JP2020520643A5 - - Google Patents
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- Publication number
- JP2020520643A5 JP2020520643A5 JP2019563548A JP2019563548A JP2020520643A5 JP 2020520643 A5 JP2020520643 A5 JP 2020520643A5 JP 2019563548 A JP2019563548 A JP 2019563548A JP 2019563548 A JP2019563548 A JP 2019563548A JP 2020520643 A5 JP2020520643 A5 JP 2020520643A5
- Authority
- JP
- Japan
- Prior art keywords
- item
- expression cassette
- factor
- transgene
- cassette according
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2022152422A JP2022173348A (ja) | 2017-05-19 | 2022-09-26 | 高活性制御エレメント |
| JP2023211093A JP2024015408A (ja) | 2017-05-19 | 2023-12-14 | 高活性制御エレメント |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762508968P | 2017-05-19 | 2017-05-19 | |
| US62/508,968 | 2017-05-19 | ||
| PCT/US2018/033515 WO2018213786A1 (en) | 2017-05-19 | 2018-05-18 | High activity regulatory elements |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022152422A Division JP2022173348A (ja) | 2017-05-19 | 2022-09-26 | 高活性制御エレメント |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2020520643A JP2020520643A (ja) | 2020-07-16 |
| JP2020520643A5 true JP2020520643A5 (enExample) | 2021-07-26 |
| JP7315475B2 JP7315475B2 (ja) | 2023-07-26 |
Family
ID=64274721
Family Applications (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019563548A Active JP7315475B2 (ja) | 2017-05-19 | 2018-05-18 | 高活性制御エレメント |
| JP2022152422A Pending JP2022173348A (ja) | 2017-05-19 | 2022-09-26 | 高活性制御エレメント |
| JP2023211093A Pending JP2024015408A (ja) | 2017-05-19 | 2023-12-14 | 高活性制御エレメント |
Family Applications After (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022152422A Pending JP2022173348A (ja) | 2017-05-19 | 2022-09-26 | 高活性制御エレメント |
| JP2023211093A Pending JP2024015408A (ja) | 2017-05-19 | 2023-12-14 | 高活性制御エレメント |
Country Status (11)
| Country | Link |
|---|---|
| US (2) | US12104175B2 (enExample) |
| EP (1) | EP3624858A4 (enExample) |
| JP (3) | JP7315475B2 (enExample) |
| KR (2) | KR102636351B1 (enExample) |
| CN (2) | CN110944674B (enExample) |
| AU (1) | AU2018269050A1 (enExample) |
| BR (1) | BR112019024222A2 (enExample) |
| CA (1) | CA3063464A1 (enExample) |
| MA (1) | MA49153A (enExample) |
| TW (1) | TWI811219B (enExample) |
| WO (1) | WO2018213786A1 (enExample) |
Families Citing this family (17)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| GB201420139D0 (en) | 2014-11-12 | 2014-12-24 | Ucl Business Plc | Factor IX gene therapy |
| CN117821509A (zh) | 2017-04-03 | 2024-04-05 | 编码治疗公司 | 组织选择性转基因表达 |
| CA3063464A1 (en) | 2017-05-19 | 2018-11-22 | Encoded Therapeutics, Inc. | High activity regulatory elements |
| CN118345115A (zh) | 2017-12-01 | 2024-07-16 | 编码治疗公司 | 工程化的dna结合蛋白 |
| GB201813528D0 (en) | 2018-08-20 | 2018-10-03 | Ucl Business Plc | Factor IX encoding nucleotides |
| US10842885B2 (en) | 2018-08-20 | 2020-11-24 | Ucl Business Ltd | Factor IX encoding nucleotides |
| WO2020150832A1 (en) * | 2019-01-24 | 2020-07-30 | Valorisation-Hsj, Limited Partnership | Cell-specific transcriptional regulatory sequences and uses thereof |
| EA202192801A1 (ru) * | 2019-04-12 | 2022-02-24 | Инкоудид Терапьютикс, Инк. | Композиции и способы введения лекарственных средств |
| SG11202113048SA (en) | 2019-05-29 | 2021-12-30 | Encoded Therapeutics Inc | Compositions and methods for selective gene regulation |
| CA3147875A1 (en) | 2019-07-19 | 2021-01-28 | Flagship Pioneering Innovations Vi, Llc | Recombinase compositions and methods of use |
| CN113088519B (zh) * | 2019-12-23 | 2024-02-02 | 苏州华毅乐健生物科技有限公司 | 一种分离的核酸分子及其应用 |
