JP2024502620A - リボザイムで活性化されたｒｎａ構築物及びその使用 - Google Patents

リボザイムで活性化されたｒｎａ構築物及びその使用 Download PDF

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JP2024502620A
JP2024502620A JP2023541690A JP2023541690A JP2024502620A JP 2024502620 A JP2024502620 A JP 2024502620A JP 2023541690 A JP2023541690 A JP 2023541690A JP 2023541690 A JP2023541690 A JP 2023541690A JP 2024502620 A JP2024502620 A JP 2024502620A
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ribozyme
rna
sequence
construct
activated
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JP2024502620A5 (enExample
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マリ、プラシャント
ポルテル、アンドリュー
ダイラミー、アミール
クマール、アディティア
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University of California, San Diego
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JP2023541690A 2021-01-11 2022-01-11 リボザイムで活性化されたｒｎａ構築物及びその使用 Pending JP2024502620A (ja)

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US202163136201P 2021-01-11 2021-01-11
US63/136,201 2021-01-11
PCT/US2022/012004 WO2022150773A2 (en) 2021-01-11 2022-01-11 Ribozyme-activated rna constructs and uses thereof

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CN115806984B (zh) * 2022-10-18 2023-10-10 昆明理工大学 环状rna及载体和载体的应用
CN116200442A (zh) * 2023-03-17 2023-06-02 清华大学 一种基于毕赤酵母的无细胞合成体系及应用
CN122206801A (zh) * 2023-10-18 2026-06-12 泰思特治疗公司 反式剪接核酸分子及其使用方法

Citations (1)

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WO2018237372A1 (en) * 2017-06-23 2018-12-27 Cornell University RNA MOLECULES, METHODS FOR PRODUCING CIRCULAR RNA, AND METHODS OF TREATMENT

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EP2476707B1 (en) * 2003-11-14 2017-05-24 Children's Medical Center Corporation Self-cleaving ribozymes and uses thereof
JP5913122B2 (ja) * 2010-11-08 2016-04-27 Ｊｃｒファーマ株式会社 新規発現ベクター
MY198399A (en) * 2016-02-02 2023-08-28 Meiragtx Uk Ii Ltd Regulation of gene expression via aptamer-mediated control of self-cleaving ribozymes
SG11202111264TA (en) * 2019-04-12 2021-11-29 Agency Science Tech & Res A ribozyme comprising a target-binding domain
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EP3986458A1 (en) * 2019-06-20 2022-04-27 Janssen Sciences Ireland Unlimited Company Self-replicating rna molecules for hepatitis b virus (hbv) vaccines and uses thereof
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EP4158017A1 (en) * 2020-05-26 2023-04-05 Shape Therapeutics Inc. Engineered circular polynucleotides
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WO2018237372A1 (en) * 2017-06-23 2018-12-27 Cornell University RNA MOLECULES, METHODS FOR PRODUCING CIRCULAR RNA, AND METHODS OF TREATMENT

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CHEMBIOCHEM, vol. 9, JPN6026009394, 2008, pages 206 - 209, ISSN: 0005813038 *

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WO2022150773A2 (en) 2022-07-14
WO2022150773A3 (en) 2022-08-11
US20260115275A1 (en) 2026-04-30
EP4247946A4 (en) 2025-03-26
EP4247946A2 (en) 2023-09-27

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