JP2024537864A5 - - Google Patents

Info

Publication number
JP2024537864A5
JP2024537864A5 JP2024520855A JP2024520855A JP2024537864A5 JP 2024537864 A5 JP2024537864 A5 JP 2024537864A5 JP 2024520855 A JP2024520855 A JP 2024520855A JP 2024520855 A JP2024520855 A JP 2024520855A JP 2024537864 A5 JP2024537864 A5 JP 2024537864A5
Authority
JP
Japan
Prior art keywords
weight
seq
specifically
weeks
risdiplam
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024520855A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024537864A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/EP2022/077494 external-priority patent/WO2023057404A1/en
Publication of JP2024537864A publication Critical patent/JP2024537864A/ja
Publication of JP2024537864A5 publication Critical patent/JP2024537864A5/ja
Pending legal-status Critical Current

Links

JP2024520855A 2021-10-06 2022-10-04 新規併用投与 Pending JP2024537864A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP21201211.6 2021-10-06
EP21201211 2021-10-06
PCT/EP2022/077494 WO2023057404A1 (en) 2021-10-06 2022-10-04 Novel combined administration

Publications (2)

Publication Number Publication Date
JP2024537864A JP2024537864A (ja) 2024-10-16
JP2024537864A5 true JP2024537864A5 (https=) 2025-11-11

Family

ID=78085538

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024520855A Pending JP2024537864A (ja) 2021-10-06 2022-10-04 新規併用投与

Country Status (5)

Country Link
US (1) US20240358704A1 (https=)
EP (1) EP4426306A1 (https=)
JP (1) JP2024537864A (https=)
CN (1) CN118055767A (https=)
WO (1) WO2023057404A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4601651A1 (en) 2022-10-14 2025-08-20 Genentech, Inc. Methods for treating spinal muscular atrophy
US20250144031A1 (en) * 2023-10-27 2025-05-08 Hoffmann-La Roche Inc. Composition for treating spinal muscular atrophy
CN118045206B (zh) * 2024-04-12 2024-07-05 四川至善唯新生物科技有限公司 一种治疗脊髓型肌肉萎缩的药物组合物及其用途

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6267958B1 (en) 1995-07-27 2001-07-31 Genentech, Inc. Protein formulation
US6171586B1 (en) 1997-06-13 2001-01-09 Genentech, Inc. Antibody formulation
JO3000B1 (ar) 2004-10-20 2016-09-05 Genentech Inc مركبات أجسام مضادة .
SI3143025T1 (sl) 2014-05-15 2020-01-31 F. Hoffmann-La Roche Ag Spojine za zdravljenje spinalne mišične atrofije
KR101860280B1 (ko) 2014-12-19 2018-05-21 추가이 세이야쿠 가부시키가이샤 항-마이오스타틴 항체, 변이체 Fc 영역을 함유하는 폴리펩타이드, 및 사용 방법
JP6659841B2 (ja) 2015-11-12 2020-03-04 エフ.ホフマン−ラ ロシュ アーゲーF. Hoffmann−La Roche Aktiengesellschaft 脊髄性筋萎縮症を処置するための組成物
AR107078A1 (es) 2015-12-18 2018-03-21 Chugai Pharmaceutical Co Ltd Anticuerpo antimiostatina, polipéptidos que contienen regiones fc variantes así como métodos de uso
CN115814077A (zh) * 2016-01-08 2023-03-21 供石公司 抗-原肌生长抑制素/潜伏肌生长抑制素抗体及其使用方法
NZ789269A (en) * 2016-06-13 2026-01-30 Scholar Rock Inc Use of myostatin inhibitors and combination therapies
IL319888A (en) 2018-10-19 2025-05-01 Hoffmann La Roche Forms of pyrido[2,1-A]pyrimidin-4-one derivatives, their formulations and process for their preparation

Similar Documents

Publication Publication Date Title
JP2024537864A5 (https=)
JP2020518599A5 (https=)
JP2023515271A5 (https=)
JP2019534003A5 (https=)
CN103338772A (zh) 用于预防或治疗青光眼的药物疗法
JP2022536469A5 (https=)
EP3982967A1 (en) Methods for treating pulmonary arterial hypertension
JP2022512704A5 (https=)
JP2024540226A5 (https=)
JP2024518536A5 (https=)
JP2021511043A5 (https=)
CN116712539A (zh) 抗her2抗体药物偶联物和抗pd-1抗体联合在制备治疗肿瘤的药物中的用途
JP2021523138A5 (https=)
JP2023511956A5 (https=)
EP4076511A1 (en) Pharmaceutical formulations and dosage regimens for factor xi/xia antibodies
JP2022514561A5 (https=)
JP2021529766A5 (https=)
US20230227555A1 (en) Cd-3 antibodies for the treatment of coronavirus
JP6051315B2 (ja) 乾癬を処置するためのピドチモドの使用
JP2023514567A5 (https=)
JP2023506779A5 (https=)
CN100496500C (zh) 含布那唑嗪和前列腺素的青光眼治疗剂
JP2022536669A5 (https=)
JP2025510725A5 (https=)
WO2024051670A1 (zh) 结合tim-3的抗体与结合pd-1的抗体的药物组合