JP2024520815A5 - - Google Patents
Info
- Publication number
- JP2024520815A5 JP2024520815A5 JP2023575918A JP2023575918A JP2024520815A5 JP 2024520815 A5 JP2024520815 A5 JP 2024520815A5 JP 2023575918 A JP2023575918 A JP 2023575918A JP 2023575918 A JP2023575918 A JP 2023575918A JP 2024520815 A5 JP2024520815 A5 JP 2024520815A5
- Authority
- JP
- Japan
- Prior art keywords
- aav
- sequence
- seq
- item
- cancer
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163202359P | 2021-06-08 | 2021-06-08 | |
| US63/202,359 | 2021-06-08 | ||
| PCT/US2022/032679 WO2022261209A1 (en) | 2021-06-08 | 2022-06-08 | Compositions and methods for treating neurofibromatic disorders |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024520815A JP2024520815A (ja) | 2024-05-24 |
| JP2024520815A5 true JP2024520815A5 (https=) | 2025-06-17 |
Family
ID=84425523
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023575918A Pending JP2024520815A (ja) | 2021-06-08 | 2022-06-08 | 神経線維腫性障害を処置するための組成物および方法 |
Country Status (5)
| Country | Link |
|---|---|
| US (1) | US20230056226A1 (https=) |
| EP (1) | EP4352079A4 (https=) |
| JP (1) | JP2024520815A (https=) |
| CN (1) | CN117813314A (https=) |
| WO (1) | WO2022261209A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3216712A1 (en) * | 2021-04-14 | 2022-10-20 | Research Institute At Nationwide Children's Hospital | Materials and methods for neurofibromin 2/merlin (nf2) gene therapy |
| WO2025054256A1 (en) * | 2023-09-06 | 2025-03-13 | Tenaya Therapeutics, Inc. | Targeting peptides, engineered aav capsid proteins and virions |
| CN118291543A (zh) * | 2024-02-29 | 2024-07-05 | 神拓生物技术(杭州)有限公司 | 一种二型神经纤维瘤基因治疗的慢病毒载体及其应用 |
| WO2025205770A1 (ja) * | 2024-03-26 | 2025-10-02 | 国立大学法人 東京大学 | スタッファーｄｎａを含む組換えプラスミド |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP2345731B1 (en) * | 2003-09-30 | 2015-10-21 | The Trustees of the University of Pennsylvania | Adeno-associated virus (AAV) clades, sequences, vectors containing same, and uses thereof |
| EP2726079A4 (en) * | 2011-06-28 | 2014-12-17 | Glaxosmithkline Ip No 2 Ltd | ADMINISTRATIVE AND TREATMENT PROCEDURES |
| WO2015171270A1 (en) * | 2014-05-06 | 2015-11-12 | Felder Mitchell S | Method for the treatment of neurofibromatosis |
| EP3448874A4 (en) * | 2016-04-29 | 2020-04-22 | Voyager Therapeutics, Inc. | COMPOSITIONS FOR TREATING A DISEASE |
| WO2017191274A2 (en) * | 2016-05-04 | 2017-11-09 | Curevac Ag | Rna encoding a therapeutic protein |
| WO2020012149A1 (en) * | 2018-07-13 | 2020-01-16 | Ucl Business Ltd | Glucocerebrosidase gene therapy |
-
2022
- 2022-06-08 JP JP2023575918A patent/JP2024520815A/ja active Pending
- 2022-06-08 EP EP22820962.3A patent/EP4352079A4/en not_active Withdrawn
- 2022-06-08 WO PCT/US2022/032679 patent/WO2022261209A1/en not_active Ceased
- 2022-06-08 US US17/835,566 patent/US20230056226A1/en not_active Abandoned
- 2022-06-08 CN CN202280049047.XA patent/CN117813314A/zh active Pending
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP2024520815A5 (https=) | ||
| JP7324253B2 (ja) | 補体媒介性疾患を処置するための組成物及び方法 | |
| JP2025000642A5 (https=) | ||
| JP2018513678A (ja) | Ｆｖｉｉｉおよびｆｉｘ用の最適化された肝臓特異的発現系 | |
| RU2018143411A (ru) | Лечение комплемент-опосредуемых расстройств | |
| BR112021012048A2 (pt) | Fator complementar i e cofator de fator complementar i, vetores que codificam os mesmos e uso terapêutico | |
| US20250002546A1 (en) | Vectors for Increasing NPRL2 Expression in Cancer Cells and Methods of Use Thereof | |
| JP2024520815A (ja) | 神経線維腫性障害を処置するための組成物および方法 | |
| CA3173768A1 (en) | Viral vector constructs for delivery of nucleic acids encoding cytokines and uses thereof for treating cancer | |
| KR20260005328A (ko) | 항vegf 단백질을 코딩하는 핵산, 폴리뉴클레오타이드 발현 카세트 및 재조합 아데노 관련 바이러스 | |
| EP4509606A1 (en) | Nucleic acid construct for treating hereditary coagulation factor deficiency and use thereof | |
| CN115927412A (zh) | 密码子优化的补体因子i | |
| JP2023526892A (ja) | バルデー・ビードル症候群の遺伝子治療 | |
| KR102814185B1 (ko) | 라포라병을 예방 또는 치료하기 위한 재조합 아데노 연관 바이러스 및 이를 포함하는 약학적 조성물 | |
| HK40086178A (zh) | 用於治疗补体介导的疾病的组合物和方法 | |
| WO2026055191A1 (en) | Methods and compositions for treating glioblastoma | |
| KR20250080845A (ko) | 라포라병을 예방 또는 치료하기 위한 재조합 아데노 연관 바이러스 및 이를 포함하는 약학적 조성물 |