CN104271125A - 用于治疗唾液酸缺乏的方法和制剂 - Google Patents

用于治疗唾液酸缺乏的方法和制剂 Download PDF

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Publication number
CN104271125A
CN104271125A CN201380015020.XA CN201380015020A CN104271125A CN 104271125 A CN104271125 A CN 104271125A CN 201380015020 A CN201380015020 A CN 201380015020A CN 104271125 A CN104271125 A CN 104271125A
Authority
CN
China
Prior art keywords
sialic acid
sustained release
release formulation
pharmaceutically acceptable
acceptable salt
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
CN201380015020.XA
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English (en)
Chinese (zh)
Inventor
E·D·卡基
Current Assignee (The listed assignees may be inaccurate. Google has not performed a legal analysis and makes no representation or warranty as to the accuracy of the list.)
Ultragenyx Pharmaceutical Inc
Original Assignee
Ultragenyx Pharmaceutical Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Ultragenyx Pharmaceutical Inc filed Critical Ultragenyx Pharmaceutical Inc
Publication of CN104271125A publication Critical patent/CN104271125A/zh
Pending legal-status Critical Current

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Classifications

    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00—Medicinal preparations containing organic active ingredients
    • A61K31/70—Carbohydrates; Sugars; Derivatives thereof
    • A61K31/7012—Compounds having a free or esterified carboxyl group attached, directly or through a carbon chain, to a carbon atom of the saccharide radical, e.g. glucuronic acid, neuraminic acid
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00—Medicinal preparations characterised by special physical form
    • A61K9/0002—Galenical forms characterised by the drug release technique; Application systems commanded by energy
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00—Medicinal preparations characterised by special physical form
    • A61K9/20—Pills, tablets, discs, rods
    • A61K9/2004—Excipients; Inactive ingredients
    • A61K9/2022—Organic macromolecular compounds
    • A61K9/205—Polysaccharides, e.g. alginate, gums; Cyclodextrin
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00—Medicinal preparations characterised by special physical form
    • A61K9/20—Pills, tablets, discs, rods
    • A61K9/2004—Excipients; Inactive ingredients
    • A61K9/2022—Organic macromolecular compounds
    • A61K9/205—Polysaccharides, e.g. alginate, gums; Cyclodextrin
    • A61K9/2054—Cellulose; Cellulose derivatives, e.g. hydroxypropyl methylcellulose
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Veterinary Medicine (AREA)
  • Chemical & Material Sciences (AREA)
  • Medicinal Chemistry (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Animal Behavior & Ethology (AREA)
  • General Health & Medical Sciences (AREA)
  • Public Health (AREA)
  • Epidemiology (AREA)
  • Engineering & Computer Science (AREA)
  • Molecular Biology (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Neurology (AREA)
  • Orthopedic Medicine & Surgery (AREA)
  • Physical Education & Sports Medicine (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • General Chemical & Material Sciences (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Organic Chemistry (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Medicinal Preparation (AREA)
CN201380015020.XA 2012-01-18 2013-01-18 用于治疗唾液酸缺乏的方法和制剂 Pending CN104271125A (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201261588069P 2012-01-18 2012-01-18
US61/588,069 2012-01-18
US201261709549P 2012-10-04 2012-10-04
US61/709,549 2012-10-04
PCT/US2013/022167 WO2013109906A2 (en) 2012-01-18 2013-01-18 Methods and formulations for treating sialic acid deficiencies

Publications (1)

Publication Number Publication Date
CN104271125A true CN104271125A (zh) 2015-01-07

Family

ID=48799814

Family Applications (1)

Application Number Title Priority Date Filing Date
CN201380015020.XA Pending CN104271125A (zh) 2012-01-18 2013-01-18 用于治疗唾液酸缺乏的方法和制剂

Country Status (9)

