JP2025504474A5 - - Google Patents
Info
- Publication number
- JP2025504474A5 JP2025504474A5 JP2024543108A JP2024543108A JP2025504474A5 JP 2025504474 A5 JP2025504474 A5 JP 2025504474A5 JP 2024543108 A JP2024543108 A JP 2024543108A JP 2024543108 A JP2024543108 A JP 2024543108A JP 2025504474 A5 JP2025504474 A5 JP 2025504474A5
- Authority
- JP
- Japan
- Prior art keywords
- sarna
- antisense strand
- sense strand
- seq
- nucleotide
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| CN2022072958 | 2022-01-20 | ||
| CNPCT/CN2022/072958 | 2022-01-20 | ||
| PCT/CN2023/072076 WO2023138502A1 (en) | 2022-01-20 | 2023-01-13 | Oligonucleotide modulators activating utrophin expression |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025504474A JP2025504474A (ja) | 2025-02-12 |
| JP2025504474A5 true JP2025504474A5 (https=) | 2026-01-16 |
Family
ID=87347803
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024543108A Pending JP2025504474A (ja) | 2022-01-20 | 2023-01-13 | オリゴヌクレオチド調節因子がユートロフィン発現を活性化する |
Country Status (10)
| Country | Link |
|---|---|
| US (1) | US20250101421A1 (https=) |
| EP (1) | EP4466359A1 (https=) |
| JP (1) | JP2025504474A (https=) |
| KR (1) | KR20250005567A (https=) |
| CN (1) | CN118829728A (https=) |
| AU (1) | AU2023209973A1 (https=) |
| CA (1) | CA3249545A1 (https=) |
| MX (1) | MX2024008939A (https=) |
| TW (1) | TW202338088A (https=) |
| WO (1) | WO2023138502A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2025201529A1 (en) * | 2024-03-29 | 2025-10-02 | Ractigen Therapeutics | Compounds for synthesizing modified small activating rna molecules, modified small activating rna molecules and uses thereof |
Family Cites Families (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP5931720B2 (ja) * | 2009-05-08 | 2016-06-08 | クルナ・インコーポレーテッド | Ｄｍｄファミリーに対する天然アンチセンス転写物の抑制によるジストロフィンファミリー関連疾患の治療 |
| EA201492122A1 (ru) * | 2012-05-16 | 2015-10-30 | Рана Терапьютикс, Инк. | Композиции и способы для модулирования экспрессии utrn |
| US20170044540A1 (en) * | 2014-04-22 | 2017-02-16 | Mina Therapeutics Limited | Sarna compositions and methods of use |
| WO2021230385A1 (en) * | 2020-05-15 | 2021-11-18 | Astellas Pharma Inc. | Method for treating muscular dystrophy by targeting utrophin gene |
-
2023
- 2023-01-13 CN CN202380018216.8A patent/CN118829728A/zh active Pending
- 2023-01-13 MX MX2024008939A patent/MX2024008939A/es unknown
- 2023-01-13 US US18/730,577 patent/US20250101421A1/en active Pending
- 2023-01-13 CA CA3249545A patent/CA3249545A1/en active Pending
- 2023-01-13 WO PCT/CN2023/072076 patent/WO2023138502A1/en not_active Ceased
- 2023-01-13 EP EP23742817.2A patent/EP4466359A1/en active Pending
- 2023-01-13 JP JP2024543108A patent/JP2025504474A/ja active Pending
- 2023-01-13 AU AU2023209973A patent/AU2023209973A1/en active Pending
- 2023-01-13 KR KR1020247027787A patent/KR20250005567A/ko active Pending
- 2023-01-19 TW TW112102859A patent/TW202338088A/zh unknown
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