JP2021500029A - Ｎｔ−３遺伝子治療のための方法及び材料 - Google Patents

Ｎｔ−３遺伝子治療のための方法及び材料 Download PDF

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JP2021500029A
JP2021500029A JP2020522007A JP2020522007A JP2021500029A JP 2021500029 A JP2021500029 A JP 2021500029A JP 2020522007 A JP2020522007 A JP 2020522007A JP 2020522007 A JP2020522007 A JP 2020522007A JP 2021500029 A JP2021500029 A JP 2021500029A
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raav
nucleic acid
polypeptide
tmck
ntf3
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JP2021500029A5 (enExample
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ザリフェ サヘンク，
ザリフェ サヘンク，
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リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル
リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル
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Publication of JP2021500029A publication Critical patent/JP2021500029A/ja
Publication of JP2021500029A5 publication Critical patent/JP2021500029A5/ja
Priority to JP2023151106A priority Critical patent/JP2023166580A/ja
Priority to JP2025127206A priority patent/JP2025157575A/ja
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JP2020522007A 2017-10-20 2018-10-19 Ｎｔ−３遺伝子治療のための方法及び材料 Pending JP2021500029A (ja)

Priority Applications (2)

Application Number Priority Date Filing Date Title
JP2023151106A JP2023166580A (ja) 2017-10-20 2023-09-19 Ｎｔ－３遺伝子治療のための方法及び材料
JP2025127206A JP2025157575A (ja) 2017-10-20 2025-07-30 Ｎｔ－３遺伝子治療のための方法及び材料

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201762574828P 2017-10-20 2017-10-20
US62/574,828 2017-10-20
US201862676687P 2018-05-25 2018-05-25
US62/676,687 2018-05-25
US201862741335P 2018-10-04 2018-10-04
US62/741,335 2018-10-04
PCT/US2018/056765 WO2019079755A1 (en) 2017-10-20 2018-10-19 METHODS AND MATERIALS FOR NT-3 GENE THERAPY

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JP2023151106A Division JP2023166580A (ja) 2017-10-20 2023-09-19 Ｎｔ－３遺伝子治療のための方法及び材料

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JP2021500029A true JP2021500029A (ja) 2021-01-07
JP2021500029A5 JP2021500029A5 (enExample) 2021-12-02

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JP2020522007A Pending JP2021500029A (ja) 2017-10-20 2018-10-19 Ｎｔ−３遺伝子治療のための方法及び材料
JP2023151106A Pending JP2023166580A (ja) 2017-10-20 2023-09-19 Ｎｔ－３遺伝子治療のための方法及び材料
JP2025127206A Pending JP2025157575A (ja) 2017-10-20 2025-07-30 Ｎｔ－３遺伝子治療のための方法及び材料

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JP2023151106A Pending JP2023166580A (ja) 2017-10-20 2023-09-19 Ｎｔ－３遺伝子治療のための方法及び材料
JP2025127206A Pending JP2025157575A (ja) 2017-10-20 2025-07-30 Ｎｔ－３遺伝子治療のための方法及び材料

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US (2) US11926653B2 (enExample)
EP (1) EP3697916A4 (enExample)
JP (3) JP2021500029A (enExample)
KR (2) KR20240164969A (enExample)
CN (2) CN119193705A (enExample)
AU (2) AU2018351528B2 (enExample)
BR (1) BR112020007790A2 (enExample)
CA (1) CA3079416A1 (enExample)
CL (1) CL2020001060A1 (enExample)
CO (1) CO2020006148A2 (enExample)
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SA (1) SA520411798B1 (enExample)
SG (1) SG11202003285PA (enExample)
TW (2) TWI879721B (enExample)
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SG11202006722RA (en) 2018-01-31 2020-08-28 Res Inst Nationwide Childrens Hospital Gene therapy for limb-girdle muscular dystrophy type 2c
KR20210028162A (ko) 2018-06-29 2021-03-11 더 리서치 인스티튜트 앳 네이션와이드 칠드런스 하스피탈 지대근 이영양증 2a형을 치료하기 위한 재조합 아데노 연관 바이러스 생성물 및 방법
CA3131390A1 (en) 2019-02-26 2020-09-03 Research Institute Of Nationwide Children's Hospital Adeno-associated virus vector delivery of b-sarcoglycan and the treatment of muscular dystrophy
GB201907882D0 (en) * 2019-06-03 2019-07-17 Cyprus Foundation For Muscular Dystrophy Res Methods
HRP20240505T1 (hr) 2019-08-21 2024-07-05 Research Institute At Nationwide Children's Hospital Dostava alfa-sarkoglikana vektorom povezanim s adenovirusom i liječenje mišićne distrofije
EP4025258A4 (en) * 2019-09-03 2023-09-06 University of Cincinnati METHODS AND COMPOSITIONS FOR THE TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS
WO2021211705A1 (en) * 2020-04-14 2021-10-21 Research Institute At Nationwide Children's Hospital Treatment of sarcopenia using nt-3 gene therapy
WO2021211713A1 (en) * 2020-04-14 2021-10-21 Research Institute At Nationwide Children's Hospital Treatment of charcot-marie-tooth axonal type 2d using nt-3 gene therapy
CN116440252A (zh) * 2020-06-16 2023-07-18 温州医科大学附属第二医院（温州医科大学附属育英儿童医院） 神经营养因子3在制备提高睾丸中睾酮含量的药物中的应用
EP4108263A3 (en) * 2021-06-02 2023-03-22 Research Institute at Nationwide Children's Hospital Recombinant adeno-associated virus products and methods for treating limb girdle muscular dystrophy 2a
EP4219726A1 (en) 2021-10-15 2023-08-02 Research Institute at Nationwide Children's Hospital Self-complementary adeno-associated virus vector and its use in treatment of muscular dystrophy
CN115838725B (zh) * 2022-12-30 2023-09-08 广州派真生物技术有限公司 在哺乳动物心脏中特异性启动基因的启动子序列及其应用
AU2024265705A1 (en) 2023-05-02 2025-11-20 Research Institute At Nationwide Children's Hospital Gene therapy for treatment of protein misfolding diseases
WO2024229115A1 (en) * 2023-05-02 2024-11-07 Research Institute At Nationwide Children's Hospital Treatment of multiple sclerosis using nt-3 gene therapy
CN119899809A (zh) * 2025-01-07 2025-04-29 广州派真生物技术有限公司 一种提高重组腺相关病毒生产效率的方法及应用

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