CN116981775A - 用于治疗神经退行性疾病的基因治疗 - Google Patents
用于治疗神经退行性疾病的基因治疗 Download PDFInfo
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PCT/KR2022/001598 WO2022164260A1 (ko) | 2021-01-28 | 2022-01-28 | 신경 퇴행성 질환의 치료를 위한 유전자 요법 |
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JP (1) | JP2024508635A (ja) |
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US4797368A (en) | 1985-03-15 | 1989-01-10 | The United States Of America As Represented By The Department Of Health And Human Services | Adeno-associated virus as eukaryotic expression vector |
US5139941A (en) | 1985-10-31 | 1992-08-18 | University Of Florida Research Foundation, Inc. | AAV transduction vectors |
WO2017069182A1 (ja) * | 2015-10-22 | 2017-04-27 | 免疫療法開発株式会社 | アミロイドβ及びタウに対するDNAワクチン |
WO2017075119A1 (en) * | 2015-10-28 | 2017-05-04 | The Trustees Of The Univeresity Of Pennsylvania | Intrathecal administration of adeno-associated-viral vectors for gene therapy |
BR112020008033A2 (pt) | 2017-10-23 | 2020-10-27 | Prevail Therapeutics, Inc. | terapias gênicas para doença neurodegenerativa |
KR102050296B1 (ko) | 2018-05-04 | 2019-12-02 | (주)지뉴인텍 | 유전자 전달용 재조합 벡터 및 이를 이용한 퇴행성 뇌질환 예방 또는 치료용 조성물 |
WO2020232440A1 (en) * | 2019-05-16 | 2020-11-19 | The Regents Of The University Of California | Peptide-based inhibitors that block aggregation, seeding and cross-seeding of amyloid beta and tau |
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JP2024508635A (ja) | 2024-02-28 |
AU2022213255A1 (en) | 2023-08-24 |
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