JP2024515902A5 - - Google Patents
Info
- Publication number
- JP2024515902A5 JP2024515902A5 JP2024508819A JP2024508819A JP2024515902A5 JP 2024515902 A5 JP2024515902 A5 JP 2024515902A5 JP 2024508819 A JP2024508819 A JP 2024508819A JP 2024508819 A JP2024508819 A JP 2024508819A JP 2024515902 A5 JP2024515902 A5 JP 2024515902A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- aav
- polypeptide
- amino acid
- nos
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163179968P | 2021-04-26 | 2021-04-26 | |
| US63/179,968 | 2021-04-26 | ||
| PCT/IB2022/053775 WO2022229807A1 (en) | 2021-04-26 | 2022-04-22 | Adeno-associated viral vector capsids with improved tissue tropism |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024515902A JP2024515902A (ja) | 2024-04-10 |
| JP2024515902A5 true JP2024515902A5 (enExample) | 2025-05-01 |
Family
ID=81579930
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024508819A Pending JP2024515902A (ja) | 2021-04-26 | 2022-04-22 | 組織向性が改善されたアデノ随伴ウイルスベクターカプシド |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20250188126A1 (enExample) |
| EP (1) | EP4329820A1 (enExample) |
| JP (1) | JP2024515902A (enExample) |
| CN (1) | CN117377500A (enExample) |
| CA (1) | CA3216420A1 (enExample) |
| WO (1) | WO2022229807A1 (enExample) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN114450411A (zh) | 2019-04-01 | 2022-05-06 | 特纳亚治疗股份有限公司 | 具有工程化衣壳的腺相关病毒 |
| AU2021259422A1 (en) | 2020-04-20 | 2022-12-08 | Tenaya Therapeutics, Inc. | Adeno-associated virus with engineered capsid |
| CN119569834B (zh) * | 2023-09-06 | 2026-06-16 | 北京锦篮基因科技股份有限公司 | 靶向心肌细胞的aav衣壳蛋白变体及其用途 |
Family Cites Families (16)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP4108746B2 (ja) | 1995-06-07 | 2008-06-25 | ユニバーシティ オブ ノース カロライナ アット チャペル ヒル | ヘルパーウイルスを含まないａａｖ産生 |
| EP1696036B1 (en) | 1996-09-06 | 2010-04-21 | The Trustees of The University of Pennsylvania | Use of recombinant adeno-associated virus in the manufacture of a medicament for gene therapy via muscle cells |
| AU4645697A (en) | 1996-09-11 | 1998-04-02 | Government Of The United States Of America, As Represented By The Secretary Of The Department Of Health And Human Services, The | Aav4 vector and uses thereof |
| US6156303A (en) | 1997-06-11 | 2000-12-05 | University Of Washington | Adeno-associated virus (AAV) isolates and AAV vectors derived therefrom |
| US6566118B1 (en) | 1997-09-05 | 2003-05-20 | Targeted Genetics Corporation | Methods for generating high titer helper-free preparations of released recombinant AAV vectors |
| DE69939169D1 (de) | 1998-05-28 | 2008-09-04 | Us Gov Health & Human Serv | Aav5 vektoren und deren verwendung |
| DE69936104T2 (de) | 1998-11-05 | 2008-01-17 | The Trustees Of The University Of Pennsylvania | Nukleinsäuresequenzen des adeno-assoziierten virus des serotyps i, und vektoren und wirtszellen, die diese enthalten |
| EP1135468B1 (en) | 1998-11-10 | 2010-01-06 | University Of North Carolina At Chapel Hill | Virus vectors and methods of making and administering the same |
| EP1668143B1 (en) | 2003-09-30 | 2013-03-20 | The Trustees of The University of Pennsylvania | Adeno-associated virus (aav) clades, sequences, vectors containing same, and uses therefor |
| EP2771455B1 (en) | 2011-10-28 | 2016-10-05 | The University of North Carolina At Chapel Hill | Cell line for production of adeno-associated virus |
| US11136557B2 (en) | 2013-05-31 | 2021-10-05 | The Regents Of The University Of California | Adeno-associated virus variants and methods of use thereof |
| NZ716102A (en) | 2013-07-22 | 2021-12-24 | The Children’S Hospital Of Philadelphia | Variant aav and compositions, methods and uses for gene transfer to cells, organs and tissues |
| GB201403684D0 (en) | 2014-03-03 | 2014-04-16 | King S College London | Vector |
| EP4378487A3 (en) | 2015-06-23 | 2024-09-04 | The Children's Hospital of Philadelphia | Modified factor ix, and compositions, methods and uses for gene transfer to cells, organs and tissues |
| EP3774853A1 (en) * | 2018-03-30 | 2021-02-17 | The Board of Trustees of the Leland Stanford Junior University | Novel recombinant adeno-associated virus capsids with enhanced human pancreatic tropism |
| WO2019222444A2 (en) * | 2018-05-16 | 2019-11-21 | Voyager Therapeutics, Inc. | Directed evolution |
-
2022
- 2022-04-22 CA CA3216420A patent/CA3216420A1/en active Pending
- 2022-04-22 JP JP2024508819A patent/JP2024515902A/ja active Pending
- 2022-04-22 US US18/288,461 patent/US20250188126A1/en active Pending
- 2022-04-22 CN CN202280037194.5A patent/CN117377500A/zh active Pending
- 2022-04-22 WO PCT/IB2022/053775 patent/WO2022229807A1/en not_active Ceased
- 2022-04-22 EP EP22721133.1A patent/EP4329820A1/en active Pending
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