Country Link
EP (1) EP2804600A4 (https=)
JP (2) JP2015504094A (https=)
KR (1) KR20150000872A (https=)
CN (1) CN104271125A (https=)
AU (1) AU2013209610B2 (https=)
BR (1) BR112014017587A8 (https=)
CA (1) CA2862836A1 (https=)
IL (1) IL233225A0 (https=)
WO (1) WO2013109906A2 (https=)

Cited By (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN117969774A (zh) * 2024-04-02 2024-05-03 小仙炖霸州食品有限公司 一种自动化燕窝检测与分级系统

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US9241896B2 (en) 2008-12-19 2016-01-26 Ultragenyx Pharmaceutical Inc. Methods and formulations for treating sialic acid deficiencies
CA2805222A1 (en) 2010-07-13 2012-01-19 Ultragenyx Pharmaceutical Inc. Methods and formulations for treating sialic acid deficiencies
HK1201067A1 (en) 2011-10-24 2015-08-21 罕见病药物研发公司 Sialic acid analogs
US10385085B2 (en) 2015-09-14 2019-08-20 Ultragenyx Pharmaceutical Inc. Crystal forms of sialic acid or salt or solvate thereof
EP3486326A1 (en) 2017-11-21 2019-05-22 Jennewein Biotechnologie GmbH Method for the purification of n-acetylneuraminic acid from a fermentation broth

Citations (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2010080580A2 (en) * 2008-12-19 2010-07-15 Aaipharma Servcies Corp. Extended-release pharmaceutical formulations
WO2012009474A1 (en) * 2010-07-13 2012-01-19 Ultragenyx Pharmaceutical Inc. Method and formulations for treating sialic acid deficiencies

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP2155207A2 (en) * 2007-05-31 2010-02-24 Government Of The United States Of America As Represented by Secretary of the Dep. of Health and Human Services National Institute of Health N-acetyl mannosamine as a therapeutic agent
CN102427817B (zh) * 2009-05-15 2015-02-11 财团法人日本健康科学振兴财团 起因于gne蛋白质功能降低的疾病的治疗用药物、食品组合物、食品添加剂
HK1201067A1 (en) * 2011-10-24 2015-08-21 罕见病药物研发公司 Sialic acid analogs

Patent Citations (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2010080580A2 (en) * 2008-12-19 2010-07-15 Aaipharma Servcies Corp. Extended-release pharmaceutical formulations
WO2012009474A1 (en) * 2010-07-13 2012-01-19 Ultragenyx Pharmaceutical Inc. Method and formulations for treating sialic acid deficiencies

Non-Patent Citations (1)

* Cited by examiner, † Cited by third party
Title
MAY CHRISTINE V MALICDAN等: "Prophylactic treatment with sialic acid metabolites precludes the development of the myopathic phenotype in the DMRV-hIBM mouse model", 《NATURE MEDICINE》 *

Cited By (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN117969774A (zh) * 2024-04-02 2024-05-03 小仙炖霸州食品有限公司 一种自动化燕窝检测与分级系统
CN117969774B (zh) * 2024-04-02 2024-06-11 小仙炖霸州食品有限公司 一种自动化燕窝检测与分级系统

Also Published As

Publication number Publication date
EP2804600A2 (en) 2014-11-26
JP2015504094A (ja) 2015-02-05
KR20150000872A (ko) 2015-01-05
EP2804600A4 (en) 2015-09-02
BR112014017587A8 (pt) 2017-07-04
AU2013209610A1 (en) 2014-07-10
IL233225A0 (en) 2014-08-31
JP2017186381A (ja) 2017-10-12
AU2013209610B2 (en) 2017-11-30
CA2862836A1 (en) 2013-07-25
WO2013109906A2 (en) 2013-07-25
BR112014017587A2 (pt) 2017-06-13

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PB01 Publication
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SE01 Entry into force of request for substantive examination
WD01 Invention patent application deemed withdrawn after publication
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Application publication date: 20150107