JP2024542023A5 - - Google Patents

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Publication number
JP2024542023A5
JP2024542023A5 JP2024525636A JP2024525636A JP2024542023A5 JP 2024542023 A5 JP2024542023 A5 JP 2024542023A5 JP 2024525636 A JP2024525636 A JP 2024525636A JP 2024525636 A JP2024525636 A JP 2024525636A JP 2024542023 A5 JP2024542023 A5 JP 2024542023A5
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JP
Japan
Prior art keywords
approximately
gal
composition
months
composition according
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024525636A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024542023A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/079249 external-priority patent/WO2023081781A1/en
Publication of JP2024542023A publication Critical patent/JP2024542023A/ja
Publication of JP2024542023A5 publication Critical patent/JP2024542023A5/ja
Pending legal-status Critical Current

Links

JP2024525636A 2021-11-03 2022-11-03 ファブリー病の治療のためのウイルスベクター構築物の使用方法 Pending JP2024542023A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202163275390P 2021-11-03 2021-11-03
US63/275,390 2021-11-03
US202263373826P 2022-08-29 2022-08-29
US63/373,826 2022-08-29
PCT/US2022/079249 WO2023081781A1 (en) 2021-11-03 2022-11-03 Methods for use of viral vector constructs for the treatment of fabry disease

Publications (2)

Publication Number Publication Date
JP2024542023A JP2024542023A (ja) 2024-11-13
JP2024542023A5 true JP2024542023A5 (https=) 2025-11-11

Family

ID=86242203

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024525636A Pending JP2024542023A (ja) 2021-11-03 2022-11-03 ファブリー病の治療のためのウイルスベクター構築物の使用方法

Country Status (8)

Country Link
US (1) US20250144240A1 (https=)
EP (1) EP4426846A4 (https=)
JP (1) JP2024542023A (https=)
KR (1) KR20240099332A (https=)
AU (1) AU2022381751A1 (https=)
CA (1) CA3236677A1 (https=)
IL (1) IL312548A (https=)
WO (1) WO2023081781A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20240197706A1 (en) * 2022-12-13 2024-06-20 Amicus Therapeutics, Inc. Methods of improving the pharmacokinetics of migalastat

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
KR102712926B1 (ko) * 2016-10-20 2024-10-07 상가모 테라퓨틱스, 인코포레이티드 파브리병의 치료를 위한 방법 및 조성물
CN113423419A (zh) * 2019-01-04 2021-09-21 桑格摩生物治疗股份有限公司 用于治疗法布里病的方法和组合物
EP4103211A4 (en) * 2020-04-27 2023-08-23 4D Molecular Therapeutics Inc. CODON-OPTIMISED GLA GENES AND THEIR USES
MX2023008362A (es) * 2021-01-14 2023-10-04 Spark Therapeutics Inc Composiciones y metodos para el tratamiento de la enfermedad de fabry.

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