CA2916880C - Methods and compositions for the prevention or treatment of barth syndrome - Google Patents
Methods and compositions for the prevention or treatment of barth syndrome Download PDFInfo
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- CA2916880C CA2916880C CA2916880A CA2916880A CA2916880C CA 2916880 C CA2916880 C CA 2916880C CA 2916880 A CA2916880 A CA 2916880A CA 2916880 A CA2916880 A CA 2916880A CA 2916880 C CA2916880 C CA 2916880C
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Classifications
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- A61K38/04—Peptides having up to 20 amino acids in a fully defined sequence; Derivatives thereof
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- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K45/00—Medicinal preparations containing active ingredients not provided for in groups A61K31/00 - A61K41/00
- A61K45/06—Mixtures of active ingredients without chemical characterisation, e.g. antiphlogistics and cardiaca
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- A61P11/00—Drugs for disorders of the respiratory system
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- A—HUMAN NECESSITIES
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- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P21/00—Drugs for disorders of the muscular or neuromuscular system
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- A—HUMAN NECESSITIES
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- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
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- A—HUMAN NECESSITIES
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P9/00—Drugs for disorders of the cardiovascular system
- A61P9/04—Inotropic agents, i.e. stimulants of cardiac contraction; Drugs for heart failure
Landscapes
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- Life Sciences & Earth Sciences (AREA)
- Veterinary Medicine (AREA)
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- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
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| US201361771642P | 2013-03-01 | 2013-03-01 | |
| US201361771534P | 2013-03-01 | 2013-03-01 | |
| US61/771,534 | 2013-03-01 | ||
| US61/771,642 | 2013-03-01 | ||
| US201361839753P | 2013-06-26 | 2013-06-26 | |
| US61/839,753 | 2013-06-26 | ||
| PCT/US2014/019622 WO2014134554A1 (en) | 2013-03-01 | 2014-02-28 | Methods and compositions for the prevention or treatment of barth syndrome |
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| CA2916880A1 CA2916880A1 (en) | 2014-09-04 |
| CA2916880C true CA2916880C (en) | 2021-02-09 |
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| EP2788013A4 (en) * | 2011-12-09 | 2015-08-19 | Stealth Peptides Int Inc | AROMATIC-CATIONIC PEPTIDES AND USES THEREOF |
| CN117752766A (zh) | 2013-03-01 | 2024-03-26 | 康德生物医疗有限公司 | 治疗线粒体疾病的方法 |
| CN115990242A (zh) * | 2013-03-01 | 2023-04-21 | 康德生物医疗有限公司 | 预防或治疗巴斯综合征的方法和组合物 |
| WO2014209905A2 (en) * | 2013-06-26 | 2014-12-31 | Stealth Peptides International, Inc. | Methods and compositions for detecting and diagnosing diseases and conditions |
| US9550981B2 (en) | 2014-01-22 | 2017-01-24 | University Of Washington | Modified tafazzin proteins and methods of making and using the same |
| EP3230308B1 (en) | 2014-12-12 | 2019-05-01 | University of Washington | Methods for treating and preventing cardiomyopathy |
| WO2018104172A1 (en) | 2016-12-06 | 2018-06-14 | Centre National De La Recherche Scientifique (Cnrs) | Compounds for treating barth syndrome |
| US11034724B2 (en) | 2017-04-05 | 2021-06-15 | Stealth Biotherapeutics Corp. | Crystalline salt forms of Boc-D-Arg-DMT-Lys-(Boc)-Phe-NH2 |
| US10676506B2 (en) | 2018-01-26 | 2020-06-09 | Stealth Biotherapeutics Corp. | Crystalline bis- and tris-hydrochloride salt of elamipretide |
| JP7606966B2 (ja) * | 2018-12-18 | 2024-12-26 | ステルス バイオセラピューティクス インコーポレイテッド | ミトコンドリア病を標的とするアナログ |
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| WO2014134554A1 (en) | 2014-09-04 |
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| JP6918046B2 (ja) | 2021-08-11 |
| EP2961420A4 (en) | 2016-08-17 |
| CN115990241A (zh) | 2023-04-21 |
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| CN115990242A (zh) | 2023-04-21 |
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| JP2019147815A (ja) | 2019-09-05 |
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| EP2961420A1 (en) | 2016-01-06 |
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| CA2916880A1 (en) | 2014-09-04 |
| JP6518197B2 (ja) | 2019-05-22 |
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