JP2020506714A5 - - Google Patents
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- JP2020506714A5 JP2020506714A5 JP2019542703A JP2019542703A JP2020506714A5 JP 2020506714 A5 JP2020506714 A5 JP 2020506714A5 JP 2019542703 A JP2019542703 A JP 2019542703A JP 2019542703 A JP2019542703 A JP 2019542703A JP 2020506714 A5 JP2020506714 A5 JP 2020506714A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- nucleic acid
- ids
- apoeii
- seq
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| GBGB1701968.8A GB201701968D0 (en) | 2017-02-07 | 2017-02-07 | Gene therapy |
| GB1701968.8 | 2017-02-07 | ||
| PCT/GB2018/050347 WO2018146473A1 (en) | 2017-02-07 | 2018-02-07 | Gene therapy |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2020506714A JP2020506714A (ja) | 2020-03-05 |
| JP2020506714A5 true JP2020506714A5 (https=) | 2021-03-25 |
| JP7237364B2 JP7237364B2 (ja) | 2023-03-13 |
Family
ID=58462471
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019542703A Active JP7237364B2 (ja) | 2017-02-07 | 2018-02-07 | 遺伝子治療 |
Country Status (6)
| Country | Link |
|---|---|
| US (2) | US11701390B2 (https=) |
| EP (2) | EP3960188B1 (https=) |
| JP (1) | JP7237364B2 (https=) |
| ES (2) | ES2895263T3 (https=) |
| GB (1) | GB201701968D0 (https=) |
| WO (1) | WO2018146473A1 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| GB201701968D0 (en) * | 2017-02-07 | 2017-03-22 | Univ Manchester | Gene therapy |
| CR20200129A (es) | 2017-10-02 | 2020-08-22 | Denali Therapeutics Inc | Proteínas de fusión que comprenden enzimas de terapia de reemplazo de enzimas |
| CN120603951A (zh) | 2022-11-01 | 2025-09-05 | 鹿特丹伊拉斯谟大学医疗中心 | 用于代谢病症的基因治疗 |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2003286870A1 (en) | 2003-06-05 | 2005-01-04 | Salk Institute For Biological Studies | Targeting polypeptides to the central nervous system |
| EP1694345A1 (en) * | 2003-12-04 | 2006-08-30 | Regents Of The University Of Minnesota | Compositions and methods for the treatment of lysosomal storage disorders |
| EP2709670A4 (en) | 2011-05-18 | 2015-01-21 | Childrens Hosp Medical Center | TARGETED TRANSFER OF PROTEINS OVER THE BLOOD BRAIN BARRIER |
| BR112014013250A2 (pt) | 2011-12-01 | 2019-09-24 | Angiochem Inc | compostos com enzima alvo e usos dos mesmos |
| US20180185495A1 (en) * | 2014-11-10 | 2018-07-05 | Alexion Pharmaceuticals, Inc. | Therapeutic compositions of alpha-l-iduronidase, iduronate-2-sulfatase, and alpha-galactosidase a and methods of use thereof |
| GB201701968D0 (en) * | 2017-02-07 | 2017-03-22 | Univ Manchester | Gene therapy |
-
2017
- 2017-02-07 GB GBGB1701968.8A patent/GB201701968D0/en not_active Ceased
-
2018
- 2018-02-07 ES ES18705462T patent/ES2895263T3/es active Active
- 2018-02-07 EP EP21187825.1A patent/EP3960188B1/en active Active
- 2018-02-07 EP EP18705462.2A patent/EP3579849B1/en active Active
- 2018-02-07 ES ES21187825T patent/ES3035262T3/es active Active
- 2018-02-07 JP JP2019542703A patent/JP7237364B2/ja active Active
- 2018-02-07 US US16/484,311 patent/US11701390B2/en active Active
- 2018-02-07 WO PCT/GB2018/050347 patent/WO2018146473A1/en not_active Ceased
-
2022
- 2022-12-22 US US18/086,719 patent/US20230390340A1/en active Pending
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