JP2024528417A5 - - Google Patents

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Publication number
JP2024528417A5
JP2024528417A5 JP2023577564A JP2023577564A JP2024528417A5 JP 2024528417 A5 JP2024528417 A5 JP 2024528417A5 JP 2023577564 A JP2023577564 A JP 2023577564A JP 2023577564 A JP2023577564 A JP 2023577564A JP 2024528417 A5 JP2024528417 A5 JP 2024528417A5
Authority
JP
Japan
Application number
JP2023577564A
Other languages
Japanese (ja)
Other versions
JPWO2022271972A5 (https=
JP2024528417A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/034765 external-priority patent/WO2022271972A1/en
Publication of JP2024528417A publication Critical patent/JP2024528417A/ja
Publication of JPWO2022271972A5 publication Critical patent/JPWO2022271972A5/ja
Publication of JP2024528417A5 publication Critical patent/JP2024528417A5/ja
Pending legal-status Critical Current

Links

JP2023577564A 2021-06-23 2022-06-23 フィラミンa(flna)をサイレンシングするためのirna組成物および方法 Pending JP2024528417A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202163214220P 2021-06-23 2021-06-23
US63/214,220 2021-06-23
US202163274248P 2021-11-01 2021-11-01
US63/274,248 2021-11-01
PCT/US2022/034765 WO2022271972A1 (en) 2021-06-23 2022-06-23 Irna compositions and methods for silencing filamin a (flna)

Publications (3)

Publication Number Publication Date
JP2024528417A JP2024528417A (ja) 2024-07-30
JPWO2022271972A5 JPWO2022271972A5 (https=) 2025-07-01
JP2024528417A5 true JP2024528417A5 (https=) 2025-07-01

Family

ID=84545942

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023577564A Pending JP2024528417A (ja) 2021-06-23 2022-06-23 フィラミンa(flna)をサイレンシングするためのirna組成物および方法

Country Status (4)

Country Link
US (1) US20240301418A1 (https=)
EP (1) EP4359522A4 (https=)
JP (1) JP2024528417A (https=)
WO (1) WO2022271972A1 (https=)

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2014110205A1 (en) * 2013-01-11 2014-07-17 Children's Medical Center Corporation Methods and compositions for the production of sirnas
WO2016014808A1 (en) * 2014-07-24 2016-01-28 Memorial Sloan Kettering Cancer Center Method and composition for targeted delivery of therapeutic agents
KR101734652B1 (ko) * 2015-06-10 2017-05-11 성균관대학교산학협력단 독소루비신 내성 관련 유전자 및 이의 용도
US20190262469A1 (en) * 2015-09-04 2019-08-29 C. Jeffrey Brinker Protocells to treat microbial infection and for synergistic delivery
WO2019217459A1 (en) * 2018-05-07 2019-11-14 Alnylam Pharmaceuticals, Inc. Extrahepatic delivery
EP4073251A1 (en) * 2019-12-13 2022-10-19 Alnylam Pharmaceuticals, Inc. Human chromosome 9 open reading frame 72 (c9orf72) irna agent compositions and methods of use thereof
JP7721130B2 (ja) * 2020-01-15 2025-08-12 国立大学法人東海国立大学機構 進行性核上性麻痺の治療

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