| AU2021218703A1 (en) * | 2020-02-14 | 2022-07-28 | Ultragenyx Pharmaceutical Inc. | Gene therapy for treating CDKL5 deficiency disorder |
| JP7862321B2 (ja) * | 2020-04-27 | 2026-05-19 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | Ｃｄｋｌ５欠損症（ｃｄｄ）の治療において有用な組成物 |
| WO2023015304A1 (en) * | 2021-08-05 | 2023-02-09 | Insmed Incorporated | Adeno-associated virus particles and methods of use thereof |
| JP2025533994A (ja) * | 2022-10-11 | 2025-10-09 | メイラグティーエックス ユーケー アイアイ リミティド | Ａｔｐ７ｂ遺伝子療法 |
| CN117925624B (zh) * | 2024-03-22 | 2024-05-31 | 上海凌医生物科技有限公司 | 一种金属响应调控元件 |
| CN117947035A (zh) * | 2024-03-25 | 2024-04-30 | 上海凌医生物科技有限公司 | 一种增强基因表达的启动子 |
Family Cites Families (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2001036620A2 (en) * | 1999-11-16 | 2001-05-25 | Genzyme Corporation | Vectors and transgenies with regulatory elements for gene delivery to the liver |
| US6436703B1 (en) * | 2000-03-31 | 2002-08-20 | Hyseq, Inc. | Nucleic acids and polypeptides |
| EP1783645A1 (en) * | 2005-11-08 | 2007-05-09 | Actigenics | Methods for the identification of microRNA and their applications in research and human health |
| EP2097538A4 (en) | 2006-12-07 | 2011-11-30 | Switchgear Genomics | TRANSCRIPTION REAGULATION ELEMENTS OF BIOLOGICAL PATHS, TOOLS AND METHODS |
| GB0911870D0 (en) | 2009-07-08 | 2009-08-19 | Ucl Business Plc | Optimised coding sequence and promoter |
| US20130129668A1 (en) * | 2011-09-01 | 2013-05-23 | The Regents Of The University Of California | Diagnosis and treatment of arthritis using epigenetics |
| BR112014020325A2 (pt) | 2012-02-17 | 2017-08-08 | Childrens Hospital Philadelphia | composições de vetor do aav e métodos para a transferência de gene para as células, órgãos e tecidos |
| EP2909324B1 (en) | 2012-10-25 | 2020-02-26 | Tocagen Inc. | Retroviral vector with mini-promoter cassette |
| CN107208105A (zh) * | 2014-12-17 | 2017-09-26 | 基础应用医学研究基金会 | 用于治疗威尔森病的核酸构建体和基因治疗载体 |
| TWI707951B (zh) * | 2015-04-08 | 2020-10-21 | 美商健臻公司 | 過大腺相關載體之製造 |
| CA3063464A1 (en) | 2017-05-19 | 2018-11-22 | Encoded Therapeutics, Inc. | High activity regulatory elements |
| CN118345115A (zh) * | 2017-12-01 | 2024-07-16 | 编码治疗公司 | 工程化的dna结合蛋白 |
| WO2020176896A1 (en) * | 2019-02-28 | 2020-09-03 | Encoded Therapeutics, Inc. | Compositions and methods for treating laminopathies |
-
2018
- 2018-05-18 CA CA3063464A patent/CA3063464A1/en active Pending
- 2018-05-18 CN CN201880048355.4A patent/CN110944674B/zh not_active Expired - Fee Related
- 2018-05-18 MA MA049153A patent/MA49153A/fr unknown
- 2018-05-18 AU AU2018269050A patent/AU2018269050A1/en not_active Abandoned
- 2018-05-18 KR KR1020197037368A patent/KR102636351B1/ko active Active
- 2018-05-18 KR KR1020247004550A patent/KR20240024326A/ko not_active Ceased
- 2018-05-18 WO PCT/US2018/033515 patent/WO2018213786A1/en not_active Ceased
- 2018-05-18 CN CN202411101805.5A patent/CN118956965A/zh active Pending
- 2018-05-18 JP JP2019563548A patent/JP7315475B2/ja active Active
- 2018-05-18 TW TW107117128A patent/TWI811219B/zh not_active IP Right Cessation
- 2018-05-18 BR BR112019024222-8A patent/BR112019024222A2/pt not_active Application Discontinuation
- 2018-05-18 EP EP18803184.3A patent/EP3624858A4/en not_active Withdrawn
-
2019
- 2019-11-18 US US16/687,426 patent/US12104175B2/en active Active
-
2022
- 2022-09-26 JP JP2022152422A patent/JP2022173348A/ja active Pending
-
2023
- 2023-12-14 JP JP2023211093A patent/JP2024015408A/ja active Pending
-
2024
- 2024-08-01 US US18/792,310 patent/US20240376441A1/en not_active Abandoned
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