=)
TW (1) TW202342070A (https=)
WO (1) WO2023192904A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2021354760A1 (en) * 2020-09-30 2023-05-11 Biomarin Technologies B.V. Antisense oligonucleotides targeting the exon 51 of dystrophin gene

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