CA2979229A1 - Rp2 vectors for treating x-linked retinitis pigmentosa - Google Patents
Rp2 vectors for treating x-linked retinitis pigmentosaInfo
- Publication number
- CA2979229A1 CA2979229A1 CA2979229A CA2979229A CA2979229A1 CA 2979229 A1 CA2979229 A1 CA 2979229A1 CA 2979229 A CA2979229 A CA 2979229A CA 2979229 A CA2979229 A CA 2979229A CA 2979229 A1 CA2979229 A1 CA 2979229A1
- Authority
- CA
- Canada
- Prior art keywords
- vector
- mammal
- rpgr
- retina
- protein
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
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| CN117752822A (zh) * | 2017-11-15 | 2024-03-26 | 密歇根大学董事会 | 包括rdh12编码区的病毒载体和治疗视网膜营养不良的方法 |
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| EP3927380A1 (en) * | 2019-02-22 | 2021-12-29 | University of Massachusetts | Oxr1 gene therapy |
| WO2021041924A2 (en) * | 2019-08-30 | 2021-03-04 | Baylor College Of Medicine | System for regulating gene expression |
| WO2021178668A1 (en) * | 2020-03-04 | 2021-09-10 | University Of Massachusetts | Compositions and methods for modulating rpgr expression |
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| CA2900231C (en) * | 2013-02-15 | 2019-07-30 | Paul Albert Sieving | Aav8 retinoschisin expression vector for treating x-linked retinoschisis |
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| JP6635942B2 (ja) | 2014-04-15 | 2020-01-29 | アプライド ジェネティック テクノロジーズ コーポレイション | 網膜色素変性症ｇｔｐアーゼレギュレーター（ｒｐｇｒ）をコードするコドン最適化核酸 |
| AU2015252797C1 (en) * | 2014-05-02 | 2021-04-22 | Genzyme Corporation | AAV vectors for retinal and CNS gene therapy |
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| HRP20241154T1 (hr) | 2014-07-24 | 2024-11-22 | Massachusetts Eye & Ear Infirmary | Rpgr genska terapija za pigmentnu retinopatiju |
| HRP20220776T1 (hr) * | 2015-03-03 | 2022-09-16 | Fondazione Telethon | Sustav višestrukih vektora i njegova upotreba |
| AU2016228751B2 (en) | 2015-03-11 | 2022-01-13 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Rp2 vectors for treating x-linked retinitis pigmentosa |
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| US10646588B2 (en) | 2020-05-12 |
| JP2021019611A (ja) | 2021-02-18 |
| EP3268481A4 (en) | 2018-03-21 |
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| WO2016145345A1 (en) | 2016-09-15 |
| EP3268481A1 (en) | 2018-01-17 |
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| US20200289670A1 (en) | 2020-09-17 |
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