JP2022512667A5 - - Google Patents

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Publication number
JP2022512667A5
JP2022512667A5 JP2021519805A JP2021519805A JP2022512667A5 JP 2022512667 A5 JP2022512667 A5 JP 2022512667A5 JP 2021519805 A JP2021519805 A JP 2021519805A JP 2021519805 A JP2021519805 A JP 2021519805A JP 2022512667 A5 JP2022512667 A5 JP 2022512667A5
Authority
JP
Japan
Prior art keywords
vector
gene therapy
promoter
therapy vector
seq
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2021519805A
Other languages
English (en)
Japanese (ja)
Other versions
JP2022512667A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/055635 external-priority patent/WO2020077091A1/en
Publication of JP2022512667A publication Critical patent/JP2022512667A/ja
Publication of JP2022512667A5 publication Critical patent/JP2022512667A5/ja
Pending legal-status Critical Current

Links

JP2021519805A 2018-10-10 2019-10-10 Kir7.1遺伝子療法ベクターおよびその使用方法 Pending JP2022512667A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862743623P 2018-10-10 2018-10-10
US62/743,623 2018-10-10
PCT/US2019/055635 WO2020077091A1 (en) 2018-10-10 2019-10-10 Kir 7.1 gene therapy vectors and methods of using the same

Publications (2)

Publication Number Publication Date
JP2022512667A JP2022512667A (ja) 2022-02-07
JP2022512667A5 true JP2022512667A5 (https=) 2022-11-09

Family

ID=70164038

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021519805A Pending JP2022512667A (ja) 2018-10-10 2019-10-10 Kir7.1遺伝子療法ベクターおよびその使用方法

Country Status (9)

Country Link
US (1) US20210348196A1 (https=)
EP (1) EP3864160A4 (https=)
JP (1) JP2022512667A (https=)
CN (1) CN113227386A (https=)
AU (1) AU2019357602A1 (https=)
CA (1) CA3115782A1 (https=)
IL (1) IL282181A (https=)
JO (1) JOP20210067A1 (https=)
WO (1) WO2020077091A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20230108025A1 (en) * 2020-03-13 2023-04-06 Wisconsin Alumni Research Foundation Kir 7.1 gene therapy vectors and methods of using the same

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP0922763A1 (en) * 1997-12-12 1999-06-16 Synthelabo Inwardly rectifying potassium channel gene and protein
US6399761B1 (en) * 1998-08-07 2002-06-04 Icagen, Inc. Nucleic acid encoding human potassium channel K+ nov1 protein
WO2011068801A2 (en) * 2009-12-01 2011-06-09 The Rockefeller University Methods for identifying compounds that modulate ion channel activity of a kir channel
US9567376B2 (en) * 2013-02-08 2017-02-14 The Trustees Of The University Of Pennsylvania Enhanced AAV-mediated gene transfer for retinal therapies
AU2014305218B2 (en) * 2013-08-05 2020-01-16 Academisch Ziekenhuis Leiden H.O.D.N. Leids Universitair Medisch Centrum Recombinant AAV-Crumbs homologue composition and methods for treating LCA-8 and progressive RP
LT3137497T (lt) * 2014-05-02 2021-07-26 Genzyme Corporation Aav vektoriai, skirti tinklainės ir cns genų terapijai
GB201519086D0 (en) * 2015-10-28 2015-12-09 Syncona Partners Llp Gene Therapy
US11364308B2 (en) * 2016-05-13 2022-06-21 4D Molecular Therapeutics Inc. Adeno-associated virus variant capsids and methods of use thereof
JP7086928B2 (ja) * 2016-07-25 2022-06-20 ザ ユナイテッド ステイツ オブ アメリカ, アズ リプレゼンテッド バイ ザ セクレタリー, デパートメント オブ ヘルス アンド ヒューマン サービシーズ 改変されたナチュラルキラー細胞を生成する方法および使用方法

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