CN108348576B - Htt阻抑物及其用途 - Google Patents

Htt阻抑物及其用途 Download PDF

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CN108348576B
CN108348576B CN201680061809.2A CN201680061809A CN108348576B CN 108348576 B CN108348576 B CN 108348576B CN 201680061809 A CN201680061809 A CN 201680061809A CN 108348576 B CN108348576 B CN 108348576B
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htt
cell
cells
protein
domain
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CN108348576A (zh
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S·弗洛里奇
J·C·米勒
D·帕斯乔恩
E·J·瑞巴
B·泽特勒
H·S·张
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Sangamo Therapeutics Inc
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    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
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CN201680061809.2A 2015-09-23 2016-09-23 Htt阻抑物及其用途 Active CN108348576B (zh)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562222588P 2015-09-23 2015-09-23
US62/222,588 2015-09-23
PCT/US2016/053374 WO2017053753A1 (en) 2015-09-23 2016-09-23 Htt repressors and uses thereof

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CN108348576A CN108348576A (zh) 2018-07-31
CN108348576B true CN108348576B (zh) 2022-01-11

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EP (1) EP3352776B1 (https=)
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