CA3186700A1 - Gene therapy vector for eef1a2 and uses thereof - Google Patents
Gene therapy vector for eef1a2 and uses thereofInfo
- Publication number
- CA3186700A1 CA3186700A1 CA3186700A CA3186700A CA3186700A1 CA 3186700 A1 CA3186700 A1 CA 3186700A1 CA 3186700 A CA3186700 A CA 3186700A CA 3186700 A CA3186700 A CA 3186700A CA 3186700 A1 CA3186700 A1 CA 3186700A1
- Authority
- CA
- Canada
- Prior art keywords
- promoter
- eef1a2
- polynucleotide sequence
- raav virion
- seq
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063055775P | 2020-07-23 | 2020-07-23 | |
| US63/055,775 | 2020-07-23 | ||
| PCT/EP2021/070455 WO2022018171A1 (en) | 2020-07-23 | 2021-07-21 | GENE THERAPY VECTOR FOR eEF1A2 AND USES THEREOF |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| CA3186700A1 true CA3186700A1 (en) | 2022-01-27 |
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| CA3186700A Pending CA3186700A1 (en) | 2020-07-23 | 2021-07-21 | Gene therapy vector for eef1a2 and uses thereof |
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| EP (1) | EP4185332A1 (enExample) |
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| CA (1) | CA3186700A1 (enExample) |
| IL (1) | IL299955A (enExample) |
| MX (1) | MX2023000995A (enExample) |
| WO (2) | WO2022017630A1 (enExample) |
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| PL3445406T3 (pl) | 2016-04-20 | 2022-02-07 | Centro De Investigaciones Energéticas, Medioambientales Y Tecnológicas, O.A., M.P. | Kompozycje i sposoby zwiększonej ekspresji genów PKLR |
| AU2018352583B2 (en) | 2017-10-16 | 2025-04-17 | Centro de Investigaciones Energeticas, Medioambientales Y Tecnologicas, O.A., M.P. | Lentiviral vectors for delivery of PKLR to treat Pyruvate Kinase Deficiency |
| RU2020134965A (ru) | 2018-04-27 | 2022-04-27 | Спейскрафт Севен, Ллк | Генная терапия при дегенерации цнс |
| IL300263A (en) | 2020-08-07 | 2023-03-01 | Spacecraft Seven Llc | Plakophilin-2 (PKP2) gene therapy using an AAV vector |
Family Cites Families (12)
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| ATE386131T1 (de) | 1994-04-13 | 2008-03-15 | Univ Rockefeller | Aav-vermittelte überbringung von dna in zellen des nervensystems |
| JP2004514407A (ja) | 2000-04-28 | 2004-05-20 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | 異種キャプシド中にシュードタイピングされたａａｖ５キャプシドおよびａａｖ５ベクターを含む組換えａａｖベクター |
| ATE317916T1 (de) | 2001-11-13 | 2006-03-15 | Univ Pennsylvania | Verfahren zur identifizierung von adeno- assoziiertem virus (aav) sequenzen sowie kit zur ausführung der methode |
| US7122350B2 (en) * | 2003-12-12 | 2006-10-17 | Zymogenetics, Inc. | Methods for enhancing expression of recombinant proteins |
| US8299215B2 (en) | 2007-07-14 | 2012-10-30 | University Of Iowa Research Foundation | Methods and compositions for treating brain diseases |
| WO2011123842A2 (en) | 2010-04-02 | 2011-10-06 | Ceregene, Inc. | Methods for treating parkinson's disease and other disorders of dopaminergic neurons of the brain |
| WO2013078316A1 (en) | 2011-11-23 | 2013-05-30 | Nationwide Children's Hospital, Inc. | Recombinant adeno-associated virus delivery of alpha-sarcoglycan polynucleotides |
| EP3561062A1 (en) | 2013-09-13 | 2019-10-30 | California Institute of Technology | Selective recovery |
| AU2015252797C1 (en) | 2014-05-02 | 2021-04-22 | Genzyme Corporation | AAV vectors for retinal and CNS gene therapy |
| JP2018531926A (ja) * | 2015-09-17 | 2018-11-01 | コーダ バイオセラピューティクス， インコーポレイテッド | 神経学的障害を処置するための組成物および方法 |
| ES2869284T3 (es) | 2015-12-11 | 2021-10-25 | California Inst Of Techn | Péptidos de diana para dirigir virus adenoasociados (AAV) |
| AU2019299970B2 (en) * | 2018-07-12 | 2025-12-11 | Spacecraft Seven, Llc | Gene therapy vectors for treatment of Danon disease |
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2020
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2021
- 2021-07-21 MX MX2023000995A patent/MX2023000995A/es unknown
- 2021-07-21 JP JP2023504517A patent/JP2023535576A/ja active Pending
- 2021-07-21 KR KR1020237003445A patent/KR20230039669A/ko active Pending
- 2021-07-21 CN CN202180056421.4A patent/CN116171325A/zh active Pending
- 2021-07-21 US US18/017,502 patent/US20230330265A1/en active Pending
- 2021-07-21 IL IL299955A patent/IL299955A/en unknown
- 2021-07-21 CA CA3186700A patent/CA3186700A1/en active Pending
- 2021-07-21 EP EP21755896.4A patent/EP4185332A1/en active Pending
- 2021-07-21 AU AU2021312320A patent/AU2021312320A1/en active Pending
- 2021-07-21 WO PCT/EP2021/070455 patent/WO2022018171A1/en not_active Ceased
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| MX2023000995A (es) | 2023-06-16 |
| WO2022017630A1 (en) | 2022-01-27 |
| WO2022018171A1 (en) | 2022-01-27 |
| EP4185332A1 (en) | 2023-05-31 |
| JP2023535576A (ja) | 2023-08-18 |
| KR20230039669A (ko) | 2023-03-21 |
| IL299955A (en) | 2023-03-01 |
| CN116171325A (zh) | 2023-05-26 |
| US20230330265A1 (en) | 2023-10-19 |
| AU2021312320A1 (en) | 2023-03-16 |
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