JP2023526311A5 - - Google Patents
Info
- Publication number
- JP2023526311A5 JP2023526311A5 JP2022569267A JP2022569267A JP2023526311A5 JP 2023526311 A5 JP2023526311 A5 JP 2023526311A5 JP 2022569267 A JP2022569267 A JP 2022569267A JP 2022569267 A JP2022569267 A JP 2022569267A JP 2023526311 A5 JP2023526311 A5 JP 2023526311A5
- Authority
- JP
- Japan
- Prior art keywords
- pharmaceutical composition
- composition according
- patient
- brain mass
- administered
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063023459P | 2020-05-12 | 2020-05-12 | |
| US63/023,459 | 2020-05-12 | ||
| US202063070653P | 2020-08-26 | 2020-08-26 | |
| US63/070,653 | 2020-08-26 | ||
| US202063073756P | 2020-09-02 | 2020-09-02 | |
| US63/073,756 | 2020-09-02 | ||
| PCT/US2021/031802 WO2021231443A1 (en) | 2020-05-12 | 2021-05-11 | Compositions useful in treatment of krabbe disease |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2023526311A JP2023526311A (ja) | 2023-06-21 |
| JP2023526311A5 true JP2023526311A5 (OSRAM) | 2024-05-22 |
| JP7832898B2 JP7832898B2 (ja) | 2026-03-18 |
Family
ID=76284168
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022569267A Active JP7832898B2 (ja) | 2020-05-12 | 2021-05-11 | クラッベ病の治療に有用な組成物 |
Country Status (13)
| Country | Link |
|---|---|
| US (1) | US20230210941A1 (OSRAM) |
| EP (1) | EP4149564A1 (OSRAM) |
| JP (1) | JP7832898B2 (OSRAM) |
| KR (1) | KR20230023637A (OSRAM) |
| CN (1) | CN116057175A (OSRAM) |
| AU (1) | AU2021271635A1 (OSRAM) |
| BR (1) | BR112022021786A2 (OSRAM) |
| CA (1) | CA3177924A1 (OSRAM) |
| CO (1) | CO2022017953A2 (OSRAM) |
| IL (1) | IL298137A (OSRAM) |
| MX (1) | MX2022014245A (OSRAM) |
| TW (1) | TW202208622A (OSRAM) |
| WO (1) | WO2021231443A1 (OSRAM) |
Family Cites Families (24)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US1967872A (en) | 1930-07-14 | 1934-07-24 | Gilbert E Doan | Welding electrode |
| JP2002521107A (ja) | 1998-07-23 | 2002-07-16 | コーニンクレッカ フィリップス エレクトロニクス エヌ ヴィ | 高解像度画像センサを備えたｘ線検査装置 |
| EP2369002A1 (en) | 1999-08-09 | 2011-09-28 | Targeted Genetics Corporation | Enhancement of expression of a single-stranded, heterologous nucleotide sequence from recombinant viral vectors by designing the sequence such that it forms intrastrand base pairs |
| SG10202108118RA (en) | 2001-11-13 | 2021-08-30 | Univ Pennsylvania | A method of detecting and/or identifying adeno-associated virus (aav) sequences and isolating novel sequences identified thereby |
| US8005620B2 (en) | 2003-08-01 | 2011-08-23 | Dna Twopointo Inc. | Systems and methods for biopolymer engineering |
| WO2005013090A2 (en) | 2003-08-01 | 2005-02-10 | Dna Twopointo Inc. | Systems and methods for biopolymer engineering |
| HUE054805T2 (hu) | 2003-09-30 | 2021-09-28 | Univ Pennsylvania | Adeno-asszociált vírus (AAV) kládok, szekvenciák, az azokat tartalmazó vektorok és alkalmazásaik |
| EP3085389A1 (en) | 2005-04-07 | 2016-10-26 | The Trustees Of The University Of Pennsylvania | Method of increasing the function of an aav vector |
| WO2006132118A1 (ja) | 2005-06-09 | 2006-12-14 | Matsushita Electric Industrial Co., Ltd. | 振幅誤差補償装置及び直交度誤差補償装置 |
