CN111433361B - 天使综合征反义治疗 - Google Patents

天使综合征反义治疗 Download PDF

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CN111433361B
CN111433361B CN201880077892.1A CN201880077892A CN111433361B CN 111433361 B CN111433361 B CN 111433361B CN 201880077892 A CN201880077892 A CN 201880077892A CN 111433361 B CN111433361 B CN 111433361B
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artificial sequence
synthetic construct
rna
dna
aso
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CN111433361A (zh
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S·V·迪多
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Texas A&M University
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CN201880077892.1A 2017-12-01 2018-11-30 天使综合征反义治疗 Active CN111433361B (zh)

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US201762593431P 2017-12-01 2017-12-01
US62/593,431 2017-12-01
US201862676034P 2018-05-24 2018-05-24
US62/676,034 2018-05-24
PCT/US2018/063416 WO2019109001A1 (en) 2017-12-01 2018-11-30 Angelman syndrome antisense treatment

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WO2019168950A1 (en) * 2018-02-27 2019-09-06 The University Of North Carolina At Chapel Hill Methods and compositions for treating angelman syndrome
TWI874376B (zh) 2019-03-29 2025-03-01 美商Ionis製藥公司 用於調節ube3a-ats 之化合物及方法
TW202216996A (zh) * 2020-06-29 2022-05-01 美商Ionis製藥公司 調節ｐｌｐ１之化合物及方法
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CN120476156A (zh) 2023-01-31 2025-08-12 富士胶片株式会社 固化性组合物、固化物、光学材料、衍射光学元件及化合物
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EP4328306A2 (en) 2024-02-28
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EP3717646A4 (en) 2021-12-01
FI3717646T3 (fi) 2025-07-17
US11685920B2 (en) 2023-06-27
JP2021505129A (ja) 2021-02-18
US12180480B2 (en) 2024-12-31
PL3717646T3 (pl) 2025-10-27
CO2020006361A2 (es) 2020-08-10
PT3717646T (pt) 2025-07-28
IL274146A (en) 2020-06-30
US20230332152A1 (en) 2023-10-19
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AU2018375807B2 (en) 2025-04-10
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JP2025041632A (ja) 2025-03-26
US20230112629A1 (en) 2023-04-13
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