JP2022525888A5 - - Google Patents
Info
- Publication number
- JP2022525888A5 JP2022525888A5 JP2021555592A JP2021555592A JP2022525888A5 JP 2022525888 A5 JP2022525888 A5 JP 2022525888A5 JP 2021555592 A JP2021555592 A JP 2021555592A JP 2021555592 A JP2021555592 A JP 2021555592A JP 2022525888 A5 JP2022525888 A5 JP 2022525888A5
- Authority
- JP
- Japan
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962822310P | 2019-03-22 | 2019-03-22 | |
| US62/822,310 | 2019-03-22 | ||
| PCT/US2020/023768 WO2020197967A1 (en) | 2019-03-22 | 2020-03-20 | Combination of nasal gene delivery and oral cinnamic acid, oleamide or gemfibrozil for lysosomal stoarge disorders |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022525888A JP2022525888A (ja) | 2022-05-20 |
| JPWO2020197967A5 JPWO2020197967A5 (https=) | 2023-03-28 |
| JP2022525888A5 true JP2022525888A5 (https=) | 2023-03-28 |
Family
ID=72609912
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021555592A Pending JP2022525888A (ja) | 2019-03-22 | 2020-03-20 | リソソーム蓄積症のための、経鼻遺伝子送達と経口の桂皮酸、オレアミド、またはゲムフィブロジルとの組合せ |
Country Status (9)
| Country | Link |
|---|---|
| US (1) | US20220152165A1 (https=) |
| EP (1) | EP3941584A4 (https=) |
| JP (1) | JP2022525888A (https=) |
| KR (1) | KR20210143848A (https=) |
| CN (1) | CN113811359A (https=) |
| AU (1) | AU2020245415B2 (https=) |
| CA (1) | CA3132379A1 (https=) |
| EA (1) | EA202192328A1 (https=) |
| WO (1) | WO2020197967A1 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3121785A1 (en) * | 2018-12-05 | 2020-06-11 | Washington University | Methods of detecting, preventing, reversing, and treating neurological diseases |
| CN116723870A (zh) * | 2021-01-20 | 2023-09-08 | 拉什大学医学中心 | 球形细胞脑白质营养不良症或克拉伯病的改良治疗 |
| JP2026504932A (ja) * | 2023-01-18 | 2026-02-10 | ラッシュ・ユニバーシティ・メディカル・センター | Ｃｌｎ３関連若年型神経セロイドリポフスチン症の治療のための経口ゲムフィブロジル |
Family Cites Families (15)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN100402026C (zh) * | 2002-06-03 | 2008-07-16 | 诺瓦提斯公司 | 取代的氰基吡咯烷和含有它们的组合制剂用于治疗高脂血症和相关疾病的用途 |
| WO2008049058A2 (en) * | 2006-10-18 | 2008-04-24 | Cornell Research Foundation, Inc. | Cln2 treatment of alzheimer's disease |
| WO2012177997A1 (en) * | 2011-06-22 | 2012-12-27 | The General Hospital Corporation | Treatment of proteinopathies |
| WO2014089449A1 (en) * | 2012-12-07 | 2014-06-12 | Rush University Nedical Center | Composition and method for treating neuronal ceroid lipofuscinosis |
| WO2016081365A1 (en) * | 2014-11-19 | 2016-05-26 | Rush University Medical Center | Compositions and methods for treating lysosomal disorders |
| CN107249646B (zh) * | 2014-12-16 | 2021-06-29 | 内布拉斯加大学董事会 | 用于青少年巴滕病的基因疗法 |
| HK1256341A1 (zh) * | 2015-05-15 | 2019-09-20 | 明尼苏达大学董事会 | 用於治疗性递送到中枢神经系统的腺相关物 |
| US20180236105A1 (en) * | 2015-10-23 | 2018-08-23 | University Of Iowa Research Foundation | Methods for treating neurodegenerative diseases using gene therapy to delay disease onset and progression while providing cognitive protection |
| US11045557B2 (en) * | 2016-06-09 | 2021-06-29 | Queen's University At Kingston | Methods and gene therapy constructs for treating GM2 gangliosidoses |
| US20220323612A1 (en) * | 2016-06-13 | 2022-10-13 | Bluebird Bio, Inc. | Gene therapy of neuronal ceroid lipofuscinoses |
| RU2764919C2 (ru) * | 2016-06-13 | 2022-01-24 | Дзе Юниверсити Оф Норт Каролина Эт Чепел Хилл | Оптимизированные гены и экспрессионные кассеты cln1, и их применение |
| BR112019010210A2 (pt) * | 2016-12-29 | 2019-09-03 | Rush University Medical Center | melhora na atividade locomotora e aumento da longevidade de indivíduos com lipofuscinose ceroide neuronal infantil tardia por gemfibrozil |
| US12599636B2 (en) * | 2017-01-20 | 2026-04-14 | University of Pittsburgh—of the Commonwealth System of Higher Education | Treatment of Krabbe disease with umbilical cord blood transplantion (UCBT) and increased galactocerebrosidase (GALC) expression |
| US12454701B2 (en) * | 2018-12-05 | 2025-10-28 | Abeona Therapeutics Inc. | Recombinant adeno-associated viral vector for gene delivery |
| MX2021009250A (es) * | 2019-02-01 | 2021-11-04 | Spark Therapeutics Inc | Metodos de tratamiento por vectores aav para la lipofuscinosis ceroidea neuronal infantil tardia tipo 2. |
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2020
- 2020-03-20 KR KR1020217034175A patent/KR20210143848A/ko active Pending
- 2020-03-20 WO PCT/US2020/023768 patent/WO2020197967A1/en not_active Ceased
- 2020-03-20 EP EP20777092.6A patent/EP3941584A4/en not_active Withdrawn
- 2020-03-20 CA CA3132379A patent/CA3132379A1/en active Pending
- 2020-03-20 JP JP2021555592A patent/JP2022525888A/ja active Pending
- 2020-03-20 CN CN202080022852.4A patent/CN113811359A/zh active Pending
- 2020-03-20 US US17/441,029 patent/US20220152165A1/en active Pending
- 2020-03-20 EA EA202192328A patent/EA202192328A1/ru unknown
- 2020-03-20 AU AU2020245415A patent/AU2020245415B2/en active Active