JP2024084670A5 - - Google Patents
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- Publication number
- JP2024084670A5 JP2024084670A5 JP2023090210A JP2023090210A JP2024084670A5 JP 2024084670 A5 JP2024084670 A5 JP 2024084670A5 JP 2023090210 A JP2023090210 A JP 2023090210A JP 2023090210 A JP2023090210 A JP 2023090210A JP 2024084670 A5 JP2024084670 A5 JP 2024084670A5
- Authority
- JP
- Japan
- Prior art keywords
- formulation
- migalastat
- salt
- patient
- caffeine
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025169972A JP2026031546A (ja) | 2022-12-13 | 2025-10-08 | ミガラスタットの薬物動態を改善する方法 |
Applications Claiming Priority (4)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202263432235P | 2022-12-13 | 2022-12-13 | |
| US63/432,235 | 2022-12-13 | ||
| US18/315,928 US20240197706A1 (en) | 2022-12-13 | 2023-05-11 | Methods of improving the pharmacokinetics of migalastat |
| US18/315,928 | 2023-05-11 |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025169972A Division JP2026031546A (ja) | 2022-12-13 | 2025-10-08 | ミガラスタットの薬物動態を改善する方法 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2024084670A JP2024084670A (ja) | 2024-06-25 |
| JP2024084670A5 true JP2024084670A5 (https=) | 2025-04-23 |
| JP7757345B2 JP7757345B2 (ja) | 2025-10-21 |
Family
ID=86646511
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023090210A Active JP7757345B2 (ja) | 2022-12-13 | 2023-05-31 | ミガラスタットの薬物動態を改善する方法 |
| JP2025169972A Pending JP2026031546A (ja) | 2022-12-13 | 2025-10-08 | ミガラスタットの薬物動態を改善する方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025169972A Pending JP2026031546A (ja) | 2022-12-13 | 2025-10-08 | ミガラスタットの薬物動態を改善する方法 |
Country Status (23)
| Country | Link |
|---|---|
| US (1) | US20240197706A1 (https=) |
| EP (2) | EP4667050A3 (https=) |
| JP (2) | JP7757345B2 (https=) |
| KR (1) | KR20240094973A (https=) |
| AU (1) | AU2023396459A1 (https=) |
| CA (1) | CA3201512A1 (https=) |
| CL (1) | CL2025001743A1 (https=) |
| CO (1) | CO2025009079A2 (https=) |
| DE (1) | DE202023003007U1 (https=) |
| DK (1) | DK4385509T3 (https=) |
| ES (1) | ES3055214T3 (https=) |
| FI (1) | FI4385509T3 (https=) |
| HR (1) | HRP20251472T1 (https=) |
| IL (1) | IL321404A (https=) |
| LT (1) | LT4385509T (https=) |
| MX (1) | MX2025006897A (https=) |
| PL (1) | PL4385509T3 (https=) |
| PT (1) | PT4385509T (https=) |
| RS (1) | RS67478B1 (https=) |
| SI (1) | SI4385509T1 (https=) |
| SM (1) | SMT202500453T1 (https=) |
| TW (1) | TW202423436A (https=) |
| WO (1) | WO2024129220A1 (https=) |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6274597B1 (en) | 1998-06-01 | 2001-08-14 | Mount Sinai School Of Medicine Of New York University | Method of enhancing lysosomal α-Galactosidase A |
| AU2008232614A1 (en) | 2007-03-30 | 2008-10-09 | Amicus Therapeutics, Inc. | Method for the treatment of Fabry disease using pharmacological chaperones |
| US9999618B2 (en) * | 2007-04-26 | 2018-06-19 | Amicus Therapeutics, Inc. | Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones |
| SI3470077T1 (sl) | 2008-02-12 | 2020-12-31 | Amicus Therapeutics, Inc. | Postopek za napovedovanje odgovora na zdravljenje bolezni s farmakološkim spremljevalcem |
| CN103974619B (zh) * | 2011-03-11 | 2017-02-15 | 阿米库斯治疗学公司 | 治疗法布里病的给药方案 |
| EP4426846A4 (en) * | 2021-11-03 | 2025-11-05 | Sangamo Therapeutics Inc | METHODS OF USING VIRAL VECTOR CONSTRUCTIONS FOR THE TREATMENT OF FABRY DISEASE |
-
2023
- 2023-05-11 US US18/315,928 patent/US20240197706A1/en active Pending
- 2023-05-31 SM SM20250453T patent/SMT202500453T1/it unknown
- 2023-05-31 IL IL321404A patent/IL321404A/en unknown
- 2023-05-31 WO PCT/US2023/067656 patent/WO2024129220A1/en not_active Ceased
- 2023-05-31 SI SI202330057T patent/SI4385509T1/sl unknown
- 2023-05-31 ES ES23176366T patent/ES3055214T3/es active Active
- 2023-05-31 EP EP25199386.1A patent/EP4667050A3/en active Pending
- 2023-05-31 HR HRP20251472TT patent/HRP20251472T1/hr unknown
- 2023-05-31 LT LTEP23176366.5T patent/LT4385509T/lt unknown
- 2023-05-31 DK DK23176366.5T patent/DK4385509T3/da active
- 2023-05-31 PL PL23176366.5T patent/PL4385509T3/pl unknown
- 2023-05-31 TW TW112120343A patent/TW202423436A/zh unknown
- 2023-05-31 RS RS20251212A patent/RS67478B1/sr unknown
- 2023-05-31 AU AU2023396459A patent/AU2023396459A1/en active Pending
- 2023-05-31 EP EP23176366.5A patent/EP4385509B1/en active Active
- 2023-05-31 CA CA3201512A patent/CA3201512A1/en active Pending
- 2023-05-31 FI FIEP23176366.5T patent/FI4385509T3/fi active
- 2023-05-31 KR KR1020230070371A patent/KR20240094973A/ko not_active Ceased
- 2023-05-31 JP JP2023090210A patent/JP7757345B2/ja active Active
- 2023-05-31 DE DE202023003007.2U patent/DE202023003007U1/de active Active
- 2023-05-31 PT PT231763665T patent/PT4385509T/pt unknown
-
2025
- 2025-06-12 CL CL2025001743A patent/CL2025001743A1/es unknown
- 2025-06-12 MX MX2025006897A patent/MX2025006897A/es unknown
- 2025-07-03 CO CONC2025/0009079A patent/CO2025009079A2/es unknown
- 2025-10-08 JP JP2025169972A patent/JP2026031546A/ja active Pending
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