JP2010525084A - 薬理シャペロンを用いたリソソーム蓄積症治療のための投薬計画 - Google Patents
薬理シャペロンを用いたリソソーム蓄積症治療のための投薬計画 Download PDFInfo
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P7/00—Drugs for disorders of the blood or the extracellular fluid
- A61P7/06—Antianaemics
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P9/00—Drugs for disorders of the cardiovascular system
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- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
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Applications Claiming Priority (4)
| Application Number | Priority Date | Filing Date | Title |
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| US91428807P | 2007-04-26 | 2007-04-26 | |
| US1474407P | 2007-12-18 | 2007-12-18 | |
| US2810508P | 2008-02-12 | 2008-02-12 | |
| PCT/US2008/061764 WO2008134628A2 (en) | 2007-04-26 | 2008-04-28 | Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones |
Publications (2)
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| JP2010525084A true JP2010525084A (ja) | 2010-07-22 |
| JP2010525084A5 JP2010525084A5 (enExample) | 2011-05-19 |
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| JP2010506557A Pending JP2010525084A (ja) | 2007-04-26 | 2008-04-28 | 薬理シャペロンを用いたリソソーム蓄積症治療のための投薬計画 |
Country Status (8)
| Country | Link |
|---|---|
| US (2) | US9056101B2 (enExample) |
| EP (1) | EP2150254A4 (enExample) |
| JP (1) | JP2010525084A (enExample) |
| AU (1) | AU2008245578A1 (enExample) |
| CA (1) | CA2685332A1 (enExample) |
| IL (1) | IL201733A0 (enExample) |
| MX (1) | MX2009011473A (enExample) |
| WO (1) | WO2008134628A2 (enExample) |
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| JP2017511372A (ja) * | 2014-04-14 | 2017-04-20 | アミカス セラピューティックス インコーポレイテッド | 脳アミロイドーシスを処置及び／又は予防する投与計画 |
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| WO2004069190A2 (en) | 2003-01-31 | 2004-08-19 | Mount Sinai School Of Medicine Of New York University | Combination therapy for treating protein deficiency disorders |
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| KR102430856B1 (ko) | 2016-05-03 | 2022-08-08 | 에스큐지 바이오테크놀로지스 컴퍼니 | 관용을 유도하는 생체분자의 세포내 전달 |
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| EP1909812A4 (en) * | 2005-07-27 | 2009-11-25 | Univ Florida | SMALL CONNECTIONS FOR THE CORRECTION OF PROTEIN MISFAIRINGS AND USES THEREOF |
| WO2007137072A2 (en) * | 2006-05-16 | 2007-11-29 | Amicus Therapeutics, Inc. | Assays for diagnosing and evaluating treatment options for fabry disease |
| US20100113517A1 (en) * | 2007-03-30 | 2010-05-06 | Amicus Therapeutics, Inc. | Method for the treatment of fabry disease using pharmacological chaperones |
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- 2008-04-28 WO PCT/US2008/061764 patent/WO2008134628A2/en not_active Ceased
- 2008-04-28 EP EP08747020A patent/EP2150254A4/en not_active Withdrawn
- 2008-04-28 CA CA002685332A patent/CA2685332A1/en not_active Abandoned
- 2008-04-28 US US12/597,238 patent/US9056101B2/en active Active
- 2008-04-28 MX MX2009011473A patent/MX2009011473A/es not_active Application Discontinuation
- 2008-04-28 JP JP2010506557A patent/JP2010525084A/ja active Pending
- 2008-04-28 AU AU2008245578A patent/AU2008245578A1/en not_active Abandoned
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2009
- 2009-10-25 IL IL201733A patent/IL201733A0/en unknown
-
2015
- 2015-05-15 US US14/713,821 patent/US20150352093A1/en not_active Abandoned
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Also Published As
| Publication number | Publication date |
|---|---|
| EP2150254A4 (en) | 2010-11-10 |
| MX2009011473A (es) | 2010-01-18 |
| WO2008134628A2 (en) | 2008-11-06 |
| US9056101B2 (en) | 2015-06-16 |
| US20100266571A1 (en) | 2010-10-21 |
| US20150352093A1 (en) | 2015-12-10 |
| IL201733A0 (en) | 2010-06-16 |
| EP2150254A2 (en) | 2010-02-10 |
| CA2685332A1 (en) | 2008-11-06 |
| AU2008245578A1 (en) | 2008-11-06 |
| WO2008134628A3 (en) | 2010-01-14 |
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