JP2024520411A5 - - Google Patents
Info
- Publication number
- JP2024520411A5 JP2024520411A5 JP2023572721A JP2023572721A JP2024520411A5 JP 2024520411 A5 JP2024520411 A5 JP 2024520411A5 JP 2023572721 A JP2023572721 A JP 2023572721A JP 2023572721 A JP2023572721 A JP 2023572721A JP 2024520411 A5 JP2024520411 A5 JP 2024520411A5
- Authority
- JP
- Japan
- Prior art keywords
- patient
- approximately
- viral vector
- administered
- weeks
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163192279P | 2021-05-24 | 2021-05-24 | |
| US63/192,279 | 2021-05-24 | ||
| US202163245611P | 2021-09-17 | 2021-09-17 | |
| US63/245,611 | 2021-09-17 | ||
| PCT/US2022/030716 WO2022251208A1 (en) | 2021-05-24 | 2022-05-24 | Compositions and methods for improved treatment of x-linked myotubular myopathy |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024520411A JP2024520411A (ja) | 2024-05-24 |
| JP2024520411A5 true JP2024520411A5 (https=) | 2025-05-30 |
Family
ID=84229086
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023572721A Pending JP2024520411A (ja) | 2021-05-24 | 2022-05-24 | Ｘ連鎖性ミオチュブラーミオパチーの改善された治療のための組成物及び方法 |
Country Status (13)
| Country | Link |
|---|---|
| US (1) | US20240366785A1 (https=) |
| EP (1) | EP4351725A4 (https=) |
| JP (1) | JP2024520411A (https=) |
| KR (1) | KR20240025536A (https=) |
| AU (1) | AU2022283262A1 (https=) |
| BR (1) | BR112023024509A2 (https=) |
| CA (1) | CA3219834A1 (https=) |
| CO (1) | CO2023018156A2 (https=) |
| IL (1) | IL308736A (https=) |
| MX (1) | MX2023013926A (https=) |
| PH (1) | PH12023553216A1 (https=) |
| TW (1) | TW202306589A (https=) |
| WO (1) | WO2022251208A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20240148906A1 (en) * | 2021-03-11 | 2024-05-09 | Audentes Therapeutics, Inc. | Compositions and methods for treating x-linked myotubular myopathy |
Family Cites Families (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2012328526B2 (en) * | 2011-10-28 | 2017-05-25 | Shire Human Genetic Therapies, Inc. | Bile acid recycling inhibitors for treatment of pediatric cholestatic liver diseases |
| US8957044B2 (en) * | 2013-03-01 | 2015-02-17 | Wake Forest University Health Sciences | Systemic gene replacement therapy for treatment of X-linked myotubular myopathy (XLMTM) |
-
2022
- 2022-05-24 PH PH1/2023/553216A patent/PH12023553216A1/en unknown
- 2022-05-24 WO PCT/US2022/030716 patent/WO2022251208A1/en not_active Ceased
- 2022-05-24 IL IL308736A patent/IL308736A/en unknown
- 2022-05-24 CA CA3219834A patent/CA3219834A1/en active Pending
- 2022-05-24 EP EP22811976.4A patent/EP4351725A4/en active Pending
- 2022-05-24 US US18/563,633 patent/US20240366785A1/en active Pending
- 2022-05-24 MX MX2023013926A patent/MX2023013926A/es unknown
- 2022-05-24 BR BR112023024509A patent/BR112023024509A2/pt unknown
- 2022-05-24 KR KR1020237044264A patent/KR20240025536A/ko active Pending
- 2022-05-24 AU AU2022283262A patent/AU2022283262A1/en active Pending
- 2022-05-24 JP JP2023572721A patent/JP2024520411A/ja active Pending
- 2022-05-24 TW TW111119276A patent/TW202306589A/zh unknown
-
2023
- 2023-12-21 CO CONC2023/0018156A patent/CO2023018156A2/es unknown
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