JP2022505381A - アルファ１アンチトリプシン欠乏症を治療するための組成物及び方法 - Google Patents

アルファ１アンチトリプシン欠乏症を治療するための組成物及び方法 Download PDF

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JP2022505381A
JP2022505381A JP2021521383A JP2021521383A JP2022505381A JP 2022505381 A JP2022505381 A JP 2022505381A JP 2021521383 A JP2021521383 A JP 2021521383A JP 2021521383 A JP2021521383 A JP 2021521383A JP 2022505381 A JP2022505381 A JP 2022505381A
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sequence
aat
rna
seq
nucleic acid
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ダグラス フィン，ジョナサン
フアン，ホン－レン
フォーゲット，アンソニー
シエ，シン
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インテリア セラピューティクス，インコーポレーテッド
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JP2021521383A 2018-10-18 2019-10-18 アルファ１アンチトリプシン欠乏症を治療するための組成物及び方法 Pending JP2022505381A (ja)

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US201862747522P 2018-10-18 2018-10-18
US62/747,522 2018-10-18
PCT/US2019/057092 WO2020082047A1 (en) 2018-10-18 2019-10-18 Compositions and methods for treating alpha-1 antitrypsin deficiencey

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IL282237A (en) 2021-05-31
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PH12021550842A1 (en) 2021-12-06
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