JP2024546950A5 - - Google Patents

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Publication number
JP2024546950A5
JP2024546950A5 JP2024535950A JP2024535950A JP2024546950A5 JP 2024546950 A5 JP2024546950 A5 JP 2024546950A5 JP 2024535950 A JP2024535950 A JP 2024535950A JP 2024535950 A JP2024535950 A JP 2024535950A JP 2024546950 A5 JP2024546950 A5 JP 2024546950A5
Authority
JP
Japan
Application number
JP2024535950A
Other languages
Japanese (ja)
Other versions
JP2024546950A (ja
JPWO2023114944A5 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/081714 external-priority patent/WO2023114944A1/en
Publication of JP2024546950A publication Critical patent/JP2024546950A/ja
Publication of JP2024546950A5 publication Critical patent/JP2024546950A5/ja
Publication of JPWO2023114944A5 publication Critical patent/JPWO2023114944A5/ja
Pending legal-status Critical Current

Links

JP2024535950A 2021-12-16 2022-12-15 脂質ナノ粒子に用いるフッ化カチオン性脂質 Pending JP2024546950A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163290384P 2021-12-16 2021-12-16
US63/290,384 2021-12-16
PCT/US2022/081714 WO2023114944A1 (en) 2021-12-16 2022-12-15 Fluorinated cationic lipids for use in lipid nanoparticles

Publications (3)

Publication Number Publication Date
JP2024546950A JP2024546950A (ja) 2024-12-26
JP2024546950A5 true JP2024546950A5 (https=) 2025-12-12
JPWO2023114944A5 JPWO2023114944A5 (https=) 2025-12-12

Family

ID=85108851

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024535950A Pending JP2024546950A (ja) 2021-12-16 2022-12-15 脂質ナノ粒子に用いるフッ化カチオン性脂質

Country Status (11)

Country Link
US (1) US20250092002A1 (https=)
EP (2) EP4700017A2 (https=)
JP (1) JP2024546950A (https=)
KR (1) KR20240124983A (https=)
CN (1) CN118647601A (https=)
CA (1) CA3242406A1 (https=)
DK (1) DK4448486T3 (https=)
ES (1) ES3058144T3 (https=)
FI (1) FI4448486T3 (https=)
IL (1) IL313487A (https=)
WO (1) WO2023114944A1 (https=)

Families Citing this family (16)

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Publication number Priority date Publication date Assignee Title
US12311033B2 (en) 2023-05-31 2025-05-27 Capstan Therapeutics, Inc. Lipid nanoparticle formulations and compositions
US20250161227A1 (en) 2023-11-17 2025-05-22 Acuitas Therapeutics, Inc. Pegylated lipids
WO2025128696A1 (en) 2023-12-12 2025-06-19 Acuitas Therapeutics, Inc. Cationic lipid compounds for use in lipid nanoparticles
WO2025132122A1 (en) 2023-12-13 2025-06-26 Berlin Institute Of Health Methods of delivering therapeutics using lipid nanoparticles
WO2025126071A1 (en) 2023-12-14 2025-06-19 Pfizer Inc. Rna molecules
WO2025166323A2 (en) 2024-02-02 2025-08-07 Editas Medicine, Inc. Crispr-related methods and compositions targeting lipoprotein (a) expression
WO2025174858A1 (en) 2024-02-15 2025-08-21 Acuitas Therapeutics, Inc. Cationic lipid compounds for use in lipid nanoparticles
TW202543583A (zh) 2024-03-01 2025-11-16 加拿大商阿奎特斯醫療公司 用於將治療劑包覆於脂質奈米顆粒中之材料及方法
WO2025186725A2 (en) 2024-03-06 2025-09-12 Pfizer Inc. Improved lnp formulations and uses thereof
WO2025189064A1 (en) 2024-03-08 2025-09-12 Genzyme Corporation Lipid nanoparticles
WO2025213138A1 (en) 2024-04-05 2025-10-09 Editas Medicine, Inc. Crispr/rna-guided nuclease related methods and compositions for treating primary open angle glaucoma
TW202602839A (zh) 2024-04-10 2026-01-16 加拿大商阿奎特斯醫療公司 用於脂質奈米顆粒之陽離子脂質化合物
WO2025231114A1 (en) 2024-05-01 2025-11-06 Acuitas Therapeutics, Inc. Method of using lipid nanoparticles for intramuscular delivery
WO2025240833A1 (en) 2024-05-17 2025-11-20 Acuitas Therapeutics, Inc. Galnac lipid compounds for use in lipid nanoparticles
WO2026018181A1 (en) 2024-07-17 2026-01-22 Pfizer Inc. Immunogenic compositions and uses thereof
WO2026030375A2 (en) 2024-07-30 2026-02-05 Genzyme Corporation Lipid nanoparticles and methods of manufacture and use thereof

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6197553B1 (en) 1994-07-15 2001-03-06 Merck & Co., Inc. Method for large scale plasmid purification
US7901708B2 (en) 2002-06-28 2011-03-08 Protiva Biotherapeutics, Inc. Liposomal apparatus and manufacturing methods
US9005654B2 (en) 2005-07-27 2015-04-14 Protiva Biotherapeutics, Inc. Systems and methods for manufacturing liposomes
EP2691101A2 (en) 2011-03-31 2014-02-05 Moderna Therapeutics, Inc. Delivery and formulation of engineered nucleic acids
WO2013016058A1 (en) 2011-07-22 2013-01-31 Merck Sharp & Dohme Corp. Novel bis-nitrogen containing cationic lipids for oligonucleotide delivery
US20140308304A1 (en) 2011-12-07 2014-10-16 Alnylam Pharmaceuticals, Inc. Lipids for the delivery of active agents
SMT202200502T1 (it) 2014-06-25 2023-01-13 Acuitas Therapeutics Inc Nuovi lipidi e formulazioni di nanoparticelle lipidiche per l'erogazione di acidi nucleici
LT3313829T (lt) * 2015-06-29 2024-08-12 Acuitas Therapeutics Inc. Lipidai ir lipidų nanodalelių sudėtys, skirtos nukleorūgščių tiekimui
EP3668834B1 (en) * 2017-08-17 2024-10-02 Acuitas Therapeutics, Inc. Lipids for use in lipid nanoparticle formulations
US20200093936A1 (en) * 2018-09-21 2020-03-26 The Trustees Of The University Of Pennsylvania Therapeutic Targeting of Lipid Nanoparticles

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