JP2010525084A - 薬理シャペロンを用いたリソソーム蓄積症治療のための投薬計画 - Google Patents
薬理シャペロンを用いたリソソーム蓄積症治療のための投薬計画 Download PDFInfo
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P7/00—Drugs for disorders of the blood or the extracellular fluid
- A61P7/06—Antianaemics
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P9/00—Drugs for disorders of the cardiovascular system
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- Chemical & Material Sciences (AREA)
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- Animal Behavior & Ethology (AREA)
- Life Sciences & Earth Sciences (AREA)
- Engineering & Computer Science (AREA)
- Bioinformatics & Cheminformatics (AREA)
- General Chemical & Material Sciences (AREA)
- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
- Chemical Kinetics & Catalysis (AREA)
- Organic Chemistry (AREA)
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- Neurosurgery (AREA)
- Biomedical Technology (AREA)
- Diabetes (AREA)
- Hematology (AREA)
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- Heart & Thoracic Surgery (AREA)
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- Psychology (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
- Hydrogenated Pyridines (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
Applications Claiming Priority (4)
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| US91428807P | 2007-04-26 | 2007-04-26 | |
| US1474407P | 2007-12-18 | 2007-12-18 | |
| US2810508P | 2008-02-12 | 2008-02-12 | |
| PCT/US2008/061764 WO2008134628A2 (en) | 2007-04-26 | 2008-04-28 | Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones |
Publications (2)
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| JP2010525084A true JP2010525084A (ja) | 2010-07-22 |
| JP2010525084A5 JP2010525084A5 (enExample) | 2011-05-19 |
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| EP (1) | EP2150254A4 (enExample) |
| JP (1) | JP2010525084A (enExample) |
| AU (1) | AU2008245578A1 (enExample) |
| CA (1) | CA2685332A1 (enExample) |
| IL (1) | IL201733A0 (enExample) |
| MX (1) | MX2009011473A (enExample) |
| WO (1) | WO2008134628A2 (enExample) |
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| WO2009102895A2 (en) | 2008-02-12 | 2009-08-20 | Amicus Therapeutics, Inc. | Method to predict response to pharmacological chaperone treatment of diseases |
| JP5616336B2 (ja) | 2008-06-26 | 2014-10-29 | オルファザイム エーピーエスＯｒｐｈａｚｙｍｅ Ａｐｓ | 酵素活性の調節因子としてのＨｓｐ７０の使用 |
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| JP5645918B2 (ja) | 2009-04-09 | 2014-12-24 | アミカス セラピューティックス インコーポレイテッド | リソソーム蓄積障害の予防および／または治療方法 |
| DK2490712T3 (en) * | 2009-10-19 | 2015-10-05 | Amicus Therapeutics Inc | PROCESS FOR THE TREATMENT OF ALZHEIMER'S DISEASE BY USING Pharmacological chaperones TO INCREASE ACTIVITY OF GANGLIOSIDASER |
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| KR20190134807A (ko) | 2017-04-25 | 2019-12-04 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 중추 신경계의 퇴행성 질환 및/또는 리소솜 저장병을 예방 및/또는 치료하기 위한 신규한 조성물 |
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2008
- 2008-04-28 AU AU2008245578A patent/AU2008245578A1/en not_active Abandoned
- 2008-04-28 US US12/597,238 patent/US9056101B2/en active Active
- 2008-04-28 MX MX2009011473A patent/MX2009011473A/es not_active Application Discontinuation
- 2008-04-28 JP JP2010506557A patent/JP2010525084A/ja active Pending
- 2008-04-28 CA CA002685332A patent/CA2685332A1/en not_active Abandoned
- 2008-04-28 WO PCT/US2008/061764 patent/WO2008134628A2/en not_active Ceased
- 2008-04-28 EP EP08747020A patent/EP2150254A4/en not_active Withdrawn
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2009
- 2009-10-25 IL IL201733A patent/IL201733A0/en unknown
-
2015
- 2015-05-15 US US14/713,821 patent/US20150352093A1/en not_active Abandoned
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Also Published As
| Publication number | Publication date |
|---|---|
| CA2685332A1 (en) | 2008-11-06 |
| WO2008134628A3 (en) | 2010-01-14 |
| MX2009011473A (es) | 2010-01-18 |
| WO2008134628A2 (en) | 2008-11-06 |
| EP2150254A4 (en) | 2010-11-10 |
| IL201733A0 (en) | 2010-06-16 |
| US9056101B2 (en) | 2015-06-16 |
| US20150352093A1 (en) | 2015-12-10 |
| EP2150254A2 (en) | 2010-02-10 |
| US20100266571A1 (en) | 2010-10-21 |
| AU2008245578A1 (en) | 2008-11-06 |
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