JP2020506714A5 - - Google Patents

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JP2020506714A5
JP2020506714A5 JP2019542703A JP2019542703A JP2020506714A5 JP 2020506714 A5 JP2020506714 A5 JP 2020506714A5 JP 2019542703 A JP2019542703 A JP 2019542703A JP 2019542703 A JP2019542703 A JP 2019542703A JP 2020506714 A5 JP2020506714 A5 JP 2020506714A5
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Japan
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sequence
nucleic acid
ids
apoeii
seq
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JP2019542703A
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Japanese (ja)
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JP7237364B2 (ja
JP2020506714A (ja
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Priority claimed from GBGB1701968.8A external-priority patent/GB201701968D0/en
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JP2019542703A 2017-02-07 2018-02-07 遺伝子治療 Active JP7237364B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
GBGB1701968.8A GB201701968D0 (en) 2017-02-07 2017-02-07 Gene therapy
GB1701968.8 2017-02-07
PCT/GB2018/050347 WO2018146473A1 (en) 2017-02-07 2018-02-07 Gene therapy

Publications (3)

Publication Number Publication Date
JP2020506714A JP2020506714A (ja) 2020-03-05
JP2020506714A5 true JP2020506714A5 (https=) 2021-03-25
JP7237364B2 JP7237364B2 (ja) 2023-03-13

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ID=58462471

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JP2019542703A Active JP7237364B2 (ja) 2017-02-07 2018-02-07 遺伝子治療

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US (2) US11701390B2 (https=)
EP (2) EP3579849B1 (https=)
JP (1) JP7237364B2 (https=)
ES (2) ES3035262T3 (https=)
GB (1) GB201701968D0 (https=)
WO (1) WO2018146473A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
GB201701968D0 (en) * 2017-02-07 2017-03-22 Univ Manchester Gene therapy
AU2018345303B2 (en) 2017-10-02 2025-09-18 Denali Therapeutics Inc. Fusion proteins comprising enzyme replacement therapy enzymes
EP4611783A1 (en) 2022-11-01 2025-09-10 Erasmus University Rotterdam Medical Center Gene therapy constructs for metabolic disorders

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2004108071A2 (en) 2003-06-05 2004-12-16 Salk Institute For Biological Studies Targeting polypeptides to the central nervous system
AU2004296848A1 (en) * 2003-12-04 2005-06-23 Regents Of The University Of Minnesota Compositions and methods for the treatment of lysosomal storage disorders
EP2709670A4 (en) 2011-05-18 2015-01-21 Childrens Hosp Medical Center TARGETED TRANSFER OF PROTEINS OVER THE BLOOD BRAIN BARRIER
WO2013078562A2 (en) 2011-12-01 2013-06-06 Angiochem Inc. Targeted enzyme compounds and uses thereof
EP3218000A2 (en) * 2014-11-10 2017-09-20 Alexion Pharmaceuticals, Inc. Therapeutic compositions of alpha-l-iduronidase, iduronate-2-sulfatase, and alpha-galactosidase a and methods of use thereof
GB201701968D0 (en) * 2017-02-07 2017-03-22 Univ Manchester Gene therapy

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