JP2024520411A - Ｘ連鎖性ミオチュブラーミオパチーの改善された治療のための組成物及び方法 - Google Patents

Ｘ連鎖性ミオチュブラーミオパチーの改善された治療のための組成物及び方法 Download PDF

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JP2024520411A
JP2024520411A JP2023572721A JP2023572721A JP2024520411A JP 2024520411 A JP2024520411 A JP 2024520411A JP 2023572721 A JP2023572721 A JP 2023572721A JP 2023572721 A JP2023572721 A JP 2023572721A JP 2024520411 A JP2024520411 A JP 2024520411A
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ミラー，ウェストン
バクテル，ネイサン
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アステラス ジーン セラピーズ，インコーポレーテッド
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JP2023572721A 2021-05-24 2022-05-24 Ｘ連鎖性ミオチュブラーミオパチーの改善された治療のための組成物及び方法 Pending JP2024520411A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202163192279P 2021-05-24 2021-05-24
US63/192,279 2021-05-24
US202163245611P 2021-09-17 2021-09-17
US63/245,611 2021-09-17
PCT/US2022/030716 WO2022251208A1 (en) 2021-05-24 2022-05-24 Compositions and methods for improved treatment of x-linked myotubular myopathy

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JP2024520411A true JP2024520411A (ja) 2024-05-24
JP2024520411A5 JP2024520411A5 (https=) 2025-05-30
JPWO2022251208A5 JPWO2022251208A5 (https=) 2025-05-30

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JP2023572721A Pending JP2024520411A (ja) 2021-05-24 2022-05-24 Ｘ連鎖性ミオチュブラーミオパチーの改善された治療のための組成物及び方法

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US (1) US20240366785A1 (https=)
EP (1) EP4351725A4 (https=)
JP (1) JP2024520411A (https=)
KR (1) KR20240025536A (https=)
AU (1) AU2022283262A1 (https=)
BR (1) BR112023024509A2 (https=)
CA (1) CA3219834A1 (https=)
CO (1) CO2023018156A2 (https=)
IL (1) IL308736A (https=)
MX (1) MX2023013926A (https=)
PH (1) PH12023553216A1 (https=)
TW (1) TW202306589A (https=)
WO (1) WO2022251208A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AR125077A1 (es) * 2021-03-11 2023-06-07 Audentes Therapeutics Inc Composiciones y métodos para tratar la miopatía miotubular ligada a x

Family Cites Families (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN104023727B (zh) * 2011-10-28 2017-04-05 鲁美纳医药公司 用于治疗小儿胆汁淤积性肝病的胆汁酸再循环抑制剂
US8957044B2 (en) * 2013-03-01 2015-02-17 Wake Forest University Health Sciences Systemic gene replacement therapy for treatment of X-linked myotubular myopathy (XLMTM)

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IL308736A (en) 2024-01-01
CA3219834A1 (en) 2022-12-01
AU2022283262A1 (en) 2023-11-23
EP4351725A1 (en) 2024-04-17
MX2023013926A (es) 2024-01-31
AU2022283262A9 (en) 2023-11-30
TW202306589A (zh) 2023-02-16
US20240366785A1 (en) 2024-11-07
KR20240025536A (ko) 2024-02-27
WO2022251208A1 (en) 2022-12-01
EP4351725A4 (en) 2025-04-23
CO2023018156A2 (es) 2024-03-07
BR112023024509A2 (pt) 2024-02-15
PH12023553216A1 (en) 2024-04-29

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