JP2022539569A5 - - Google Patents
Info
- Publication number
- JP2022539569A5 JP2022539569A5 JP2021577896A JP2021577896A JP2022539569A5 JP 2022539569 A5 JP2022539569 A5 JP 2022539569A5 JP 2021577896 A JP2021577896 A JP 2021577896A JP 2021577896 A JP2021577896 A JP 2021577896A JP 2022539569 A5 JP2022539569 A5 JP 2022539569A5
- Authority
- JP
- Japan
- Prior art keywords
- promoter
- dual
- vector system
- grna
- vector
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962870488P | 2019-07-03 | 2019-07-03 | |
| US62/870,488 | 2019-07-03 | ||
| PCT/US2020/040608 WO2021003337A1 (en) | 2019-07-03 | 2020-07-02 | Compositions and methods for gene replacement |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022539569A JP2022539569A (ja) | 2022-09-12 |
| JP2022539569A5 true JP2022539569A5 (enExample) | 2023-06-30 |
| JP7724721B2 JP7724721B2 (ja) | 2025-08-18 |
Family
ID=74101132
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021577896A Active JP7724721B2 (ja) | 2019-07-03 | 2020-07-02 | 遺伝子置換のための組成物および方法 |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20220395583A1 (enExample) |
| EP (1) | EP3994254A4 (enExample) |
| JP (1) | JP7724721B2 (enExample) |
| AU (1) | AU2020298549A1 (enExample) |
| CA (1) | CA3145289A1 (enExample) |
| WO (1) | WO2021003337A1 (enExample) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2022221397A2 (en) * | 2021-04-14 | 2022-10-20 | Capsida, Inc. | Plasmids and methods of production of adeno-associated viruses |
| CN113584082B (zh) * | 2021-06-22 | 2023-07-25 | 复旦大学附属眼耳鼻喉科医院 | CRISPR/Cas9基因编辑系统及其在制备治疗遗传性感音神经性聋的药物中的应用 |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US11028388B2 (en) * | 2014-03-05 | 2021-06-08 | Editas Medicine, Inc. | CRISPR/Cas-related methods and compositions for treating Usher syndrome and retinitis pigmentosa |
| US9758781B2 (en) * | 2014-09-30 | 2017-09-12 | University Of Iowa Research Foundation | Methods to prevent and treat autosomal dominant non-syndromic hearing loss |
| WO2016094872A1 (en) * | 2014-12-12 | 2016-06-16 | The Broad Institute Inc. | Dead guides for crispr transcription factors |
| JP6817215B2 (ja) * | 2015-03-03 | 2021-01-20 | ザ ジェネラル ホスピタル コーポレイション | 変更ＰＡＭ特異性を有する遺伝子操作ＣＲＩＳＰＲ−Ｃａｓ９ヌクレアーゼ |
| JP6851319B2 (ja) * | 2015-04-27 | 2021-03-31 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | ヒト疾患のＣＲＩＳＰＲ／Ｃａｓ９媒介性の修正のためのデュアルＡＡＶベクター系 |
| EP3353296B1 (en) * | 2015-09-24 | 2020-11-04 | Editas Medicine, Inc. | Use of exonucleases to improve crispr/cas-mediated genome editing |
-
2020
- 2020-07-02 WO PCT/US2020/040608 patent/WO2021003337A1/en not_active Ceased
- 2020-07-02 US US17/624,145 patent/US20220395583A1/en active Pending
- 2020-07-02 CA CA3145289A patent/CA3145289A1/en active Pending
- 2020-07-02 JP JP2021577896A patent/JP7724721B2/ja active Active
- 2020-07-02 EP EP20834446.5A patent/EP3994254A4/en active Pending
- 2020-07-02 AU AU2020298549A patent/AU2020298549A1/en active Pending
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