| WO2007120542A2 (en) | 2006-03-30 | 2007-10-25 | The Board Of Trustees Of The Leland Stanford Junior University | Aav capsid library and aav capsid proteins |
| WO2010138263A2 (en) | 2009-05-28 | 2010-12-02 | University Of Massachusetts | Novel aav 's and uses thereof |
| KR20130040844A (ko) | 2010-03-29 | 2013-04-24 | 더 트러스티스 오브 더 유니버시티 오브 펜실바니아 | 약학적으로 유발된 전이유전자 제거 시스템 |
| US8927514B2 (en) | 2010-04-30 | 2015-01-06 | City Of Hope | Recombinant adeno-associated vectors for targeted treatment |
| WO2011163651A2 (en) * | 2010-06-25 | 2011-12-29 | Shire Human Genetic Therapies, Inc. | METHODS AND COMPOSITIONS FOR CNS DELIVERY OF β-GALACTOCEREBROSIDASE |
| FR2977562B1 (fr) | 2011-07-06 | 2016-12-23 | Gaztransport Et Technigaz | Cuve etanche et thermiquement isolante integree dans une structure porteuse |
| WO2015012924A2 (en) | 2013-04-29 | 2015-01-29 | The Trustees Of The University Of Pennsylvania | Tissue preferential codon modified expression cassettes, vectors containing same, and use thereof |
| AU2015320694B2 (en) | 2014-09-24 | 2021-11-11 | City Of Hope | Adeno-associated virus vector variants for high efficiency genome editing and methods thereof |
| WO2017180936A1 (en) | 2016-04-15 | 2017-10-19 | The Trustees Of The University Of Pennsylvania | Compositions for treatment of wet age-related macular degeneration |
| JP2020505317A (ja) | 2017-01-20 | 2020-02-20 | ユニバーシティ オブ ピッツバーグ − オブ ザ コモンウェルス システム オブ ハイヤー エデュケイション | 臍帯血移植（ｕｃｂｔ）および増加したガラクトセレブロシダーゼの発現によるクラッベ病の処置 |
| MX2019010275A (es) | 2017-02-28 | 2019-10-15 | Univ Pennsylvania | Novedoso vector del subtipo f del virus adenoasociado (aav) y usos de este. |
| WO2018160852A1 (en) | 2017-03-03 | 2018-09-07 | Cook Medical Technologies, LLC | Rapid exchange multiple catheter system |
| CN112553210B (zh) * | 2017-10-03 | 2024-09-24 | 普利维尔治疗公司 | 用于溶酶体障碍的基因疗法 |
| WO2020072835A1 (en) | 2018-10-03 | 2020-04-09 | Siteone Therapeutics, Inc. | 11,13-modified saxitoxins for the treatment of pain |
| SG11202108480UA (en) * | 2019-02-26 | 2021-09-29 | Univ Pennsylvania | Compositions useful in treatment of krabbe disease |
-
2021
- 2021-05-11 US US17/998,330 patent/US20230210941A1/en active Pending
- 2021-05-11 CA CA3177924A patent/CA3177924A1/en active Pending
- 2021-05-11 MX MX2022014245A patent/MX2022014245A/es unknown
- 2021-05-11 CN CN202180049138.9A patent/CN116057175A/zh active Pending
- 2021-05-11 EP EP21730355.1A patent/EP4149564A1/en active Pending
- 2021-05-11 WO PCT/US2021/031802 patent/WO2021231443A1/en not_active Ceased
- 2021-05-11 BR BR112022021786A patent/BR112022021786A2/pt unknown
- 2021-05-11 AU AU2021271635A patent/AU2021271635A1/en active Pending
- 2021-05-11 IL IL298137A patent/IL298137A/en unknown
- 2021-05-11 KR KR1020227042731A patent/KR20230023637A/ko active Pending
- 2021-05-11 JP JP2022569267A patent/JP7832898B2/ja active Active
- 2021-05-11 TW TW110116911A patent/TW202208622A/zh unknown
-
2022
- 2022-12-12 CO CONC2022/0017953A patent/CO2022017953A2/es unknown
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