JP2022525888A - リソソーム蓄積症のための、経鼻遺伝子送達と経口の桂皮酸、オレアミド、またはゲムフィブロジルとの組合せ - Google Patents

リソソーム蓄積症のための、経鼻遺伝子送達と経口の桂皮酸、オレアミド、またはゲムフィブロジルとの組合せ Download PDF

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JP2022525888A
JP2022525888A JP2021555592A JP2021555592A JP2022525888A JP 2022525888 A JP2022525888 A JP 2022525888A JP 2021555592 A JP2021555592 A JP 2021555592A JP 2021555592 A JP2021555592 A JP 2021555592A JP 2022525888 A JP2022525888 A JP 2022525888A
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カリパーダ パハン，
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ラッシュ・ユニバーシティ・メディカル・センター
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JP2021555592A 2019-03-22 2020-03-20 リソソーム蓄積症のための、経鼻遺伝子送達と経口の桂皮酸、オレアミド、またはゲムフィブロジルとの組合せ Pending JP2022525888A (ja)

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US201962822310P 2019-03-22 2019-03-22
US62/822,310 2019-03-22
PCT/US2020/023768 WO2020197967A1 (en) 2019-03-22 2020-03-20 Combination of nasal gene delivery and oral cinnamic acid, oleamide or gemfibrozil for lysosomal stoarge disorders

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JP2022525888A true JP2022525888A (ja) 2022-05-20
JPWO2020197967A5 JPWO2020197967A5 (https=) 2023-03-28
JP2022525888A5 JP2022525888A5 (https=) 2023-03-28

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US (1) US20220152165A1 (https=)
EP (1) EP3941584A4 (https=)
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KR (1) KR20210143848A (https=)
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CA (1) CA3132379A1 (https=)
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JP2026504932A (ja) * 2023-01-18 2026-02-10 ラッシュ・ユニバーシティ・メディカル・センター Ｃｌｎ３関連若年型神経セロイドリポフスチン症の治療のための経口ゲムフィブロジル

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