JP2024528417A5 - - Google Patents

Info

Publication number
JP2024528417A5
JP2024528417A5 JP2023577564A JP2023577564A JP2024528417A5 JP 2024528417 A5 JP2024528417 A5 JP 2024528417A5 JP 2023577564 A JP2023577564 A JP 2023577564A JP 2023577564 A JP2023577564 A JP 2023577564A JP 2024528417 A5 JP2024528417 A5 JP 2024528417A5
Authority
JP
Japan
Prior art keywords
nucleotides
nucleotide
chain
dsrna agent
antisense
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023577564A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024528417A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/034765 external-priority patent/WO2022271972A1/en
Publication of JP2024528417A publication Critical patent/JP2024528417A/ja
Publication of JP2024528417A5 publication Critical patent/JP2024528417A5/ja
Pending legal-status Critical Current

Links

JP2023577564A 2021-06-23 2022-06-23 フィラミンa(flna)をサイレンシングするためのirna組成物および方法 Pending JP2024528417A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202163214220P 2021-06-23 2021-06-23
US63/214,220 2021-06-23
US202163274248P 2021-11-01 2021-11-01
US63/274,248 2021-11-01
PCT/US2022/034765 WO2022271972A1 (en) 2021-06-23 2022-06-23 Irna compositions and methods for silencing filamin a (flna)

Publications (2)

Publication Number Publication Date
JP2024528417A JP2024528417A (ja) 2024-07-30
JP2024528417A5 true JP2024528417A5 (https=) 2025-07-01

Family

ID=84545942

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023577564A Pending JP2024528417A (ja) 2021-06-23 2022-06-23 フィラミンa(flna)をサイレンシングするためのirna組成物および方法

Country Status (4)

Country Link
US (1) US20240301418A1 (https=)
EP (1) EP4359522A4 (https=)
JP (1) JP2024528417A (https=)
WO (1) WO2022271972A1 (https=)

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US9840703B2 (en) * 2013-01-11 2017-12-12 Children's Medical Center Corporation Methods and compositions for the production of siRNAs
EP3171858A4 (en) * 2014-07-24 2018-07-25 Memorial Sloan-Kettering Cancer Center Method and composition for targeted delivery of therapeutic agents
KR101734652B1 (ko) * 2015-06-10 2017-05-11 성균관대학교산학협력단 독소루비신 내성 관련 유전자 및 이의 용도
US20190262469A1 (en) * 2015-09-04 2019-08-29 C. Jeffrey Brinker Protocells to treat microbial infection and for synergistic delivery
MX2020011570A (es) * 2018-05-07 2020-11-24 Alnylam Pharmaceuticals Inc Administracion extrahepatica.
KR20220115995A (ko) * 2019-12-13 2022-08-19 알닐람 파마슈티칼스 인코포레이티드 인간 염색체 9 개방 판독 프레임 72 (C9orf72) iRNA 제제 조성물 및 이의 사용 방법
US20230045629A1 (en) * 2020-01-15 2023-02-09 National University Corporation Tokai National Higher Education And Research System Treatment of progressive supranuclear palsy

Similar Documents

Publication Publication Date Title
JP7805386B2 (ja) Lpa発現を阻害するための組成物及び方法
CN113164509B (zh) 用于抑制17β-HSD 13型(HSD17B13)表达的RNAi试剂、其组合物和使用方法
JP2022515193A5 (https=)
TWI727963B (zh) 甲狀腺素運載蛋白(TTR)iRNA組成物及其治療或預防TTR相關疾病之使用方法
JP2023521604A5 (https=)
JP2024536811A5 (https=)
JP2023523993A5 (https=)
JP2024528503A5 (https=)
CN115397436B (zh) 用于抑制PNPLA3表达的RNAi剂、其药物组合物和使用方法
JP2022518929A (ja) Appの発現を低減するための化合物及び方法
NZ718995A (en) Compositions and methods for inhibiting expression of the alas1 gene
JP2023544385A (ja) Snca関連神経変性疾患を治療又は予防するためのsnca irna組成物及びその使用方法
JP2023544413A5 (https=)
JP2023511434A5 (https=)
JP2024522068A5 (https=)
JP2024509783A5 (https=)
IL294728A (en) lrrk2 RNA material preparations and methods of using them
WO2024008114A1 (zh) 用于抑制补体因子B表达的siRNA、其缀合物和药物组合物及其用途
JP2024508714A5 (https=)
JP2025507372A5 (https=)
WO2023208109A9 (zh) 用于抑制HSD17B13表达的siRNA、其缀合物和药物组合物及其用途
WO2022143531A1 (zh) 一种核酸、含有该核酸的药物组合物与siRNA缀合物及制备方法和用途
JP2024528417A5 (https=)
JP2024521907A5 (https=)
JP2024519293A5 (https=)